NCT06202027

Brief Summary

The objective of this post-marketing surveillance (PMS) study is to assess the safety and effectiveness of CRYSVITA injection 10, 20, and 30mg, equivalent to in routine clinical settings

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
100

participants targeted

Target at P50-P75 for all trials

Timeline
64mo left

Started Aug 2023

Longer than P75 for all trials

Geographic Reach
1 country

13 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress35%
Aug 2023Jul 2031

Study Start

First participant enrolled

August 11, 2023

Completed
5 months until next milestone

First Submitted

Initial submission to the registry

January 2, 2024

Completed
9 days until next milestone

First Posted

Study publicly available on registry

January 11, 2024

Completed
7.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 16, 2031

Expected
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

July 16, 2031

Last Updated

August 29, 2025

Status Verified

August 1, 2025

Enrollment Period

7.9 years

First QC Date

January 2, 2024

Last Update Submit

August 28, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • safety (Special situation, adverse event, symptom, or disease occuring during treatment with a drug)

    Investigators have to record all events (i.e., all AEs and special situations) in CRFs including undesirable medical findings obtained during the medical examination as well as spontaneous reports from subjects. All AEs occurring for at least 4 weeks after the last dose of CRYSVITA® should be included in this study

    4 weeks after follow up

Secondary Outcomes (2)

  • Serum Phosphorus Concentration

    24 weeks

  • 1,25-Dihydroxyvitamin D

    24 weeks

Interventions

FGF23-related hypophosphataemic rickets and osteomalacia

Eligibility Criteria

Age1 Day+
Sexall
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

FGF23-related hypophosphataemic rickets and osteomalacia

You may qualify if:

  • Patients who have been started on CRYSVITA® in accordance with the approved label in Korea
  • Those (or his/her legal guardian) who have agreed in writing to participate in the survey. Children who have obtained a written consent of his/her legal guardian about participation in this survey. In case of pediatric patient, explain sufficiently what you think the patient can understand. In this case, the legal guardian may provide supplementary explanations of the survey.

You may not qualify if:

  • Patients for whom Burosumab is contraindicated according local label of CRYSVITA®
  • Patients who intend to use this drug for other purposes
  • Patients who participated in pre-market clinical trials with CRYSVITA® (Consecutive investigation method ONLY)
  • Patients who have been taking this drug before the starting day of this study (Consecutive investigation method ONLY)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Wonju Severance Christian Hospital

Wŏnju, Gangwon-do, 26426, South Korea

RECRUITING

Ajou University Hospital

Suwon, Gyeonggi-do, 16499, South Korea

RECRUITING

Yangsan Pusan National University Hospital

Yangsan, Gyeongsangnam-do, 50612, South Korea

RECRUITING

Chonnam National University Hospital

Gwangju, Jeollanam-do, 61469, South Korea

RECRUITING

Chungnam National University Sejong Hospital

Sejong, Sejong Special Self-Governing City, 30099, South Korea

RECRUITING

Inje University Busan Paik Hospital

Busan, 47392, South Korea

RECRUITING

Pusan National University Hospital

Busan, 49241, South Korea

RECRUITING

Seoul National University Hospital

Seoul, 03080, South Korea

RECRUITING

Seoul National University Hospital

Seoul, 03080, South Korea

RECRUITING

Seoul National University Hospital

Seoul, 03080, South Korea

RECRUITING

Severance Hospital

Seoul, 03722, South Korea

RECRUITING

Severance Hospital

Seoul, 03722, South Korea

RECRUITING

Korea University Guro Hospital

Seoul, 08308, South Korea

RECRUITING

MeSH Terms

Conditions

Osteomalacia

Condition Hierarchy (Ancestors)

RicketsBone Diseases, MetabolicBone DiseasesMusculoskeletal DiseasesMetabolic DiseasesNutritional and Metabolic DiseasesCalcium Metabolism DisordersVitamin D DeficiencyAvitaminosisDeficiency DiseasesMalnutritionNutrition Disorders

Study Officials

  • HaeMi Park

    Kyowa Kirin Korea Co., Ltd.

    STUDY DIRECTOR

Central Study Contacts

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Target Duration
24 Weeks
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 2, 2024

First Posted

January 11, 2024

Study Start

August 11, 2023

Primary Completion (Estimated)

June 16, 2031

Study Completion (Estimated)

July 16, 2031

Last Updated

August 29, 2025

Record last verified: 2025-08

Locations