NCT06471946

Brief Summary

The goal of this phase 1/2 trial is to test the safety and efficacy of Venetoclax Plus Azacytidine Conditioning Regimen Allo-HSCT in treating patients with higher-risk MDS.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
54

participants targeted

Target at P50-P75 for phase_1

Timeline
53mo left

Started Oct 2024

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress27%
Oct 2024Sep 2030

First Submitted

Initial submission to the registry

June 17, 2024

Completed
7 days until next milestone

First Posted

Study publicly available on registry

June 24, 2024

Completed
3 months until next milestone

Study Start

First participant enrolled

October 1, 2024

Completed
4.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2029

Expected
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2030

Last Updated

October 1, 2024

Status Verified

September 1, 2024

Enrollment Period

4.9 years

First QC Date

June 17, 2024

Last Update Submit

September 28, 2024

Conditions

Outcome Measures

Primary Outcomes (1)

  • Overall Survival

    OS was defined as time from diagnosis to death from any cause or the last follow-up

    3 year

Secondary Outcomes (4)

  • Progression Free Survival (PFS)

    3 year

  • Incidence of acute GVHD and chronic GVHD

    3 year

  • Non-relapse mortality (NRM)

    3 year

  • Graft-versus-host disease (GVHD)-free relapse-free survival(GRFS)

    3 year

Study Arms (1)

Venetoclax Plus Azacytidine Conditioning Regimen Allo-HSCT

EXPERIMENTAL

Patients were treated by Venetoclax Plus Azacytidine Conditioning Regimen Allo-HSCT

Drug: Venetoclax Plus Azacytidine Conditioning Regimen Allo-HSCT

Interventions

Patients were treated by VA Conditioning Regimen Allo-HSCT: Venetoclax 100mg po qd d1, 200mg po qd d2, 400mg po qd d3-14; Azacytidine 75 mg/m2 subcutaneous injection qd d1-7, donor stem cells infused from d9

Also known as: VA Conditioning Regimen Allo-HSCT
Venetoclax Plus Azacytidine Conditioning Regimen Allo-HSCT

Eligibility Criteria

Age70 Years+
Sexall
Healthy VolunteersNo
Age GroupsOlder Adult (65+)

You may qualify if:

  • The patient should, in the investigator's opinion, be able to meet all clinical trial requirements.
  • The patient is willing and able to adhere to the study visit schedule and other protocol requirements.
  • The patient should be diagnosed with higher risk MDS according to the standard criteria of the World Health Organization (WHO).

You may not qualify if:

  • Active or uncontrolled infections requiring systemic treatment within 14 days before enrollment.
  • Any instability of systemic disease, including but not limited to severe cardiac, liver, kidney, or metabolic disease need therapy.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Navy General Hospital

Beijing, Beijing Municipality, 100048, China

RECRUITING

MeSH Terms

Interventions

venetoclax

Study Officials

  • Liren Qian, PhD

    Navy General Hospital, Beijing

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Liren Qian, PhD

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Vice Director

Study Record Dates

First Submitted

June 17, 2024

First Posted

June 24, 2024

Study Start

October 1, 2024

Primary Completion (Estimated)

September 1, 2029

Study Completion (Estimated)

September 1, 2030

Last Updated

October 1, 2024

Record last verified: 2024-09

Locations