NCT05809934

Brief Summary

A Study to Evaluate the Efficacy, Safety and Tolerability of AZD2693 given by subcutaneous injection in adult participants with non-cirrhotic non-alcoholic steatohepatitis with fibrosis and who are carriers of the PNPLA3 148M Risk Allele

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
220

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2023

Geographic Reach
22 countries

164 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 23, 2023

Completed
20 days until next milestone

Study Start

First participant enrolled

March 15, 2023

Completed
28 days until next milestone

First Posted

Study publicly available on registry

April 12, 2023

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 14, 2025

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 29, 2025

Completed
Last Updated

October 28, 2025

Status Verified

October 1, 2025

Enrollment Period

2.3 years

First QC Date

February 23, 2023

Last Update Submit

October 27, 2025

Conditions

Keywords

Nonalcoholic SteatohepatitisNASHfatty liver diseaseNon alcoholic fatty liverliver fibrosisPNPLA3 148M Risk AlleleNon Cirrhotic

Outcome Measures

Primary Outcomes (1)

  • Proportion of participants achieving NASH resolution without worsening of fibrosis based on histology after 52 weeks treatment

    To assess the effect of AZD2693 versus placebo on histological resolution of NASH in participants with non-cirrhotic NASH with fibrosis and PNPLA3 risk allele carriers after 52 weeks

    after 52 weeks

Secondary Outcomes (3)

  • Proportion of participants with at least one stage of liver fibrosis improvement with no worsening of NASH based on biopsy after 52 weeks treatment

    after 52 weeks

  • Proportion of participants with ≥ 2-point improvement from baseline in NAS based on biopsy after 52 weeks treatment

    after 52 weeks

  • Proportion of participants with improvement in fibrosis by at least one stage based on biopsy after 52 weeks treatment

    after 52 weeks

Other Outcomes (2)

  • Number of participants with Adverse Events/Serious Adverse Events (AEs/SAEs) and abnormal laboratory test results

    64 weeks

  • Number of participants with Adverse Events/Serious Adverse Events (AEs/SAEs) and abnormal clinical test results

    64 weeks

Study Arms (3)

AZD2693 dose 1

EXPERIMENTAL

Participants will receive AZD2693 dose 1

Drug: AZD2693

AZD2693 dose 2

EXPERIMENTAL

Participants will receive AZD2693 dose 2

Drug: AZD2693

Placebo

PLACEBO COMPARATOR

Participants in this arm will receive placebo

Other: Placebo

Interventions

AZD2693 solution SC once per month

AZD2693 dose 1AZD2693 dose 2
PlaceboOTHER

Sodium chloride 0.9% solution SC once per month

Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants are eligible to be included in the study only if all the following criteria apply:
  • Age
  • Participant must be 18 to 75 years of age (inclusive) at the time of signing the informed consent.
  • Type of Participant and Disease Characteristics
  • Participants who are carriers for the PNPLA3 rs738409 148M risk allele.
  • Participants with histological evidence of NASH based on central pathologist evaluation of a liver biopsy obtained up to 6 months before randomisation, or during screening, fulfilling both criteria:
  • Definitive NASH with NAS ≥ 4 with ≥ 1 in each component (ie, steatosis, lobular inflammation, and ballooning).
  • <!-- -->
  • Presence of fibrosis stage F2 or F3 according to the NASH CRN fibrosis staging system based on central pathologist evaluation.

You may not qualify if:

  • Participants are excluded from the study if any of the following criteria apply:
  • Medical Conditions
  • Liver disease of other aetiologies (eg, alcoholic steatohepatitis; drug-induced, viral or autoimmune hepatitis; primary biliary cirrhosis; primary sclerosing cholangitis; hemochromatosis; alpha-1 antitrypsin deficiency; Wilson's disease)
  • History of cirrhosis and/or hepatic decompensation, including ascites, hepatic encephalopathy, or variceal bleeding.
  • Historical persistent or pre-existing renal disease marked by eGFR \< 40 mL/min/1.73 m2 (as defined by Kidney Disease Improving Global Outcomes guidelines).
  • Confirmed platelet count outside the normal range at the screening visit.
  • Any of the following confirmed at the screening visit:
  • ALT \> 5.0 × ULN
  • TBL \> 1.5 mg/dL (TBL \> 1.5 mg/dL is allowed if conjugated bilirubin is \< 1.5 × ULN)
  • INR \> 1.3
  • ALP \> 1.5 × ULN (unless the ALP elevation is not from hepatic origin as determined by a bone-specific ALP)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (164)

Research Site

Chandler, Arizona, 85224, United States

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Peoria, Arizona, 85381, United States

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Surprise, Arizona, 85378, United States

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Tucson, Arizona, 85712, United States

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Tucson, Arizona, 85715, United States

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Gardena, California, 90247, United States

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La Mesa, California, 91942, United States

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Lancaster, California, 93534, United States

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Los Angeles, California, 90057, United States

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Montclair, California, 91763, United States

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Orange, California, 92868, United States

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Rialto, California, 92377, United States

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Santa Ana, California, 92704, United States

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Boca Raton, Florida, 33434, United States

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Hialeah, Florida, 33016, United States

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Jacksonville, Florida, 32216, United States

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Port Orange, Florida, 32127, United States

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Winter Park, Florida, 32792, United States

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Marietta, Georgia, 30060, United States

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Topeka, Kansas, 66606, United States

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Detroit, Michigan, 48202, United States

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Las Vegas, Nevada, 89101, United States

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Westlake, Ohio, 44145, United States

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Chickasha, Oklahoma, 73018, United States

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Hershey, Pennsylvania, 17033, United States

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Summerville, South Carolina, 29485, United States

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Cordova, Tennessee, 38018, United States

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Austin, Texas, 78757, United States

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Brownsville, Texas, 78520, United States

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Denison, Texas, 75020, United States

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Edinburg, Texas, 78539, United States

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Houston, Texas, 77030, United States

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Red Oak, Texas, 75154, United States

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San Antonio, Texas, 78229, United States

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Sugar Land, Texas, 77479, United States

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Richmond, Virginia, 23249, United States

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Seattle, Washington, 98105, United States

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CABA, C1119ACN, Argentina

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CABA, C1426, Argentina

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Ciudad de Buenos Aires, 1280, Argentina

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Córdoba, X5000EPU, Argentina

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La Plata, 1900, Argentina

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Mar del Plata, B7600GNY, Argentina

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San Juan Bautista, 1888, Argentina

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Botucatu, 18618-687, Brazil

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Porto Alegre, 90035-000, Brazil

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Porto Alegre, 90035-903, Brazil

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Salvador, 40110-160, Brazil

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São José do Rio Preto, 15090-000, Brazil

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São Paulo, 05403-000, Brazil

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Santiago, 7620157, Chile

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Santiago, 8380456, Chile

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Santiago, Chile

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Valdivia, 5110683, Chile

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Baotou, 014010, China

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Beijing, 100057, China

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Beijing, 100069, China

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Chengdu, 610072, China

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Fuzhou, 350005, China

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Guangzhou, 510515, China

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Hangzhou, 310003, China

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Liaocheng, 252000, China

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Nanchang, 330000, China

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Qingdao, 266011, China

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Shanghai, 200025, China

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Shanghai, 200080, China

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Shanghai, 200092, China

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Shenyang, 110004, China

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Taiyuan, 030001, China

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Wenzhou, 325000, China

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Xi'an, 710061, China

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Xuzhou, 221000, China

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Zhenjiang, 212021, China

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Cartagena, 130013, Colombia

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Konstanz, 78464, Germany

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Magdeburg, Germany

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Mainz, 55131, Germany

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Münster, 48149, Germany

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Hong Kong, 999077, Hong Kong

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Shatin, Hong Kong

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Hyderabad, 500072, India

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Jaipur, 302001, India

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Jaipur, 302018, India

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Punjab, 160062, India

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Surat, 395009, India

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Milan, 20122, Italy

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Palermo, 90127, Italy

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Roma, 00128, Italy

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Rome, 00168, Italy

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Torino, 10126, Italy

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Bunkyō City, 113-8655, Japan

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Fukui-shi, 918-8503, Japan

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Fukuoka, 810-0065, Japan

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Gifu, 500-8513, Japan

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Kagoshima, 890-8520, Japan

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Kawasaki-shi, 215-0026, Japan

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Kobe, 650-0017, Japan

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Kumamoto, 860-8556, Japan

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Kure-shi, 737-0023, Japan

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Kurume-shi, 830-0011, Japan

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Kyoto, 602-8566, Japan

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Minatoku, 105-8470, Japan

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Nagoya, 460-0001, Japan

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Okayama, 700-8505, Japan

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Omura-shi, 856-8562, Japan

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Osaka, 545-8586, Japan

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Ōita, 870-0837, Japan

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Saga, 849-8501, Japan

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Shinjuku-ku, 160-0023, Japan

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Shinjuku-ku, 160-8582, Japan

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Shinjuku-ku, 162-8655, Japan

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Takasaki-shi, 370-0829, Japan

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Tsu, 514-8507, Japan

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Yokohama, 236-0004, Japan

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Yokohama, 245-8575, Japan

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Kota Kinabalu, 88586, Malaysia

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Kuala Lumpur, 56000, Malaysia

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Kuala Lumpur, 59100, Malaysia

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Pulau Pinang, 10450, Malaysia

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Seremban, 70300, Malaysia

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Acapulco, 39670, Mexico

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Guadalajara, 44340, Mexico

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Mexico City, 03330, Mexico

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Mexico City, 06700, Mexico

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Torreón, 27000, Mexico

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Veracruz, 91851, Mexico

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Xalapa, 91020, Mexico

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Chorrillos, Lima 9, Peru

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Lima, 15023, Peru

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Lima, 15036, Peru

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Lima, 15046, Peru

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Cebu, 6000, Philippines

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Puerto Princesa City, 5300, Philippines

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Roxas City, 5800, Philippines

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San Fernando City, 2000, Philippines

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Singapore, 119074, Singapore

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Singapore, 169608, Singapore

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Singapore, 308433, Singapore

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Junggu, 41944, South Korea

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Seoul, 03080, South Korea

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Seoul, 06351, South Korea

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A Coruña, 15006, Spain

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Almería, 04009, Spain

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Lleida, 25198, Spain

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Málaga, 29010, Spain

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Zaragoza, 50009, Spain

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Kaohsiung City, 80756, Taiwan

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Tainan, 70403, Taiwan

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Taipei, 10002, Taiwan

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Taipei, 112, Taiwan

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Taoyuan District, 333, Taiwan

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Bangkok, 10330, Thailand

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Bangkok, 10400, Thailand

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Bangkok, 10700, Thailand

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Hat Yai, 90110, Thailand

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Khon Kaen, 40002, Thailand

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Adana, 01060, Turkey (Türkiye)

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Antalya, 07059, Turkey (Türkiye)

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Bursa, 16059, Turkey (Türkiye)

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Eskişehir, 26480, Turkey (Türkiye)

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Izmir, 35340, Turkey (Türkiye)

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Rize, 530020, Turkey (Türkiye)

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Ho Chi Minh City, 700000, Vietnam

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Ho Chi Minh City, 70000, Vietnam

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MeSH Terms

Conditions

Non-alcoholic Fatty Liver DiseaseLiver Cirrhosis

Condition Hierarchy (Ancestors)

Fatty LiverLiver DiseasesDigestive System DiseasesFibrosisPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Quadruple (Participant, Care Provider, Investigator, Outcomes Assessor)
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Randomised, Double-blind, Placebo-controlled, Multi-centre Phase 2b Study
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 23, 2023

First Posted

April 12, 2023

Study Start

March 15, 2023

Primary Completion

July 14, 2025

Study Completion

September 29, 2025

Last Updated

October 28, 2025

Record last verified: 2025-10

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the deidentified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
More information

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