NCT05192200

Brief Summary

The purpose of this research study is to evaluate the long-term safety, and tolerability of PF-06823859 study drug in adult participants with Dermatomyositis (DM) from a qualifying study.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
24

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Dec 2021

Geographic Reach
4 countries

25 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 1, 2021

Completed
19 days until next milestone

Study Start

First participant enrolled

December 20, 2021

Completed
25 days until next milestone

First Posted

Study publicly available on registry

January 14, 2022

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 20, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 20, 2023

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

February 6, 2025

Completed
Last Updated

February 6, 2025

Status Verified

February 1, 2025

Enrollment Period

1.9 years

First QC Date

December 1, 2021

Results QC Date

November 12, 2024

Last Update Submit

February 5, 2025

Conditions

Outcome Measures

Primary Outcomes (4)

  • Number of Participants With Treatment Emergent Adverse Events (TEAEs)

    An Adverse Event (AE) was any untoward medical occurrence in a participant or clinical study participant, temporally associated with the use of study intervention, whether or not considered related to the study intervention. An AE was considered treatment emergent relative to a given treatment if the event occurred for the first time during the effective duration of treatment and was not seen prior to the start of treatment, or the event was seen prior to the start of treatment but increased in severity during treatment. AEs included both serious adverse events (SAEs) and all non-SAEs.

    From Day 1 of dosing maximum up to Week 68

  • Number of Participants With Laboratory Abnormalities

    Hematology laboratory parameters: hemoglobin (grams per deciliter \[g/dL\]); hematocrit (percentage \[%\]); lymphocytes (10\^3 per (/) millimeter\[mm\]\^3); lymphocytes/leukocytes (%); neutrophils (10\^3/mm\^3) less than (\<)0.8\*lower limit of normal (LLN), leukocytes (10\^3/mm\^3) \<0.6\*LLN, neutrophils (10\^3/mm\^3); basophils (10\^3/mm\^3); basophils/leukocytes (%); monocytes/leukocytes (%); activated partial thromboplastin time (seconds \[sec\]); prothrombin time (sec) more than (\>)1.2\*upper limit of normal (ULN). Clinical chemistry: potassium (milliequivalents per liter \[mEq/L\]); bicarbonate (mEq/L) \<0.9\*LLN, creatine kinase (units per liter \[U/L\]) \>2.0\*ULN, glucose (milligram per deciliter \[mg/dl\]); glucose-fasting (mg/dl) \>1.5\*ULN. Urinalysis: Urine glucose; ketones; urine protein; urine hemoglobin; nitrite; leukocyte esterase; hyaline casts (1/per leukocytosis promoting factor (more than or equal to \[\>=\] 1, urine erythrocytes (scalar); urine leukocytes (scalar) \>=20.

    From Day 1 of dosing maximum up to Week 68

  • Number of Participants According to Categorization of Changes in Vital Signs

    Vital signs included the following parameters: sitting diastolic blood pressure (millimetres of mercury \[mmHg\]) change \>=20 mmHg increase; sitting systolic blood pressure (mmHg) change \>=30 mmHg increase, sitting diastolic blood pressure (mmHg) change \>=20 mmHg decrease and sitting systolic blood pressure (mmHg) change \>=30 mmHg decrease.

    From Day 1 of dosing maximum up to Week 68

  • Number of Participants According to Categorization of Electrocardiogram (ECG) Findings

    ECG parameters evaluated were: PR interval value \>=300 milliseconds (msec); QRS duration value \>=200 msec; QT interval value \>=500 msec; corrected QT Interval using Fridericia's formula (QTCF) 450 less than or equal to (\<=) value \<480 msec, 480 \<=value\<500 msec and value\>=500 msec.

    From Day 1 of dosing maximum up to Week 68

Secondary Outcomes (12)

  • Change From Baseline in Cutaneous Dermatomyositis Disease Area and Severity Index (CDASI) Activity Score at Week 52

    Baseline (before dose 1), Week 52

  • Change From Baseline in CDASI Activity Score at Weeks 12, 24, 36, and 48

    Baseline (before dose 1), Weeks 12, 24, 36 and 48

  • Absolute Values of CDASI Activity Score at Weeks 12, 24, 36, 48, and 52

    Weeks 12, 24, 36, 48 and 52

  • Change From Baseline in CDASI Damage Score at Weeks 12, 24, 36, 48, and 52

    Baseline (before dose on Day 1), Weeks 12, 24, 36, 48 and 52

  • Absolute Values of CDASI Damage Score at Weeks 12, 24, 36, 48, and 52

    Weeks 12, 24, 36, 48 and 52

  • +7 more secondary outcomes

Study Arms (1)

Anti-Beta Interferon drug (PF-06823859)

EXPERIMENTAL

IV infusion

Drug: Anti-Beta Interferon (PF-06823859)

Interventions

IV infusion

Anti-Beta Interferon drug (PF-06823859)

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants aged ≥18 and ≤80 with moderate to severe dermatomyositis (DM), that have completed the treatment period of a qualifying study.
  • Capable of giving signed informed consent.
  • Participants who are willing and able to comply with all scheduled visits, treatment plan, laboratory tests, lifestyle considerations, and other study procedures.

You may not qualify if:

  • Other medical or psychiatric condition including recent (within the past year) or active suicidal ideation/behavior or laboratory abnormality that may increase the risk of study participation or, in the investigator's judgment, make the participant inappropriate for the study
  • Participants who met discontinuation criteria at any point during the participating qualifying studies.
  • Participants with an ongoing safety event in the qualifying studies which, in the opinion of the investigator or sponsor, is an ongoing safety concern OR the participant has met safety monitoring criteria in the qualifying study that has not resolved.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

University of Alabama at Birmingham, Department of Dermatology

Birmingham, Alabama, 35294, United States

Location

Mayo Clinic

Scottsdale, Arizona, 85259, United States

Location

Attune Health Research Inc.

Beverly Hills, California, 90211, United States

Location

Mayo Clinic in Florida

Jacksonville, Florida, 32224, United States

Location

KU Clinical Research Center - Clinical and Translational Science Unit (CTSU)

Fairway, Kansas, 66205, United States

Location

KU Clinical and Translational Science Unit (CTSU) Rainbow

Kansas City, Kansas, 66160, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Brigham & Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Brigham and Women's Hospital - CTH

Boston, Massachusetts, 02115, United States

Location

Center for Outpatient Health

St Louis, Missouri, 63108, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63108, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

NYU Grossman School of Medicine, The Ronald O. Perelman Department of Dermatology

New York, New York, 10016, United States

Location

NYU Langone Health Clinical Research Center

New York, New York, 10016, United States

Location

NYU Langone Radiology - Ambulatory Care Center East 41st Street

New York, New York, 10017, United States

Location

Mount Sinai Doctors Dermatology

New York, New York, 10028, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Center for Human Phenomic Science

Philadelphia, Pennsylvania, 19104, United States

Location

University of Pennsylvania, Perelman Center for Advanced Medicine (PCAM)

Philadelphia, Pennsylvania, 19104, United States

Location

Debreceni Egyetem Klinikai Kozpont

Debrecen, 4032, Hungary

Location

Nova Reuma Społka Partnerska

Bialystok, Podlaskie Voivodeship, 15-707, Poland

Location

Centrum Medyczne Plejady

Krakow, 30-363, Poland

Location

Hospital Universitario 12 de Octubre

Madrid, 28041, Spain

Location

Related Links

MeSH Terms

Conditions

Dermatomyositis

Condition Hierarchy (Ancestors)

PolymyositisMyositisMuscular DiseasesMusculoskeletal DiseasesNeuromuscular DiseasesNervous System DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesSkin Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: Eligible participants will have completed the treatment period of a qualifying Dermatomyositis parent study. All participants will receive active study drug.
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 1, 2021

First Posted

January 14, 2022

Study Start

December 20, 2021

Primary Completion

November 20, 2023

Study Completion

November 20, 2023

Last Updated

February 6, 2025

Results First Posted

February 6, 2025

Record last verified: 2025-02

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations