NCT05650281

Brief Summary

Real-World Data (RWD) exploring the natural history of MS suggested that relapses do not significantly influence the progression of irreversible disability. Disability progression independent of relapses activity (PIRA) has been confirmed as a frequent relapsing-remitting multiple sclerosis (RRMS) phenomenon based on Randomized Clinical Trials (RCT). Recently, RWD demonstrated that the absence of markers of inflammation (No Evidence of Disease Activity (NEDA) at 2 years did not predict long-term stability. Silent progression has been proposed to describe the insidious disability that accrues many patients who satisfy traditional criteria for relapsing-remitting MS. In this study, the investigators would like to evaluate the occurrence of the SPMS in a population of RRMS patient with an Highly Active Treatment (HAT).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2,230

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jan 2023

Shorter than P25 for all trials

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 8, 2022

Completed
4 months until next milestone

First Posted

Study publicly available on registry

December 14, 2022

Completed
18 days until next milestone

Study Start

First participant enrolled

January 1, 2023

Completed
3 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 31, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 31, 2023

Completed
Last Updated

July 21, 2023

Status Verified

July 1, 2023

Enrollment Period

3 months

First QC Date

August 8, 2022

Last Update Submit

July 20, 2023

Conditions

Outcome Measures

Primary Outcomes (15)

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    Age in years

    Baseline: beginning of highly active treatment

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    Disease duration (which should be \<5 years) in months

    Baseline: beginning of highly active treatment

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    Expanded Disability Status Scale (EDSS) (which must be \<4)

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    new T2 lesion(s) on brain MRI and spinal cord MRI (if available)

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    gadolinium enhancement on brain MRI and spinal cord MRI (if available)

    Baseline: beginning of highly active treatment

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    Interval time between the first and the second relapse in months

    Baseline: beginning of highly active treatment

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    Reason for HAT: naive, or switch

    Baseline: beginning of highly active treatment

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    Number of relapses since MS onset

    Baseline: beginning of highly active treatment

  • Determination of baseline clinical markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    DMT administered since MS onset: number of DMT and type

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    More than 9 T2 lesions on MRI

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    At least 1 periventicular T2 lesion on MRI

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    At least 3 periventicular T2 lesions on MRI

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    At least 1 infratentorial T2 lesion on MRI

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    At least 1 spinal cord T2 lesion on MRI

    Baseline: beginning of highly active treatment

  • Determination of baseline MRI markers associated with SPMS diagnosis despite an early, practical, Highly Active Treatment.

    At least 1 gadolinium enhancement T1 lesion on MRI

    Baseline: beginning of highly active treatment

Secondary Outcomes (21)

  • To determine re-baseline clinical markers associated with SPMS diagnosis despite an early, practical, HAT.

    Re-baseline definition: any patient with at least an EDSS and MRI examination performed 12 months after HAT onset. +/- 6 months (from 6 to 18 months).

  • To determine re-baseline clinical markers associated with SPMS diagnosis despite an early, practical, HAT.

    Re-baseline definition: any patient with at least an EDSS and MRI examination performed 12 months after HAT onset. +/- 6 months (from 6 to 18 months).

  • To determine re-baseline clinical markers associated with SPMS diagnosis despite an early, practical, HAT.

    Re-baseline definition: any patient with at least an EDSS and MRI examination performed 12 months after HAT onset. +/- 6 months (from 6 to 18 months).

  • To determine re-baseline MRI markers associated with SPMS diagnosis despite an early, practical, HAT.

    Re-baseline definition: any patient with at least an EDSS and MRI examination performed 12 months after HAT onset. +/- 6 months (from 6 to 18 months).

  • To determine re-baseline MRI markers associated with SPMS diagnosis despite an early, practical, HAT.

    Re-baseline definition: any patient with at least an EDSS and MRI examination performed 12 months after HAT onset. +/- 6 months (from 6 to 18 months).

  • +16 more secondary outcomes

Study Arms (1)

Patients

Patients with RRMS (2017 Mc Donald criteria) treated with highly active treatment in the first 5 years of symptoms onset, at least 1 year, with an EDSS below 4

Other: NO INTERVENTION

Interventions

NO INTERVENTION

Patients

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients with RRMS (2017 Mc Donald criteria) treated with highly active treatment in the first 5 years of symptoms onset, at least 1 year, with an EDSS below 4

You may qualify if:

  • HAT start after April 12th 2007 (availability of Natalizumab)
  • Naive or failure (or intolerability) to 1 or more first line DMT (injectables, teriflunomide, DMF).

You may not qualify if:

  • Progressive relapsing MS at baseline
  • Clinical or basic MRI data unavailable after on-site visit.
  • MS diagnostic \> 5 years at baseline
  • Immunosuppressive drugs (Azathioprine, Cyclophosphamide, Mycophenolate, Methotrexate) prescribed before HAT initiation

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

CHU de Nice

Nice, France

Location

MeSH Terms

Conditions

Multiple Sclerosis

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
RETROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 8, 2022

First Posted

December 14, 2022

Study Start

January 1, 2023

Primary Completion

March 31, 2023

Study Completion

March 31, 2023

Last Updated

July 21, 2023

Record last verified: 2023-07

Data Sharing

IPD Sharing
Will not share

Locations