NCT06882317

Brief Summary

The goal of this Long Term Follow-Up observational study is to monitor subjects who have received CLBR001, a lentiviral vector based chimeric antigen receptor, for delayed adverse events that may be associated with human gene therapies. Participants will be followed for 15 years post-gene therapy administration date for safety and efficacy.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
40

participants targeted

Target at P25-P50 for all trials

Timeline
216mo left

Started Aug 2025

Longer than P75 for all trials

Geographic Reach
1 country

3 active sites

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress4%
Aug 2025Feb 2044

First Submitted

Initial submission to the registry

March 12, 2025

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 18, 2025

Completed
5 months until next milestone

Study Start

First participant enrolled

August 28, 2025

Completed
18.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2044

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2044

Last Updated

April 8, 2026

Status Verified

April 1, 2026

Enrollment Period

18.4 years

First QC Date

March 12, 2025

Last Update Submit

April 2, 2026

Conditions

Keywords

Long Term Follow-Up (LTFU)CLBR001Autologous Cell TherapySwitchable CAR-T CellCell and Gene Therapy

Outcome Measures

Primary Outcomes (2)

  • Number of subjects with adverse events as assessed by CTCAE v5.0.

    To assess the long term safety of CLBR001 in subjects by evaluating the incidence, duration, and outcome of adverse events (including adverse events of special interest, CLBR001-related adverse events and serious adverse events), as assessed by CTCAE v5.0.

    To 15 years post-CLBR001 administration.

  • Number of subjects with replication competent lentivirus (RCL).

    To assess the long term safety of CLBR001 in subjects by evaluating the proportion of subjects with detectable RCL from CLBR001.

    To 15 years post-CLBR001 administration.

Study Arms (1)

CLBR001 Treated Subjects

Subjects who received CLBR001 on any Calibr treatment study.

Other: Long Term Follow-Up

Interventions

No intervention is administered on this study. Subjects who have received CLBR001 autologous CAR-T cells in a primary Calibr treatment trial will be followed long term in line with FDA guidance.

CLBR001 Treated Subjects

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Subjects who received CLBR001.

You may qualify if:

  • Subjects who received at least one CLBR001 cell dose.

You may not qualify if:

  • None

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Indiana University Melvin and Bren Simon Comprehensive Cancer Center

Indianapolis, Indiana, 46202, United States

Location

Virtual Research Group- Premier Research

Morrisville, North Carolina, 27560, United States

Location

University of Virginia

Charlottesville, Virginia, 22908, United States

Location

Biospecimen

Retention: SAMPLES WITH DNA

Frozen serum leftover following protocol-required testing of PK and ADA may be retained for future research or analytical development involving the same or related therapies or therapeutic areas, or for other relevant health research. This additional testing may involve genetic testing.

Study Officials

  • Chief Medical Officer

    Calibr-Skaggs Institute for Innovative Medicines

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 12, 2025

First Posted

March 18, 2025

Study Start

August 28, 2025

Primary Completion (Estimated)

February 1, 2044

Study Completion (Estimated)

February 1, 2044

Last Updated

April 8, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations