NCT05176210

Brief Summary

This is a phase I, double-blind, placebo-controlled, randomized, single- and multiple-ascending dose study to evaluate new study intervention, PS1. PS1 is a potential blood glucose control medication, which is developed by Pharmasaga Co. Ltd. planned for treating type II diabetes mellitus (T2DM). This is a first-in-human study to evaluate the safety, tolerability, pharmacokinetics (PK), food effect and potential efficacy of PS1 in subjects.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
64

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Dec 2023

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 29, 2021

Completed
1 month until next milestone

First Posted

Study publicly available on registry

January 4, 2022

Completed
2 years until next milestone

Study Start

First participant enrolled

December 22, 2023

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2025

Completed
Last Updated

April 15, 2024

Status Verified

April 1, 2024

Enrollment Period

1.5 years

First QC Date

November 29, 2021

Last Update Submit

April 10, 2024

Conditions

Outcome Measures

Primary Outcomes (1)

  • Incidence of dose-limiting toxicity (DLT) during the DLT observation period

    DLT is defined as: (1) any adverse event (AE) ≥ Grade 3 (CTCAE v5.0) or (2) Grade 2 AE that does not resolve to grade 1 or less within 72 hours, that occurs in the DLT observation period and is causally related (possibly, probably, or definitely related) to the test article judged by the investigator.

    Day 1~ Day 8 (SAD cohort); Day 1~ Day 35 (MAD cohort)

Secondary Outcomes (16)

  • Incidence of adverse events (AEs) and serious adverse events (SAEs)

    SAD, FE: up to 4 weeks; MAD: up to 8 weeks

  • Number of participants with abnormalities in Vital signs

    SAD, FE: Baseline,1~2 weeks; MAD: Baseline,1~6 weeks

  • Number of participants with abnormalities in Laboratory examinations

    SAD, FE: Baseline,1~2 weeks; MAD: Baseline,1~6 weeks

  • Acute kidney injury (AKI) marker

    SAD, FE: Baseline, 1~2 weeks; MAD: Baseline, 1~6 weeks

  • Number of participants with abnormalities in 12-lead electrocardiogram (EKG)

    SAD, FE: Baseline, 1~2 weeks; MAD: Baseline, 1~6 weeks

  • +11 more secondary outcomes

Study Arms (8)

SAD portion - Cohort 1 (25mg)

EXPERIMENTAL

An eligible subject will receive a single dose of 25 mg of PS1 or Placebo tablets in a fed condition on Day 1 and be followed for 7 days.

Drug: PS1Drug: Placebo

SAD portion - Cohort 2 (50mg)

EXPERIMENTAL

An eligible subject will receive a single dose of 50 mg of PS1 or Placebo tablets in a fed condition on Day 1 and be followed for 7 days.

Drug: PS1Drug: Placebo

SAD portion - Cohort 3 (75mg)

EXPERIMENTAL

An eligible subject will receive a single dose of 75 mg of PS1 or Placebo tablets in a fed condition on Day 1 and be followed for 7 days.

Drug: PS1Drug: Placebo

FE portion - Cohort 4 (50mg)

EXPERIMENTAL

An eligible subject will receive a single dose of 50 mg PS1 or Placebo tablets in a fasted condition on Day 1 and be followed for 7 days.

Drug: PS1Drug: Placebo

MAD portion - Cohort 5 (25mg)

EXPERIMENTAL

An eligible subject will receive 25 mg PS1 or Placebo tablets once daily in a fed condition for 14 days and be followed for additional 7 days.

Drug: PS1Drug: Placebo

MAD portion - Cohort 6 (50mg)

EXPERIMENTAL

An eligible subject will receive 50 mg PS1 or Placebo tablets once daily in a fed condition for 14 days and be followed for additional 7 days.

Drug: PS1Drug: Placebo

MAD portion - Cohort 7 (25mg)

EXPERIMENTAL

An eligible subject will receive 25 mg PS1 or Placebo tablets once daily in a fed condition for 28 days and be followed for additional 7 days.

Drug: PS1Drug: Placebo

MAD portion - Cohort 8 (50mg)

EXPERIMENTAL

An eligible subject will receive 50 mg PS1 or Placebo tablets once daily in a fed condition for 28 days and be followed for additional 7 days.

Drug: PS1Drug: Placebo

Interventions

PS1DRUG

PS1 will be provided as a 120 mg tablet with 25 mg active pharmaceutical ingredient.

Also known as: PS-001
FE portion - Cohort 4 (50mg)MAD portion - Cohort 5 (25mg)MAD portion - Cohort 6 (50mg)MAD portion - Cohort 7 (25mg)MAD portion - Cohort 8 (50mg)SAD portion - Cohort 1 (25mg)SAD portion - Cohort 2 (50mg)SAD portion - Cohort 3 (75mg)

Placebo will be provided as a 120 mg tablet.

FE portion - Cohort 4 (50mg)MAD portion - Cohort 5 (25mg)MAD portion - Cohort 6 (50mg)MAD portion - Cohort 7 (25mg)MAD portion - Cohort 8 (50mg)SAD portion - Cohort 1 (25mg)SAD portion - Cohort 2 (50mg)SAD portion - Cohort 3 (75mg)

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • For all cohorts, a subject is eligible for the study if all of the following apply:
  • Both genders aged 18 to 80 years, inclusive at screening
  • Body mass index (BMI) between 18.5 and 40.0 kg/m2
  • Negative test for hepatitis B surface antigen (HBsAg), Anti-HCV antibody, and human immunodeficiency virus (HIV) at screening
  • Is willing to follow the trial life style instruction and protocol procedure
  • Able to understand and sign the informed consent form.
  • Overtly healthy subject, who is considered to be generally healthy based on medical history, vital signs, laboratory tests, 12-lead EKG, and physical examination, as judged by the investigator
  • With HbA1c value of \< 6.5% and fasting plasma glucose \< 110 mg/dL at Screening
  • With estimated glomerular filtration rate (eGFR) \> 80 ml/min
  • Diagnosis of T2DM
  • T2DM treated with diet and exercise alone currently, for at least 2 weeks prior to Screening
  • With HbA1c level between 6.5% to 9.0% and fasting plasma glucose level between 130 mg/dL to 250 mg/dL at Screening
  • With estimated glomerular filtration rate (eGFR) \> 60 ml/min
  • For patients taking medication for other chronic disease, the medication should be on a stable dose for at least 4 weeks prior to Screening, and should not be a strong CYP enzyme inhibitor or inducer

You may not qualify if:

  • History of Type I diabetes mellitus
  • Under the systemic treatment of any prescription medication or over-the-counter (OTC) medication that may interfere with the safety or PK assessment judged by the investigator within 7 days before Screening
  • Received strong CYP enzyme inhibitor or inducer within 14 days before Screening
  • Received any vaccination within 14 days before Screening
  • Has required insulin therapy within the past 12 weeks
  • Known hypersensitivity to any of the components of PS1 tablet
  • History of major clinically significant hematological, renal, respiratory, gastrointestinal, cardiovascular, hepatic, psychiatric, neurological, musculoskeletal, immune, or allergic disease (including drug allergies, but excluding untreated, asymptomatic, seasonal allergies at the time of dosing) within 3 months of Screening that may significantly alter the biomarker panel, require receiving any systemic medications, or interfere with the interpretation of data, as judged by the investigator
  • History of pancreatitis
  • Serum amylase \> 1.5 × Upper Limit of Normal (ULN) or lipase \> 1.5 × ULN
  • Clinically significant ECG abnormality at Screening
  • History of cancer (malignancy) or have ever received any anti-cancer therapy
  • Regular smoker Regular smoker is defined as who smokes every day (≥ 1 cigarette/day in average in the past 8 weeks of Screening)
  • Consumed greater than 3 units of alcoholic beverages per day in average for the past 4 weeks before Screening One unit is equivalent to one can of beer (20% alcohol; about 45 mL)
  • Received any investigational therapy from another clinical study or underwent any major surgeries within the last 12 weeks prior to Screening.
  • Took glucose-lowering medications within the last 2 weeks prior to Screening
  • +10 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Mingche Liu

Taipei, Taiwan

RECRUITING

MeSH Terms

Conditions

Diabetes Mellitus, Type 2

Interventions

5-tert-butyl-N-pyrazol-4-yl-4,5,6,7-tetrahydrobenzo(d)isoxazole-3-carboxamide

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System Diseases

Study Officials

  • Mingche Liu, MD., PhD

    Taipei Medical University Hospital

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Yuyu Chung, Master

CONTACT

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 29, 2021

First Posted

January 4, 2022

Study Start

December 22, 2023

Primary Completion

July 1, 2025

Study Completion

July 1, 2025

Last Updated

April 15, 2024

Record last verified: 2024-04

Data Sharing

IPD Sharing
Will not share

Locations