NCT06198413

Brief Summary

The goal of this study is to evaluate the safety and efficacy of LX102 gene therapy for nAMD.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
12

participants targeted

Target at below P25 for phase_1

Timeline
32mo left

Started Feb 2023

Longer than P75 for phase_1

Geographic Reach
1 country

3 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress55%
Feb 2023Jan 2029

Study Start

First participant enrolled

February 27, 2023

Completed
10 months until next milestone

First Submitted

Initial submission to the registry

December 25, 2023

Completed
16 days until next milestone

First Posted

Study publicly available on registry

January 10, 2024

Completed
12 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 26, 2024

Completed
4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2029

Expected
Last Updated

July 1, 2025

Status Verified

June 1, 2025

Enrollment Period

1.8 years

First QC Date

December 25, 2023

Last Update Submit

June 26, 2025

Conditions

Keywords

Age-related macular degenerationAMDNeovascular AMDNeovascular age-related macular degeneration

Outcome Measures

Primary Outcomes (2)

  • Incidence of dose-limiting toxicity (DLT)

    Incidence of dose-limiting toxicity (DLT) following LX102 subretinal injection at different doses

    4 weeks

  • Incidence of adverse events (AEs) and serious adverse events (SAEs)

    Incidence of ocular and systemic adverse events (AEs) and serious adverse events (SAEs) following LX102 subretinal injection

    52 weeks

Secondary Outcomes (5)

  • Mean change in BCVA from Baseline

    12 weeks, 36 weeks 52 weeks

  • Mean change in Central Subfield Thickness (CST) from Baseline

    12 weeks, 36 weeks 52 weeks

  • Mean time from LX102 administration to anti-VEGF rescue injection for the first time

    52 weeks

  • Percentage of participants requiring anti-VEGF rescue injection

    52 weeks

  • Mean number of anti-VEGF rescue injections

    52 weeks

Study Arms (3)

LX102 Dose 1

EXPERIMENTAL

Low dose of LX102

Genetic: LX102 subretinal injection

LX102 Dose 2

EXPERIMENTAL

Mid dose of LX102

Genetic: LX102 subretinal injection

LX102 Dose 3

EXPERIMENTAL

High dose of LX102

Genetic: LX102 subretinal injection

Interventions

LX102: AAV-based gene therapy comprised of codon-optimized sequence encoding VEGF-trap

LX102 Dose 1LX102 Dose 2LX102 Dose 3

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Willing to sign the informed consent, and willing to attend follow-up visits.
  • Age ≥ 50
  • Diagnosis of active CNV secondary to neovascular AMD
  • BCVA ETDRS letters between 5 and 63
  • Subjects must have received a minimum of 2 injections within 6 months prior to screening
  • Demonstrated a meaningful response to anti-VEGF therapy

You may not qualify if:

  • CNV or macular edema in the study eye secondary to diseases other than nAMD
  • Retinal detachment, uveitis, uncontrolled glaucoma in the study eye, or any condition preventing visual acuity improvement
  • Acute coronary syndrome, myocardial infarction or coronary artery revascularization, CVA, TIA in the last 6 months
  • Uncontrolled hypertension defined as average SBP ≥160 mmHg or an average DBP ≥100 mmHg
  • Uncontrolled diabetes defined as HbA1c \>7.5%

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Anhui Provincial Hospital

Hefei, Anhui, China

Location

Zhejiang University Eye Hospital

Hangzhou, Zhejiang, China

Location

Shanghai General Hospital

Shanghai, China

Location

MeSH Terms

Conditions

Macular Degeneration

Condition Hierarchy (Ancestors)

Retinal DegenerationRetinal DiseasesEye Diseases

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 25, 2023

First Posted

January 10, 2024

Study Start

February 27, 2023

Primary Completion

December 26, 2024

Study Completion (Estimated)

January 1, 2029

Last Updated

July 1, 2025

Record last verified: 2025-06

Data Sharing

IPD Sharing
Will not share

Locations