NCT06864988

Brief Summary

A Phase 3, Randomized, Double-Masked, Active-Controlled Trial in Adults with Macular Neovascularization Secondary to Age-Related Macular Degeneration

Trial Health

78
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
480

participants targeted

Target at P50-P75 for phase_3

Timeline
26mo left

Started Mar 2025

Typical duration for phase_3

Geographic Reach
2 countries

100 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress36%
Mar 2025Jun 2028

Study Start

First participant enrolled

March 3, 2025

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

March 4, 2025

Completed
3 days until next milestone

First Posted

Study publicly available on registry

March 7, 2025

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2027

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2028

Last Updated

March 25, 2026

Status Verified

March 1, 2026

Enrollment Period

2.2 years

First QC Date

March 4, 2025

Last Update Submit

March 23, 2026

Conditions

Keywords

Age-related macular degenerationAMDExudative AMDNeovascular AMDExudative age-related macular degenerationNeovascular age-related macular degenerationWet age-related macular degenerationWet macular degenerationWet AMDwAMDRetinal gene therapyIntravitreal gene therapyGenetic MedicineOcular Gene TherapynAMD

Outcome Measures

Primary Outcomes (1)

  • Mean change from baseline in BCVA ETDRS letter score at Week 52

    52 Weeks

Secondary Outcomes (5)

  • Mean annualized number of aflibercept injections after Week 4 through Weeks 52 and 104

    104 Weeks

  • Incidence and timing of aflibercept injections after Week 4 through Weeks 52 and 104

    104 Weeks

  • Proportion of subjects not requiring aflibercept injections after Week 4 through Weeks 52 and 104 in the 4D-150 arm

    104 Weeks

  • Mean change from baseline in CST over time through Weeks 52 and 104

    104 Weeks

  • Mean change from baseline in BCVA ETDRS letter score over time through Weeks 52 and 104

    104 Weeks

Study Arms (2)

4D-150 IVT (3E10 vg/eye)

EXPERIMENTAL
Biological: 4D-150 IVT (3E10 vg/eye)

Aflibercept (AFLB) 2 mg IVT

ACTIVE COMPARATOR
Biological: EYLEA® (aflibercept) Injection 2 mg (0.05mL)

Interventions

Eylea (aflibercept) will be administered at applicable visits

Aflibercept (AFLB) 2 mg IVT

If randomized to the 4D-150 treatment arm, 4D-150 will be administered at the assigned dose level as a single dose IVT injection on Day 1

4D-150 IVT (3E10 vg/eye)

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • ≥50 years of age at time of consent
  • Treatment naïve MNV secondary to nAMD in the study eye
  • Active subfoveal MNV or juxtafoveal/ extrafoveal MNV with a subfoveal component (where activity is defined as evidence of SRF, IRF, subretinal hyperreflective material, or leakage) identified by fluorescein angiography (FA) or spectral domain optical coherence tomography (SD-OCT), in the study eye, at the Screening Visit confirmed by the Reading Center
  • Demonstrated clinical response to aflibercept and functional stability in the study eye as confirmed by the Reading Center
  • BCVA between 25 and 78 ETDRS letters, inclusive (20/320-20/32 Snellen equivalent) in the study eye at the Screening Visit
  • CST less than or equal to 500 microns in the study eye at screening visit, confirmed by the central reading center

You may not qualify if:

  • Ocular Conditions:
  • MNV due to causes other than nAMD in either eye (Fibrosis, atrophy, or subretinal hemorrhage in the foveal central subfield (1 mm diameter))
  • History of retinal detachment in the study eye
  • History of or presence of active inflammation in either eye
  • Glaucoma or intraocular hypertension requiring more than 2 topical medications for control
  • Systemic Conditions and Considerations:
  • Major illness or major surgical procedure in the 28 days prior to the Screening Visit
  • Uncontrolled blood pressure
  • Acute coronary syndrome, myocardial infarction or coronary artery revascularization, cerebrovascular accident, transient ischemic attack within 6 months of the Screening Visit
  • History of autoimmune condition that may predispose to the development of uveitis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (100)

Barnet Dulaney Perkins Eye Center

Phoenix, Arizona, 85016, United States

Location

Retinal Research Institute, LLC

Scottsdale, Arizona, 85254, United States

Location

Retina Partners of Northwest Arkansas

Springdale, Arkansas, 72764, United States

Location

California Retina Consultants

Bakersfield, California, 93309, United States

Location

Retina Vitreous Associates Medical Group

Beverly Hills, California, 90211, United States

Location

The Retina Partners

Encino, California, 91436, United States

Location

Retina Associates of Southern California

Huntington Beach, California, 92647, United States

Location

Loma Linda University Faculty Medical Clinics

Loma Linda, California, 92354, United States

Location

Jules Stein Eye Institute

Los Angeles, California, 90095, United States

Location

Northern California Retina Vitreous Associates

Mountain View, California, 94040, United States

Location

Retina Consultants of San Diego

Poway, California, 92064, United States

Location

Kaiser Permanente-Riverside Medical Center

Riverside, California, 92505, United States

Location

Retinal Consultants Medical Group Inc

Sacramento, California, 95825, United States

Location

Retinal Consultants Medical Group Inc

Sacramento, California, 95840, United States

Location

Orange County Retina Medical Group

Santa Ana, California, 92705, United States

Location

California Retina Consultants - Santa Barbara

Santa Barbara, California, 93103, United States

Location

Bay Area Retina Associates

Walnut Creek, California, 94598, United States

Location

University of Colorado, Denver

Aurora, Colorado, 80045, United States

Location

Retina Consultants of Southern Colorado

Colorado Springs, Colorado, 80909, United States

Location

RSC Research, LLC

Denver, Colorado, 80210, United States

Location

Connecticut Eye Consultants

Danbury, Connecticut, 06810, United States

Location

Retina Group of Florida

Fort Lauderdale, Florida, 33308, United States

Location

Vitreo Retinal Associates

Gainesville, Florida, 34481, United States

Location

Florida Retina Institute - Jacksonville

Jacksonville, Florida, 32216, United States

Location

Florida Retina Consultants

Lakeland, Florida, 33805, United States

Location

Florida Retina Institute

Orlando, Florida, 32806, United States

Location

Retina Specialty Institute

Pensacola, Florida, 32503, United States

Location

Retina Associates of Sarasota

Sarasota, Florida, 34232, United States

Location

Retina Vitreous Associates of Florida

St. Petersburg, Florida, 33711, United States

Location

East Florida Eye Institute

Stuart, Florida, 34994, United States

Location

Southeast Retina Center

Augusta, Georgia, 30909, United States

Location

Georgia Retina PC

Marietta, Georgia, 30060, United States

Location

Retina Consultants of Hawaii

‘Aiea, Hawaii, 96701, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Retina Associates - Elmhurst

Elmhurst, Illinois, 60126, United States

Location

University Retina and Macula Associates, PC

Lemont, Illinois, 60439, United States

Location

Illinois Retina Associates

Oak Park, Illinois, 60304, United States

Location

Springfield Clinic

Springfield, Illinois, 62703, United States

Location

Midwest Eye Institute

Carmel, Indiana, 46290, United States

Location

Retina Associates of Kentucky

Lexington, Kentucky, 40509, United States

Location

Haik Humble Eye Center

West Monroe, Louisiana, 71291, United States

Location

Maine Eye Center

Portland, Maine, 04101, United States

Location

Wilmer Eye Institute John's Hopkins University

Baltimore, Maryland, 21287, United States

Location

Retina Group of Washington

Chevy Chase, Maryland, 20815, United States

Location

Cumberland Valley Retina Consultants PC

Hagerstown, Maryland, 21740, United States

Location

Mid Atlantic Retina Specialists - Hagerstown

Hagerstown, Maryland, 21740, United States

Location

MD Medical Research

Waldorf, Maryland, 20745, United States

Location

New England Retina Consultants

Springfield, Massachusetts, 01107, United States

Location

Mississippi Retina Associates

Madison, Mississippi, 39110, United States

Location

Deep Blue Retina Clinical Research

Southaven, Mississippi, 38671, United States

Location

The Retina Institute

St Louis, Missouri, 63128, United States

Location

Sierra Eye Associates

Reno, Nevada, 89502, United States

Location

Envision Ocular, LLC

Bloomfield, New Jersey, 07003, United States

Location

NJ Retina

Edison, New Jersey, 08820, United States

Location

NJ Retina

Teaneck, New Jersey, 07666, United States

Location

Eye Associates of New Mexico Vision Research Center

Albuquerque, New Mexico, 87109, United States

Location

Retina-Vitreous Surgeons of Central New York

Liverpool, New York, 13088, United States

Location

Vitreous Retina Macula Consultants of New York

New York, New York, 10022, United States

Location

Retina Associates of Western New York

Rochester, New York, 14620, United States

Location

Western Carolina Retinal Associate PA

Asheville, North Carolina, 28803, United States

Location

Duke Eye Center

Durham, North Carolina, 27705, United States

Location

North Carolina (NC) Retina Associates

Wake Forest, North Carolina, 27587, United States

Location

Atrium Health Wake Forest Baptist Medical Center

Winston-Salem, North Carolina, 27157, United States

Location

Piedmont Retina Specialists - Winston Salem Office

Winston-Salem, North Carolina, 27157, United States

Location

Retina Associates of Cleveland

Cleveland, Ohio, 44122, United States

Location

Retina Associates of Cleveland

Cleveland, Ohio, 44130, United States

Location

Cole Eye Institute

Cleveland, Ohio, 44195, United States

Location

Retina Vitreous Center

Edmond, Oklahoma, 73013, United States

Location

Verum Research, LLC

Eugene, Oregon, 97401, United States

Location

EyeHealth Northwest Peterkort

Portland, Oregon, 97225, United States

Location

Mid Atlantic Retina

Bethlehem, Pennsylvania, 18017, United States

Location

Erie Retina Research

Erie, Pennsylvania, 16507, United States

Location

The Scheie Eye Institute

Philadelphia, Pennsylvania, 19104, United States

Location

Charleston Neuroscience Center

Charleston, South Carolina, 29414, United States

Location

Charleston Neuroscience Institute

Ladson, South Carolina, 29456, United States

Location

Palmetto Retina Center

West Columbia, South Carolina, 29169, United States

Location

Black Hills Regional Eye Institute

Rapid City, South Dakota, 57701, United States

Location

Southeastern Retina Associates

Knoxville, Tennessee, 37763, United States

Location

Retina Research Institute of Texas

Abilene, Texas, 79606, United States

Location

Texas Retina Associates

Arlington, Texas, 76012, United States

Location

Austin Research Center for Retina

Austin, Texas, 78705, United States

Location

Austin Retina Associates

Austin, Texas, 78705, United States

Location

Austin Clinical Research

Austin, Texas, 78750, United States

Location

Retina & Vitreous of Texas, PLLC

Bellaire, Texas, 77401, United States

Location

Retina Consultants of Houston

Bellaire, Texas, 77401, United States

Location

Texas Retina Center

Houston, Texas, 77043, United States

Location

Retina Associates of South Texas PA

San Antonio, Texas, 78240, United States

Location

Retina Consultants of Texas San Antonio

San Antonio, Texas, 78240, United States

Location

RCTX - Westover Hills Retina Center

San Antonio, Texas, 78251, United States

Location

Retina Consultants of Texas

The Woodlands, Texas, 77384, United States

Location

Strategic Clinical Research Group, LLC

Willow Park, Texas, 76087, United States

Location

Retina Group of Washington

Fairfax, Virginia, 22031, United States

Location

Piedmont Eye Center

Lynchburg, Virginia, 24502, United States

Location

Retina Institute of Virginia

Richmond, Virginia, 23235, United States

Location

Eye Clinic of Wisconsin

Wausau, Wisconsin, 54403, United States

Location

Calgary Retina Consultants

Calgary, Alberta, T2H 0C8, Canada

Location

Retina Surgical Associates

New Westminster, British Columbia, V3L 5H1, Canada

Location

St. Michaels Hospital

North York, Ontario, M5B 1W8, Canada

Location

Retina Institute of Ottawa, Inc.

Ottawa, Ontario, K2B 7E9, Canada

Location

Krembil Neuroscience Centre

Toronto, Ontario, M5T 2S8, Canada

Location

Related Links

MeSH Terms

Conditions

Macular DegenerationWet Macular Degeneration

Interventions

afliberceptInjections

Condition Hierarchy (Ancestors)

Retinal DegenerationRetinal DiseasesEye Diseases

Intervention Hierarchy (Ancestors)

Drug Administration RoutesDrug TherapyTherapeutics

Study Officials

  • Hersh Patel

    4D Molecular Therapeutics

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 4, 2025

First Posted

March 7, 2025

Study Start

March 3, 2025

Primary Completion (Estimated)

June 1, 2027

Study Completion (Estimated)

June 1, 2028

Last Updated

March 25, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will share

Data obtained through this study may be provided, after deidentification, to qualified researchers with academic interest in AMD in compliance with ICMJE policy. Data or samples shared will be coded, with no Protected Health Information included. Additionally, descriptions of the study protocol, Statistical Analysis Plan (SAP), informed consent and clinical study report may be shared publicly. Approval of the request and execution of all applicable agreements (i.e. a material transfer agreement) are prerequisites to the sharing of data with the requesting party. Data requests can be submitted starting after final Clinical Study Report and the data will be made accessible for a duration determined by the Sponsor, and in accordance with ICMJE policy. Access to trial IPD can be requested by qualified researchers engaging in independent scientific research, and will be provided following review and approval of a research proposal and SAP and execution of a Data Sharing Agreement (DSA).

Locations