NCT05366855

Brief Summary

This is a Phase 3, long term extension study to evaluate the safety and efficacy of imsidolimab compared with placebo in adult subjects with generalized pustular psoriasis (GPP).

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
42

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Apr 2022

Geographic Reach
14 countries

59 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 21, 2022

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

April 25, 2022

Completed
14 days until next milestone

First Posted

Study publicly available on registry

May 9, 2022

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 12, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 12, 2024

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

March 27, 2026

Completed
Last Updated

March 27, 2026

Status Verified

March 1, 2026

Enrollment Period

2.2 years

First QC Date

April 25, 2022

Results QC Date

February 5, 2026

Last Update Submit

March 6, 2026

Conditions

Keywords

IL-36 receptorImsidolimabInterleukin-36

Outcome Measures

Primary Outcomes (1)

  • Incidence of Adverse Events

    All Adverse Events (AEs) were collected from Day 1 of 302 up to the final Safety Follow-up Visit (Week 116) regardless of seriousness or relationship to investigational product.

Secondary Outcomes (3)

  • Percentage of Subjects Maintaining GPPPGA Score of 0 or 1

    Week 24

  • Kaplan-Meier Estimate for Time to First GPP Flare Recurrence (Weeks)

    From Day 1 until termination of study

  • Percentage of Subjects With Zero Recurrence of GPP Flare

    Week 24

Study Arms (8)

ANB019-301 Imsidolimab Responder + ANB019-302 Imsidolimab 200 mg SC

EXPERIMENTAL

Randomized to subcutaneous 200 mg imsidolimab Q4W

Drug: Double-blind 200 mg imsidolimab

ANB019-301 Imsidolimab Responder + ANB019-302 Placebo SC

PLACEBO COMPARATOR

Randomized to subcutaneous placebo Q4W

Other: Placebo

ANB019-301 Imsidolimab Partial Responder + ANB019-302 Imsidolimab 200 mg SC

EXPERIMENTAL

Open-label subcutaneous 200 mg imsidolimab Q4W

Drug: Open-label 200 mg imsidolimab

ANB019-301 Imsidolimab Need for Rescue + ANB019-302 Any Therapy

ACTIVE COMPARATOR

Any available therapy

Other: Standard of Care (SOC)

ANB019-301 Placebo Responder + ANB019-302 Imsidolimab 200 mg SC

EXPERIMENTAL

Randomized to subcutaneous 200 mg imsidolimab Q4W

Drug: Double-blind 200 mg imsidolimab

ANB019-301 Placebo Responder + ANB019-302 Placebo SC

PLACEBO COMPARATOR

Randomized to subcutaneous placebo SC Q4W

Other: Placebo

ANB019-301 Placebo Partial Responder + ANB019-302 Imsidolimab 200 mg SC

EXPERIMENTAL

Open-label subcutaneous 200 mg imsidolimab Q4W

Drug: Open-label 200 mg imsidolimab

ANB019-301 Placebo Need for Rescue + ANB019-302 Imsidolimab 750 mg IV/200 mg SC

EXPERIMENTAL

Intravenous imsidolimab 750 mg loading dose followed by subcutaneous 200 mg imsidolimab Q4W

Drug: Imsidolimab 750 mg IV/200 mg SC

Interventions

PlaceboOTHER

Double-blind subcutaneous dosing

ANB019-301 Imsidolimab Responder + ANB019-302 Placebo SCANB019-301 Placebo Responder + ANB019-302 Placebo SC

Double-blind subcutaneous dosing

Also known as: ANB019
ANB019-301 Imsidolimab Responder + ANB019-302 Imsidolimab 200 mg SCANB019-301 Placebo Responder + ANB019-302 Imsidolimab 200 mg SC

Open-label subcutaneous dosing

Also known as: ANB019
ANB019-301 Imsidolimab Partial Responder + ANB019-302 Imsidolimab 200 mg SCANB019-301 Placebo Partial Responder + ANB019-302 Imsidolimab 200 mg SC

Any available therapy

ANB019-301 Imsidolimab Need for Rescue + ANB019-302 Any Therapy

Intravenous loading dose followed by subcutaneous dosing

Also known as: ANB019
ANB019-301 Placebo Need for Rescue + ANB019-302 Imsidolimab 750 mg IV/200 mg SC

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject participated in the preceding placebo-controlled Phase 3 study ANB019-301 and completed at least the Week 1 visit of the ANB019-301 study without the use of rescue/prohibited medication for GPP
  • Subject must be a candidate for prolonged GPP treatment according to the Investigator's judgment

You may not qualify if:

  • Use of prohibited medications between the last visit of the ANB019-301 study and the Day 1 visit of the ANB019-302 study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (65)

Site 10-109

Largo, Florida, 33770, United States

Location

Site 10-105

Louisville, Kentucky, 40217, United States

Location

Site 10-101

Ann Arbor, Michigan, 48109, United States

Location

Site 10-108

Dallas, Texas, 75231, United States

Location

Site 10-102

Springville, Utah, 84663, United States

Location

Site 35-102

Melbourne, Victoria, 3128, Australia

Location

Site 16-102

Nantes, 44093, France

Location

Site 16-101

Paris, 75010, France

Location

Site 59-104

Batumi, 6000, Georgia

Location

Site 59-102

Tbilisi, 0112, Georgia

Location

Site 59-101

Tbilisi, 0160, Georgia

Location

Site 59-105

Tbilisi, 0160, Georgia

Location

Site 59-103

Tbilisi, 0179, Georgia

Location

Site 17-102

Bad Bentheim, 48455, Germany

Location

Site 17-104

Bonn, 53127, Germany

Location

Site 17-103

Hanau, 63450, Germany

Location

Site 17-105

Würzburg, 97080, Germany

Location

Site 42-106

Johor Bahru, Johor, 80100, Malaysia

Location

Site 42-107

Johor Bahru, Johor, 81100, Malaysia

Location

Site 42-102

Muar town, Johor, 84000, Malaysia

Location

Site 42-105

Kota Bharu, Kelantan, 15586, Malaysia

Location

Site 42-108

Kuching, Sarawak, 93586, Malaysia

Location

Site 42-109

Batu Caves, Selangor, 59100, Malaysia

Location

Site 42-101

Kuala Lumpur, 50586, Malaysia

Location

Site 42-104

Kuala Lumpur, 56000, Malaysia

Location

Site 42-110

Kuala Lumpur, 59100, Malaysia

Location

Site 42-103

Putrajaya, 62250, Malaysia

Location

Site 64-103

Casablanca, 20360, Morocco

Location

Site 64-101

Marrakesh, 40000, Morocco

Location

Site 64-102

Oujda, 60000, Morocco

Location

Site 30-104

Krakow, 30-074, Poland

Location

Site 30-105

Lodz, 90-265, Poland

Location

Site 30-103

Ossy, 42-624, Poland

Location

Site 30-101

Rzeszów, 35-055, Poland

Location

Site 30-102

Wroclaw, 50-566, Poland

Location

Site 31-102

Bucharest, 020125, Romania

Location

Site 31-101

Cluj-Napoca, 400006, Romania

Location

Site 31-103

Iași, 700111, Romania

Location

Site 45-102

Busan, 49241, South Korea

Location

Site 45-104

Seoul, 03722, South Korea

Location

Site 45-101

Seoul, 05505, South Korea

Location

Site 45-103

Seoul, 06591, South Korea

Location

Site 24-101

Barcelona, 08036, Spain

Location

Site 24-104

Las Palmas de Gran Canaria, 35010, Spain

Location

Site 24-102

Madrid, 28040, Spain

Location

Site 24-103

Madrid, 28041, Spain

Location

Site 24-105

Valencia, 46026, Spain

Location

Site 63-101

Kaohsiung City, 83301, Taiwan

Location

Site 63-103

New Taipei City, 23561, Taiwan

Location

Site 63-105

Taipei, 100225, Taiwan

Location

Site 63-104

Taipei, 11217, Taiwan

Location

Site 63-102

Taipei, 11696, Taiwan

Location

Site 46-101

Bangkok, 10400, Thailand

Location

Site 46-102

Chiang Mai, 50200, Thailand

Location

Site 46-104

Khon Kaen, 40002, Thailand

Location

Site 46-103

Pathum Thani, 12120, Thailand

Location

Site 62-101

Sfax, 3000, Tunisia

Location

Site 62-102

Sousse, 4000, Tunisia

Location

Site 62-103

Tunis, 1007, Tunisia

Location

Site 33-102

Ankara, 06560, Turkey (Türkiye)

Location

Site 33-104

Antalya, 07070, Turkey (Türkiye)

Location

Site 33-103

Bursa, 16059, Turkey (Türkiye)

Location

Site 33-105

Istanbul, 24093, Turkey (Türkiye)

Location

Site 33-106

Istanbul, 34010, Turkey (Türkiye)

Location

Site 33-101

Kayseri, 38039, Turkey (Türkiye)

Location

MeSH Terms

Conditions

Psoriasis

Interventions

Double-Blind MethodStandard of Care

Condition Hierarchy (Ancestors)

Skin Diseases, PapulosquamousSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Epidemiologic Research DesignEpidemiologic MethodsInvestigative TechniquesResearch DesignMethodsHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationPublic HealthEnvironment and Public HealthQuality Indicators, Health CareHealth Services Administration

Results Point of Contact

Title
Vanda Pharmaceuticals Inc.
Organization
Vanda Pharmaceuticals Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Subjects who completed the Week 4 Visit of Study ANB019-301 and had a GPPPGA score of 0 or 1 on Day 1 were randomized 1:1 to receive imsidolimab or placebo in a double-blind manner. Subjects who completed the Week 4 Visit but did not have a GPPPGA score of 0 or 1 received open-label imsidolimab. Subjects who exited the study at the Week 1 Visit (after primary endpoint assessment) or later received open-label rescue therapy.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 25, 2022

First Posted

May 9, 2022

Study Start

April 21, 2022

Primary Completion

July 12, 2024

Study Completion

July 12, 2024

Last Updated

March 27, 2026

Results First Posted

March 27, 2026

Record last verified: 2026-03

Data Sharing

IPD Sharing
Will not share

Locations