NCT05791708

Brief Summary

This is a multinational, multi-center, observational, prospective, longitudinal disease registry designed to collect data on participants with cold agglutinin disease (CAD) or cold agglutinin syndrome (CAS). Among them, a minimum of 30 patients with CAD treated with sutimlimab are expected to take part in the sutimlimab cohort study. Patients with CAD who have been enrolled in previous sutimlimab clinical trials (e.g., BIVV009-01/LTS16214 \[NCT02502903,CAD patients\], BIVV009-03/EFC16215 \[NCT03347396\], and BIVV009-04/EFC16216 \[NCT03347422\]) and who either completed or discontinued the corresponding clinical trial are eligible to participate in the registry.

Trial Health

82
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
429

participants targeted

Target at P75+ for all trials

Timeline
30mo left

Started Dec 2019

Longer than P75 for all trials

Geographic Reach
8 countries

68 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress72%
Dec 2019Nov 2028

Study Start

First participant enrolled

December 12, 2019

Completed
3.2 years until next milestone

First Submitted

Initial submission to the registry

February 15, 2023

Completed
1 month until next milestone

First Posted

Study publicly available on registry

March 30, 2023

Completed
5.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 2, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 2, 2028

Last Updated

April 22, 2026

Status Verified

April 1, 2026

Enrollment Period

8.9 years

First QC Date

February 15, 2023

Last Update Submit

April 17, 2026

Conditions

Outcome Measures

Primary Outcomes (13)

  • Patterns of CAD and CAS disease characteristics

    CAD or CAS characteristics at diagnosis, enrollment, and during follow up (e.g., criteria used for diagnosis, symptoms, laboratory results) will be described.

    Up to 6 years

  • Number of participants with CAD or CAS complications

    Thromboembolic events (venous, arterial or cerebral), deaths related to CAD or CAS, other CAD/CAS complications (e.g., acute hemolytic crisis, hemolysis-related complications), and other comorbid conditions occurring before enrollment, at enrollment, and during follow up will be described.

    Up to 6 years

  • Patterns of use of CAD and CAS treatments

    CAD or CAS treatments received before enrollment, at enrollment, and during the follow up period will be summarized. CAD or CAS symptoms and complications, autoimmune disorders or lymphoproliferative disorders, physician assessment of treatment status, and changes in laboratory results will be described by CAD or CAS treatments.

    Up to 6 years

  • Number of participants with health-resource utilization

    Health resource utilization may include hospitalizations (including length of stay), outpatient visits, emergency room visits, specific transfusion visits, nursing home/rehabilitation center stays, and home healthcare visits during registry follow-up period

    Up to 6 years

  • Cold Agglutinin Disease Symptoms and Impact Questionnaire (CAD-SIQ)

    Up to 6 years

  • Functional Assessment of Chronic Illness Therapy-Fatigue (FACIT-Fatigue)

    Up to 6 years

  • 36-Item Short Form Survey Instrument (SF-36) v2

    Up to 6 years

  • Sutimlimab cohort: Sutimlimab treatment patterns

    Sutimlimab dosing information, reasons for dose adjustments, reasons for discontinuation will be described.

    Up to 6 years

  • Sutimlimab cohort: Number of participants with adverse events, serious adverse events, adverse events of special interests (AESIs), other events of interests (e.g., Treatment emergent)

    Up to 6 years

  • Sutimlimab cohort: change from baseline in hemoglobin

    From baseline up to 6 years

  • Sutimlimab cohort: change from baseline in bilirubin

    From baseline up to 6 years

  • Sutimlimab cohort: change from baseline in Lactate dehydrogenase (LDH)

    From baseline up to 6 years

  • Sutimlimab cohort: number of blood cells transfusions

    Up to 6 years

Study Arms (2)

cold agglutinin disease (CAD)

Patient with a diagnosis of CAD as per investigator judgment based on the diagnosis criteria listed in study protocol. In addition, this group includes a cohort of CAD patients treated with sutimlimab

Drug: Sutimlimab

cold agglutinin syndrome (CAS)

Patient with a diagnosis of CAS as per investigator judgment based on the diagnosis criteria listed in study protocol

Interventions

CAD patients in Sutimlimab cohort must be treated according to routine clinical practice

cold agglutinin disease (CAD)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

All patients with CAD or CAS will be eligible, regardless of the type of CAD or CAS-specific therapy they are receiving. In addition, the Cadence registry will include a sutimlimab cohort study whose objective is to assess the safety and the effectiveness of sutimlimab in patients with CAD in a real-world setting.

You may qualify if:

  • Patient aged ≥18 years
  • Patient able to understand the purpose of the study and who (or whose legally authorized representative) provided signed and dated informed consent and authorization to use protected health information in accordance with national and local subject privacy regulations
  • Patient with a diagnosis of CAD or CAS as per Investigator judgment based on the diagnosis criteria listed in study protocol

You may not qualify if:

  • Patient with mixed warm and cold autoimmune hemolytic anemia, or warm autoimmune hemolytic anemia
  • Patient actively participating in a CAD or CAS interventional clinical trial. After a patient completes participation in said trial, he/she may be eligible for enrollment in this registry.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (68)

University of Alabama at Birmingham Site Number : 1230

Birmingham, Alabama, 35205, United States

Location

SLO Oncology and Hematology Site Number : 1235

San Luis Obispo, California, 93401, United States

Location

Mission Hope Medical Oncology Site Number : 1241

Santa Maria, California, 93454, United States

Location

MedStar Georgetown University Hospital / Lombardi Comprehensive Cancer Center Site Number : 1208

Washington D.C., District of Columbia, 20007, United States

Location

Piedmont Cancer Institute, P.C Site Number : 1226

Atlanta, Georgia, 30290, United States

Location

Orchard Heathcare Research Inc. Site Number : 1202

Skokie, Illinois, 60077, United States

Location

Siouxland Regional Cancer Center dba June E. Nylen Cancer Center Site Number : 1220

Sioux City, Iowa, 51101, United States

Location

Reliant Medical Group Site Number : 1205

Worcester, Massachusetts, 01608, United States

Location

Henry Ford Hospital Site Number : 1232

Detroit, Michigan, 48202, United States

Location

Northwell Health-Monter Cancer Center-North Shore University Hospital and Steven and Alexandra Cohen Children's Medical Center of New York (Schneider Children's Hospital)-North Shore Long Island Jewis Site Number : 1231

Lake Success, New York, 11042, United States

Location

Center for Blood Disorders Site Number : 1214

New York, New York, 10021, United States

Location

SUNY Upstate Medical University Site Number : 1221

Syracuse, New York, 13210, United States

Location

Brody School of Medicine at East Carolina University Site Number : 1203

Greenville, North Carolina, 27834, United States

Location

Cleveland Clinic Foundation Site Number : 1207

Cleveland, Ohio, 44195, United States

Location

The Ohio State University Site Number : 1236

Columbus, Ohio, 43210, United States

Location

Hematology Oncology Associates, PC Site Number : 1211

Medford, Oregon, 97504, United States

Location

University of Pittsburgh Medical Center-UPMC Hillman Cancer Center Site Number : 1210

Pittsburgh, Pennsylvania, 15232, United States

Location

UT Medical Center Cancer Institute Site Number : 1237

Knoxville, Tennessee, 37920, United States

Location

University of Washingtion Seattle Cancer Care Alliance Site Number : 1238

Seattle, Washington, 98109, United States

Location

Investigational Site Number : 3101

Salzburg, 5020, Austria

Location

Investigational Site Number : 3102

Vienna, 1090, Austria

Location

Investigational Site Number : 3222

Amiens, 80054, France

Location

Investigational Site Number : 3214

Angers, 49933, France

Location

Investigational Site Number : 3204

Cesson-Sévigné, 35510, France

Location

Investigational Site Number : 3211

Chalon-sur-Saône, 71100, France

Location

Investigational Site Number : 3206

Corbeil-Essonnes, 91100, France

Location

Investigational Site Number : 3201

Créteil, 94010, France

Location

Investigational Site Number : 3219

Dijon, 21079, France

Location

Investigational Site Number : 3221

Epagny-Metz-Tessy, 74370, France

Location

Investigational Site Number : 3217

Paris, 75013, France

Location

Investigational Site Number : 3213

Pau, 64000, France

Location

Investigational Site Number : 3203

Pessac, 33600, France

Location

Investigational Site Number : 3216

Poitiers, 86021, France

Location

Investigational Site Number : 3202

Quimper, 2900, France

Location

Investigational Site Number : 3220

Rennes, 35033, France

Location

Investigational Site Number : 3205

Saint-Priest-en-Jarez, 42270, France

Location

Investigational Site Number : 3218

Toulouse, 31059, France

Location

Investigational Site Number : 3301

Essen, 45147, Germany

Location

Investigational Site Number : 3306

Hanover, 30161, Germany

Location

Investigational Site Number : 3302

Landshut, 84036, Germany

Location

Investigational Site Number : 3413

Brescia, Lombardy, 25123, Italy

Location

Investigational Site Number : 3410

Campobasso, 86100, Italy

Location

Investigational Site Number : 3403

Novara, 28100, Italy

Location

Investigational Site Number : 3411

Palermo, 90146, Italy

Location

Investigational Site Number : 3415

Pavia, 27100, Italy

Location

Investigational Site Number : 3412

Ravenna, 48121, Italy

Location

Investigational Site Number : 3402

Reggio Calabria, 89133, Italy

Location

Investigational Site Number : 3404

Roma, 00161, Italy

Location

Investigational Site Number : 3405

Terni, 05100, Italy

Location

Investigational Site Number : 2203

Fukushima, Fukushima, 960-1295, Japan

Location

Investigational Site Number : 2204

Himeji-shi, Hyōgo, 670-0063, Japan

Location

Investigational Site Number : 3701

Barcelona, Barcelona [Barcelona], 8036, Spain

Location

Investigational Site Number : 3712

Madrid, 28034, Spain

Location

Investigational Site Number : 3603

Truro, Cornwall, TR13LJ, United Kingdom

Location

Investigational Site Number : 3617

Carlisle, Cumbria, CA2 7HY, United Kingdom

Location

Investigational Site Number : 3608

Gillingham, Kent, ME75NY, United Kingdom

Location

Investigational Site Number : 3605

London, London, City of, NW1 2PG, United Kingdom

Location

Investigational Site Number : 3602

Salford, Manchester, M6 8HD, United Kingdom

Location

Investigational Site Number : 3623

Airdrie, North Lanarkshire, ML60JS, United Kingdom

Location

Investigational Site Number : 3601

Newcastle upon Tyne, North Tyneside, NE29 8NH, United Kingdom

Location

Investigational Site Number : 3613

Middlesbrough, North Yorkshire, TS4 3BW, United Kingdom

Location

Investigational Site Number : 3611

Oxford, Oxfordshire, OX3 7LE, United Kingdom

Location

Investigational Site Number : 3606

Taunton, Somerset, TA1 5DA, United Kingdom

Location

Investigational Site Number : 3618

Birmingham, B15 2GW, United Kingdom

Location

Investigational Site Number : 3620

Harrow, HA1 3UJ, United Kingdom

Location

Investigational Site Number : 3612

Leeds, LS9 7TF, United Kingdom

Location

Investigational Site Number : 3607

Liverpool, L7 8XP, United Kingdom

Location

Investigational Site Number : 3621

London, E1 2ES, United Kingdom

Location

MeSH Terms

Conditions

Anemia, Hemolytic, Autoimmune

Interventions

sutimlimab

Condition Hierarchy (Ancestors)

Anemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Ignacio Alvarez Rojo

    RECORDATI GROUP

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
OTHER
Time Perspective
PROSPECTIVE
Target Duration
6 Years
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 15, 2023

First Posted

March 30, 2023

Study Start

December 12, 2019

Primary Completion (Estimated)

November 2, 2028

Study Completion (Estimated)

November 2, 2028

Last Updated

April 22, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Qualified researchers may request access to patient level data and related study documents including the clinical study report, study protocol with any amendments, blank case report form, statistical analysis plan, and dataset specifications. Patient level data will be anonymized and study documents will be redacted to protect the privacy of trial participants. Further details on Sanofi's data sharing criteria, eligible studies, and process for requesting access can be found at: https://vivli.org.

Locations