NCT05307978

Brief Summary

This is a Phase 1, randomized, double-blind, placebo-controlled study designed to evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD), and immunogenicity of single ascending doses (SADs) of ALXN1910 subcutaneous (SC) and SAD of ALXN1910 intravenous (IV).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
48

participants targeted

Target at P50-P75 for phase_1 healthy

Timeline
Completed

Started Apr 2022

Longer than P75 for phase_1 healthy

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 24, 2022

Completed
8 days until next milestone

First Posted

Study publicly available on registry

April 1, 2022

Completed
11 days until next milestone

Study Start

First participant enrolled

April 12, 2022

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 7, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 7, 2023

Completed
2.1 years until next milestone

Results Posted

Study results publicly available

February 27, 2025

Completed
Last Updated

February 27, 2025

Status Verified

January 1, 2025

Enrollment Period

10 months

First QC Date

March 24, 2022

Results QC Date

January 31, 2024

Last Update Submit

February 7, 2025

Conditions

Keywords

ALXN1910SafetyPharmacokineticsPharmacodynamicsJapanese Descent

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Treatment-Emergent Adverse Events (TEAEs) and Treatment-Emergent Serious Adverse Events (TESAEs)

    The safety and tolerability of ALXN1910 was assessed.

    Day 1 (postdose) through Day 75

Secondary Outcomes (23)

  • Maximum Observed Serum Concentration (Cmax)

    Days 1 through 5 (predose and up to 96 hours postdose), postdose on Days 6, 7, 8, 15, 22, 29, 36, 43, and 75

  • Time to Maximum Observed Serum Concentration (Tmax)

    Days 1 through 5 (predose and up to 96 hours postdose), postdose on Days 6, 7, 8, 15, 22, 29, 36, 43, and 75

  • Apparent Terminal Elimination Half Life (t1/2)

    Days 1 through 5 (predose and up to 96 hours postdose), postdose on Days 6, 7, 8, 15, 22, 29, 36, 43, and 75

  • Terminal-phase Elimination Rate Constant (λz)

    Days 1 through 5 (predose and up to 96 hours postdose), postdose on Days 6, 7, 8, 15, 22, 29, 36, 43, and 75

  • AUC From Time Zero to the Last Quantifiable Concentratio (AUCt)

    Days 1 through 5 (predose and up to 96 hours postdose), postdose on Days 6, 7, 8, 15, 22, 29, 36, 43, and 75

  • +18 more secondary outcomes

Study Arms (6)

Cohort 1

EXPERIMENTAL

Participants will receive a single dose of 5 mg of ALXN1910 IV or Placebo IV.

Drug: ALXN1910Drug: Placebo

Cohort 2

EXPERIMENTAL

Participants will receive a single dose of 15 mg of ALXN1910 SC or Placebo SC.

Drug: ALXN1910Drug: Placebo

Cohort 3

EXPERIMENTAL

Participant will receive a single dose of 15 mg of ALXN1910 IV or Placebo IV.

Drug: ALXN1910Drug: Placebo

Cohort 4

EXPERIMENTAL

Japanese participants will receive a single dose of 15 mg of ALXN1910 SC or Placebo SC.

Drug: ALXN1910Drug: Placebo

Cohort 5

EXPERIMENTAL

Participants will receive a single dose of 45 mg of ALXN1910 SC or Placebo SC.

Drug: ALXN1910Drug: Placebo

Cohort 6

EXPERIMENTAL

Participants will receive a single dose of 135 mg of ALXN1910 SC or Placebo SC.

Drug: ALXN1910Drug: Placebo

Interventions

Participants will receive a single dose of ALXN1910 IV or ALXN1910 SC according to their assigned cohort.

Cohort 1Cohort 2Cohort 3Cohort 4Cohort 5Cohort 6

Participants will receive Placebo IV or Placebo SC according to their assigned cohort.

Cohort 1Cohort 2Cohort 3Cohort 4Cohort 5Cohort 6

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64)

You may qualify if:

  • Healthy participants
  • Participants of Japanese descent are defined as: First generation (born to 2 Japanese parents and 4 Japanese grandparents).
  • Participants of Japanese descent must be between 20 and 55 years of age.

You may not qualify if:

  • Current or recurrent disease
  • Current or relevant history of physical or psychiatric illness.
  • Any other significant disease or disorder that, in the opinion of the Investigator, may put the participant at risk.
  • History of significant allergic reaction (eg, anaphylaxis or angioedema) to any product (eg, food, pharmaceutical).
  • Female participants who are pregnant or breastfeeding.
  • Major surgery or hospitalization within 90 days prior to dosing on Day1.
  • History of exposure to asfotase alfa.
  • History of allergy or hypersensitivity to excipients of asfotase alfa or ALXN1910 (eg,sodium phosphate, sodium chloride).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Clinical Trial Site

Harrow, HA1 3UJ, United Kingdom

Location

Related Links

Limitations and Caveats

For Outcome measure #12 Plasma Concentration of Inorganic Pyrophosphate (PPi); #13 Plasma Concentration of Pyridoxal (PL); #14 Plasma Concentration of Pyridoxal 5-Phosphate (PLP); 15 Plasma Concentration of Pyridoxic Acid (PA); Cohort 4 Day 75 standard deviation is provided for the posting although standard deviation will not be calculated for less than 3 data points per study's Statistical Analysis Plan.

Results Point of Contact

Title
Alexion Pharmaceuticals, Inc.
Organization
Alexion Pharmaceuticals, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
BASIC SCIENCE
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 24, 2022

First Posted

April 1, 2022

Study Start

April 12, 2022

Primary Completion

February 7, 2023

Study Completion

February 7, 2023

Last Updated

February 27, 2025

Results First Posted

February 27, 2025

Record last verified: 2025-01

Locations