NCT05916469

Brief Summary

The goal of this multicenter prospective observational study and registry of U.S. adolescents and young adults with heritable bleeding disorders is to determine the bleeding outcomes, satisfaction, hemostatic parameter changes, and patient reported quality of life after 6 months of use of either of two commonly used hormonal treatments for menstrual suppression - levonorgestrel intrauterine device (LNG-IUD) and norethindrone acetate (NETA). Under this application the study will compare the two treatments and compare outcomes after LNG-IUD treatment results to a control group without a bleeding disorder, with the goal of determining the benefits and expected outcomes of these treatment options for this population.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
300

participants targeted

Target at P75+ for all trials

Timeline
36mo left

Started Sep 2025

Typical duration for all trials

Geographic Reach
1 country

9 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress20%
Sep 2025Jun 2029

First Submitted

Initial submission to the registry

June 14, 2023

Completed
9 days until next milestone

First Posted

Study publicly available on registry

June 23, 2023

Completed
2.3 years until next milestone

Study Start

First participant enrolled

September 24, 2025

Completed
3.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2028

Expected
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2029

Last Updated

December 17, 2025

Status Verified

December 1, 2025

Enrollment Period

3.2 years

First QC Date

June 14, 2023

Last Update Submit

December 9, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Treatment success rate

    Proportion with pictorial blood loss assessment score \<50 points

    6 months

Secondary Outcomes (6)

  • Median Pictorial Blood Assessment Chart (PBAC) score

    6 months

  • Patient-reported treatment success rate

    6 months

  • Change in Adolescent Menstrual Bleeding Questionnaire (aMBQ) score

    Baseline to 6 months

  • Change in Patient-Reported Outcomes Measurement Information System (PROMIS-25 or PROMIS-29) scores

    Baseline to 6 months

  • Change in serum ferritin after treatment

    Baseline to 6 months

  • +1 more secondary outcomes

Study Arms (3)

Bleeding disorder using LNG-IUD

Adolescents and young adults ages 10-24 with diagnosed bleeding disorder planning use of LNG-IUD.

Drug: Levonorgestrel Intrauterine System

Non-bleeding disorder using LNG-IUD

Adolescents and young adults ages 10-24 without diagnosed bleeding disorder planning use of LNG-IUD.

Drug: Levonorgestrel Intrauterine System

Bleeding disorder using NETA

Adolescents and young adults ages 10-24 with diagnosed bleeding disorder planning use of NETA.

Drug: Norethindrone Acetate

Interventions

52 mg levonorgestrel intrauterine system

Also known as: Mirena, Liletta
Bleeding disorder using LNG-IUDNon-bleeding disorder using LNG-IUD

norethindrone acetate 5 mg daily

Also known as: Aygestin
Bleeding disorder using NETA

Eligibility Criteria

Age10 Years - 24 Years
Sexfemale
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodNon-Probability Sample
Study Population

Adolescents and young adults ages 10-24 with and without a heritable bleeding disorder who receive medical care for heavy menstrual bleeding at a participating U.S. clinical site. All clinical sites participate in a national consortium of interdisciplinary hematology-gynecology clinics.

You may qualify if:

  • Post-menarcheal
  • Ages 10-24
  • Decision to initiate a trial of progestin therapy with either LNG-IUD or NETA
  • Able to provide assent and written informed consent by one parent (ages \<18) or written informed consent (age 18+)
  • Must meet trial criteria for heavy menstrual bleeding
  • Must meet trial criteria for a bleeding disorder or have minimum workup to rule out bleeding disorder

You may not qualify if:

  • Pregnant or seeking pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

Stanford

Palo Alto, California, 94304, United States

NOT YET RECRUITING

Colorado Anschutz Medical Campus

Aurora, Colorado, 80045, United States

NOT YET RECRUITING

Emory

Atlanta, Georgia, 30322, United States

NOT YET RECRUITING

University of Michigan Medicine

Ann Arbor, Michigan, 48109, United States

NOT YET RECRUITING

Children's Mercy

Kansas City, Missouri, 64108, United States

NOT YET RECRUITING

Oregon Health & Science University

Portland, Oregon, 97239, United States

RECRUITING

Penn State Health

Hershey, Pennsylvania, 17003, United States

NOT YET RECRUITING

University of Washington

Seattle, Washington, 98101, United States

NOT YET RECRUITING

Seattle Children's Hospital

Seattle, Washington, 98105, United States

NOT YET RECRUITING

MeSH Terms

Conditions

MenorrhagiaHemostatic Disordersvon Willebrand Diseases

Interventions

LevonorgestrelNorethindrone Acetate

Condition Hierarchy (Ancestors)

Uterine HemorrhageUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsMenstruation DisturbancesVascular DiseasesCardiovascular DiseasesHemorrhagic DisordersHematologic DiseasesHemic and Lymphatic DiseasesBlood Coagulation Disorders, InheritedBlood Coagulation DisordersCoagulation Protein DisordersBlood Platelet DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

NorgestrelNorpregnenesNorpregnanesNorsteroidsSteroidsFused-Ring CompoundsPolycyclic CompoundsNorethindrone

Study Officials

  • Maureen Baldwin, MD MPH

    Oregon Health and Science University

    PRINCIPAL INVESTIGATOR
  • Allison Wheeler

    University of Washington

    PRINCIPAL INVESTIGATOR

Central Study Contacts

OHSU Women's Health Research Unit

CONTACT

Maureen Baldwin, MD MPH

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Target Duration
5 Years
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor of Ob/Gyn

Study Record Dates

First Submitted

June 14, 2023

First Posted

June 23, 2023

Study Start

September 24, 2025

Primary Completion (Estimated)

December 1, 2028

Study Completion (Estimated)

June 1, 2029

Last Updated

December 17, 2025

Record last verified: 2025-12

Data Sharing

IPD Sharing
Will share

This study will collect clinical, laboratory, and survey data from participants ages 10-24 at multiple academic clinical sites. Participant-level clinical data will be preserved through deposition of the data in a controlled access public repository. We will make our scientific data as widely and freely available as possible while safeguarding the privacy of participants (de-identified prior to repository submission) and protecting confidential and proprietary data.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
Scientific data will be shared as soon as possible following study participant completion. Scientific data included in published manuscripts will be available at the time of publication; all other generated scientific data will be shared no later than the end of the award. The study data will be stored in the repository indefinitely, for at least 5 years.
Access Criteria
The study datasets will be collected with the following informed consent: The dataset can only be used for studying health, medical, or biomedical conditions and does not include the study of population origins or ancestry. We will also require all individuals requesting data to enter into a data sharing agreement that: 1) acknowledges the data will be stripped of identifying markers and identification; 2) acknowledges that these data will only be used for research purposes; and 3) requests investigators to reference the seminal publication describing data collection. The dataset can only be used for studying health, medical or biomedical conditions and does not include the study of population origins or ancestry. The requesting institution's IRB or equivalent body must approve the requested use.

Locations