NCT05523765

Brief Summary

This study will evaluate the clinical safety and efficacy of oral brepocitinib in participants with active intermediate, posterior, or pan non-infectious uveitis (NIU).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
26

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Nov 2022

Geographic Reach
1 country

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 25, 2022

Completed
6 days until next milestone

First Posted

Study publicly available on registry

August 31, 2022

Completed
3 months until next milestone

Study Start

First participant enrolled

November 14, 2022

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 30, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 30, 2024

Completed
Last Updated

July 25, 2025

Status Verified

July 1, 2025

Enrollment Period

1.7 years

First QC Date

August 25, 2022

Last Update Submit

July 23, 2025

Conditions

Keywords

BrepocitinibPF-06700841uveitisNIU

Outcome Measures

Primary Outcomes (1)

  • Incidence of Treatment-emergent Adverse Events (TEAEs) and Serious Adverse Events (SAEs)

    Safety assessments will consist of monitoring and recording all adverse events (AEs) and SAEs, laboratory evaluation for hematology, blood chemistry, and urinalysis; vital signs; electrocardiograms (ECGs); and physical examinations. The investigator will determine whether the change is clinically meaningful.

    Screening up to 28 days after the last dose of study drug at 52 weeks

Secondary Outcomes (1)

  • Proportion of participants meeting treatment failure criteria on or after Week 6 up to Week 24

    24 weeks

Study Arms (2)

Brepocitinib Dose Level 1 by mouth (PO) once daily (QD)

EXPERIMENTAL
Drug: Brepocitinib

Brepocitinib Dose Level 2 by mouth (PO) once daily (QD)

EXPERIMENTAL
Drug: Brepocitinib

Interventions

Oral Brepocitinib

Brepocitinib Dose Level 1 by mouth (PO) once daily (QD)Brepocitinib Dose Level 2 by mouth (PO) once daily (QD)

Eligibility Criteria

Age18 Years - 74 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Adult subjects (18-74 years old)
  • Diagnosis of non-infectious uveitis (intermediate uveitis, posterior uveitis, or panuveitis).
  • Active uveitic disease as defined by the presence of at least 1 of the following parameters in at least 1 eye, as determined by the investigator:
  • Active, inflammatory chorioretinal and/or retinal vascular lesion; OR
  • ≥2+ vitreous haze grade (NEI/SUN criteria).
  • Receiving up to one non-corticosteroid, non-biologic, immunomodulatory therapy
  • Weight \> 40 kg with a body mass index \< 40 kg/m2.

You may not qualify if:

  • Has isolated anterior uveitis.
  • Has confirmed or suspected current diagnosis of infectious uveitis
  • History of:
  • Any lymphoproliferative disorder
  • Active malignancy;
  • History of cancer within 5 years prior to screening (exceptions for basal cell carcinoma, squamous cell carcinoma, ductal carcinoma in situ of the breast, carcinoma in situ of the uterine cervix, or thyroid carcinoma.)
  • At risk of thrombosis and cardiovascular disease
  • Have a high risk for herpes zoster reactivation
  • Have active or recent infections

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Clinical Trial Site

Los Angeles, California, 90095, United States

Location

Clinical Trial Site

Palo Alto, California, 94303, United States

Location

Clinical Trial Site

Pasadena, California, 91107, United States

Location

Clinical Trial Site

Lakewood, Colorado, 80228, United States

Location

Clinical Trial Site

Waltham, Massachusetts, 02451, United States

Location

Clinical Trial Site

St Louis, Missouri, 63110, United States

Location

Clinical Trial Site

Palisades Park, New Jersey, 07650, United States

Location

Clinical Trial Site

Durham, North Carolina, 27710, United States

Location

Clinical Trial Site

Winston-Salem, North Carolina, 27157, United States

Location

Clinical Trial Site

Eugene, Oregon, 97401, United States

Location

Clinical Trial Site

Nashville, Tennessee, 37203, United States

Location

Clinical Trial Site

Bellaire, Texas, 77401, United States

Location

Clinical Trial Site

Katy, Texas, 77494, United States

Location

Clinical Trial Site

Plano, Texas, 75075, United States

Location

Clinical Trial Site

Salt Lake City, Utah, 84107, United States

Location

MeSH Terms

Conditions

Uveitis

Condition Hierarchy (Ancestors)

Uveal DiseasesEye Diseases

Study Officials

  • Brendan Johnson, PhD

    SVP, Early Development

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
OTHER
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 25, 2022

First Posted

August 31, 2022

Study Start

November 14, 2022

Primary Completion

July 30, 2024

Study Completion

July 30, 2024

Last Updated

July 25, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

Priovant Therapeutics will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) from eligible studies upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Data requests will be reviewed and approved on the basis of scientific merit.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
The data will be made available within 24 months after study completion and will be accessible for a time frame appropriate for the approved proposal.
Access Criteria
Access will be provided following review and approval of a research proposal and execution of a Data Sharing Agreement (DSA). Further details on Priovant Therapeutics' data sharing criteria and process for requesting access can be obtained by emailing info@priovanttx.com.

Locations