NCT05218850

Brief Summary

Butyrate is an important metabolite produced by the gut microbiome and has been shown as a helpful therapy in ulcerative colitis. This is a feasibility study to determine the efficacy of butryate enemas in pediatric ulcerative colitis.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_1

Timeline
14mo left

Started Jun 2022

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress77%
Jun 2022Jun 2027

First Submitted

Initial submission to the registry

January 20, 2022

Completed
12 days until next milestone

First Posted

Study publicly available on registry

February 1, 2022

Completed
5 months until next milestone

Study Start

First participant enrolled

June 29, 2022

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 30, 2027

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 30, 2027

Last Updated

April 18, 2024

Status Verified

April 1, 2024

Enrollment Period

5 years

First QC Date

January 20, 2022

Last Update Submit

April 17, 2024

Conditions

Keywords

ulcerative colitis

Outcome Measures

Primary Outcomes (1)

  • remission of clinical disease

    pediatric ulcerative colitis activity index, remission is \<10, mild disease 10-34, moderate 35-64, severe 65 or greater

    12 weeks

Secondary Outcomes (1)

  • improvement of inflammatory markers including ESR, CRP, Calprotectin

    12 weeks

Study Arms (1)

open label intervention arm

EXPERIMENTAL

Butyrate enemas will be administered once daily for twelve weeks.

Drug: Butyrate

Interventions

Butyrate enemas will be administered once a day for 12 weeks

Also known as: Butyrate enemas
open label intervention arm

Eligibility Criteria

Age7 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • years, mild to moderate ulcerative colitis

You may not qualify if:

  • UC therapy within 4 weeks of study medication initiation
  • infectious colitis, -pregnancy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Children's Hospital Los Angeles

Los Angeles, California, 90027, United States

RECRUITING

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

Butyrates

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Intervention Hierarchy (Ancestors)

Acids, AcyclicCarboxylic AcidsOrganic ChemicalsFatty Acids, VolatileFatty AcidsLipids

Study Officials

  • Sonia Michail, MD

    Children's Hospital Los Angeles

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Sonia Michail, MD

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

January 20, 2022

First Posted

February 1, 2022

Study Start

June 29, 2022

Primary Completion (Estimated)

June 30, 2027

Study Completion (Estimated)

June 30, 2027

Last Updated

April 18, 2024

Record last verified: 2024-04

Data Sharing

IPD Sharing
Will not share

data can be shared upon request

Locations