NCT05138133

Brief Summary

The purpose of this study is to evaluate the efficacy and safety of IV antifrolumab in adult patients with Active Proliferative Lupus Nephritis

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
359

participants targeted

Target at P50-P75 for phase_3

Timeline
32mo left

Started Feb 2022

Longer than P75 for phase_3

Geographic Reach
24 countries

167 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress62%
Feb 2022Dec 2028

First Submitted

Initial submission to the registry

November 17, 2021

Completed
13 days until next milestone

First Posted

Study publicly available on registry

November 30, 2021

Completed
3 months until next milestone

Study Start

First participant enrolled

February 15, 2022

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 26, 2027

Expected
1.8 years until next milestone

Study Completion

Last participant's last visit for all outcomes

December 5, 2028

Last Updated

February 24, 2026

Status Verified

February 1, 2026

Enrollment Period

5 years

First QC Date

November 17, 2021

Last Update Submit

February 23, 2026

Conditions

Keywords

Lupus Nephritis, anifrolumab, Systemic Lupus Erythematosus, intravenous

Outcome Measures

Primary Outcomes (1)

  • Difference in proportion of participants with CRR (Complete Renal Response) in anifrolumab group compared with placebo group

    CRR is defined as: * UPCR ≤ 0.5 mg/mg * eGFR ≥ 60 mL/min/1.73 m2 or no decrease from baseline of ≥ 20%

    Week 52

Secondary Outcomes (14)

  • Difference in proportion of participants achieving sustained OCS reduction in anifrolumab group compared with placebo group

    from Week 24 through Week 52

  • HR of achieving sustained CRR in anifrolumab compared with placebo group

    baseline through Week 52

  • Difference in the mean standardized AUC for UPCR between anifrolumab and placebo participants

    baseline through Week 52

  • Difference in proportion of participants with CRR in anifrolumab group compared with placebo group

    Week 24

  • HR to summarize the difference in the risk of hazard of renal-related event or death at any given time between anifrolumab and placebo participants

    Through Week 52

  • +9 more secondary outcomes

Study Arms (2)

Anifrolumab

EXPERIMENTAL

Solution for intravenous infusion

Drug: Anifrolumab

Placebo

PLACEBO COMPARATOR

Solution for intravenous infusion

Drug: Placebo

Interventions

Anifrolumab intravenous infusion (IV)

Also known as: Medi-546
Anifrolumab

Placebo intravenous infusion (IV)

Placebo

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Active proliferative LN Class III or IV either with or without the presence of Class V according to the 2003 ISN/RPS classification
  • Renal biopsy obtained within 6 months prior to signing the ICF or during Screening Period.
  • Urine protein to creatinine ratio \> 1 mg/mg (113.17 mg/mmol)
  • eGFR ≥ 35 mL/min/1.73 m2 (as calculated by the Chronic Kidney Disease Epidemiology Collaboration formula).
  • Fulfills updated 2019 EULAR/ACR SLE classification criteria.
  • No signs of symptoms of active TB prior to or during screening or no treatment for latent TB

You may not qualify if:

  • A diagnosis of pure Class V LN based on the renal biopsy obtained within 6 months prior to signing the ICF or during Screening.
  • Known history of a primary immunodeficiency, splenectomy, or any underlying condition that predisposes the participant to infection, or a positive result for HIV confirmed by the central lab at Screening - an HIV test must be performed during Screening, and the result should be available prior to Week 0 (Day 1).
  • Evidence of hepatitis C or active hepatitis B.
  • Any history of cancer except sucessfully cured skin squamos or basal skin carcinoma and cervical cancer in situ.
  • Receipt of the following for the current LN flare (ie, since the qualifying renal biopsy): IV cyclophosphamide \> 2 pulses of high-dose (≥ 0.5 g/m2) or \> 4 doses of low dose (500 mg every 2 weeks) or Average MMF \> 2.5 g/day (or \> 1800 mg/day of enteric coated mycophenolate sodium) for more than 8 weeks or Tacrolimus \> 4 mg/day for more than 8 weeks; Cyclosporine for more than 8 weeks or during last 8 weeks prior to signing the ICF; Voclosporin for more than 8 weeks or during last 8 weeks prior to signing the ICF; Belimumab for more than 12 weeks or during last 12 weeks prior the ICF.
  • Previous receipt of \>◦2 investigation treatments (other than anifrolumab) for LN or SLE since time of diagnosis and through the ICF.
  • Known intolerance to ≤ 1.0 g/day of MMF.
  • Any history of severe COVID-19 infection.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (167)

Research Site

Glendale, Arizona, 85306, United States

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La Palma, California, 90623, United States

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Los Angeles, California, 90095, United States

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Upland, California, 91786, United States

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Plantation, Florida, 33324, United States

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Atlanta, Georgia, 30308, United States

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Louisville, Kentucky, 40202, United States

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Summit, New Jersey, 07901, United States

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Manhasset, New York, 11030, United States

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New York, New York, 10016, United States

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Winston-Salem, North Carolina, 27157, United States

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Middleburg Heights, Ohio, 44130, United States

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Colleyville, Texas, 76034, United States

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Edinburg, Texas, 78539, United States

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El Paso, Texas, 79902, United States

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Houston, Texas, 77054, United States

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CABA, C1425EOE, Argentina

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Ciudad de Buenos Aires, C1015ABO, Argentina

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La Plata, 1900, Argentina

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Rosario, S2000PBJ, Argentina

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San Juan, 5400, Argentina

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Brussels, 1200, Belgium

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Leuven, 3000, Belgium

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Liège, 4000, Belgium

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Belo Horizonte, 30130 100, Brazil

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Campinas, 13087-567, Brazil

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Cuiabá, 78020-500, Brazil

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Maringá, 87060-040, Brazil

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Porto Alegre, 90035-903, Brazil

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Recife, 50740-465, Brazil

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Salvador, 40150-150, Brazil

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São José do Rio Preto, 15090-000, Brazil

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São Paulo, 04014-002, Brazil

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São Paulo, 04036-002, Brazil

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São Paulo, 05403-9000, Brazil

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Plovdiv, 4002, Bulgaria

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Sofia, 1431, Bulgaria

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Beijing, 100034, China

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Beijing, 100044, China

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Bengbu, 233004, China

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Chengdu, 610072, China

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Guangzhou, 510530, China

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Haikou, 570311, China

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Hangzhou, 310009, China

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Jinan, 250021, China

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Jining, 272011, China

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Nanchang, 330006, China

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Nanjing, 210009, China

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Nanjing, 210029, China

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Nanning, 530021, China

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Shanghai, 200025, China

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Shanghai, 200040, China

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Shengyang, 110004, China

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Shenzhen, 518036, China

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Shijiazhuang, 050001, China

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Tianjin, 300201, China

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Wuhan, 430060, China

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Wuxi, 214023, China

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Xi'an, 710061, China

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Zhengzhou, 450000, China

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Barranquilla, 080020, Colombia

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Medellín, 050010, Colombia

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Medellín, 050025, Colombia

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Aurillac, 15002, France

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Bordeaux, 33076, France

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Marseille, 13005, France

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Paris, 75013, France

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Paris, 75018, France

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Paris, 75679, France

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Strasbourg, 67098, France

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Toulouse, 31059, France

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Cologne, 50937, Germany

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Dresden, 1307, Germany

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Hanover, 30625, Germany

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Heidelberg, 69120, Germany

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Kirchheim, 73230, Germany

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Mainz Am Rhein, 55131, Germany

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Budapest, 1085, Hungary

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Budapest, 1097, Hungary

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Debrecen, 4032, Hungary

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Ahmedabad, 380005, India

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Ahmedabad, 382421, India

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Dehradun, 248001, India

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Delhi, 110029, India

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Hyderabad, 500082, India

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Kolkata, 700020, India

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Nadiād, 387001, India

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Pune, 411001, India

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Secunderabad, 500003, India

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Vijayawada, 522002, India

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Visakapatnam, 530013, India

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Ancona, 60126, Italy

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Bologna, 40138, Italy

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Cona, 44124, Italy

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Eboli, 84025, Italy

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Padua, 35128, Italy

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Roma, 00161, Italy

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Bunkyō City, 113-8655, Japan

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Chiba, 260-8712, Japan

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Hiroshima, 734-8551, Japan

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Kita-gun, 761-0793, Japan

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Kitakyushu-shi, 807-8555, Japan

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Matsumoto-shi, 390-8621, Japan

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Nagasaki, 852-8501, Japan

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Okayama, 700-8558, Japan

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Ono, 675-1392, Japan

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Sagamihara-shi, 252-0375, Japan

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Sendai, 980-0872, Japan

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Shinagawa-ku, 142-0054, Japan

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Shinjuku-ku, 160-8582, Japan

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Shinjuku-ku, 162-8655, Japan

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Shinjuku-ku, 162-8666, Japan

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Toyoake-shi, 470-1192, Japan

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Batu Caves, 68100, Malaysia

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Ipoh, 30450, Malaysia

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Kajang, 43000, Malaysia

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Kuala Lumpur, 59100, Malaysia

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Kuantan, 25100, Malaysia

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Taiping, 34000, Malaysia

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Chihuahua City, 31000, Mexico

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Guadalajara, 44160, Mexico

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Guadalajara, 44650, Mexico

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México, 06726, Mexico

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México, 14080, Mexico

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San Luis Potosí City, 78290, Mexico

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Amsterdam, 1105 AZ, Netherlands

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Lima, 15023, Peru

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Lima, 15046, Peru

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Lima, 15102, Peru

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Lima, L34, Peru

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Lima, LIMA 27, Peru

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Lima, LIMA 29, Peru

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Lodz, 92-213, Poland

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Olsztyn, 10-561, Poland

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Opole, 46-020, Poland

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Poznan, 60-355, Poland

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Poznan, 61-545, Poland

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Rzeszów, 35-301, Poland

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Warsaw, 02-006, Poland

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Caguas, 00725, Puerto Rico

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Moscow, 115522, Russia

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Kaohsiung City, 833, Taiwan

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New Taipei City, 220, Taiwan

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Taichung, 40447, Taiwan

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Taichung, 40705, Taiwan

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Taipei, 11217, Taiwan

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Taipei, 114, Taiwan

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Taipei, 235, Taiwan

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Bangkok, 10220, Thailand

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Bangkok, 10330, Thailand

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Hat Yai, 90110, Thailand

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Muang, 50200, Thailand

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Ratchathewi, 10400, Thailand

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Adapazarı, 54290, Turkey (Türkiye)

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Ankara, 06100, Turkey (Türkiye)

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Ankara, Turkey (Türkiye)

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Istanbul, 34865, Turkey (Türkiye)

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Istanbul, Turkey (Türkiye)

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Izmir, 35965, Turkey (Türkiye)

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Kahramanmaraş, 46100, Turkey (Türkiye)

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Kayseri, 38039, Turkey (Türkiye)

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Kocaeli, 41380, Turkey (Türkiye)

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Hanoi, 100000, Vietnam

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Hanoi, 10000, Vietnam

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Hà Nội, 100000, Vietnam

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Ho Chi Minh City, 700000, Vietnam

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Hochiminh, 70000, Vietnam

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Related Publications (1)

  • Avasare R, Drexler Y, Caster DJ, Mitrofanova A, Jefferson JA. Management of Lupus Nephritis: New Treatments and Updated Guidelines. Kidney360. 2023 Oct 1;4(10):1503-1511. doi: 10.34067/KID.0000000000000230.

MeSH Terms

Conditions

Lupus NephritisLupus Erythematosus, Systemic

Interventions

anifrolumab

Condition Hierarchy (Ancestors)

GlomerulonephritisNephritisKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double Blind (Participant, Care Provider and Investigator)
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 17, 2021

First Posted

November 30, 2021

Study Start

February 15, 2022

Primary Completion (Estimated)

February 26, 2027

Study Completion (Estimated)

December 5, 2028

Last Updated

February 24, 2026

Record last verified: 2026-02

Data Sharing

IPD Sharing
Will share

Qualified researchers can request access to anonymized individual patient-level data from AstraZeneca group of companies sponsored clinical trials via the request portal. All request will be evaluated as per the AZ disclosure commitment: https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure. Yes, indicates that AZ are accepting requests for IPD, but this does not mean that all requests will be shared.

Shared Documents
STUDY PROTOCOL, SAP
Time Frame
AstraZeneca will meet or exceed data availability as per the commitments made to the EFPIA Pharma Data Sharing Principles. For details of our timelines, please rerefer to our disclosure commitment at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
Access Criteria
When a request has been approved AstraZeneca will provide access to the de-identified individual patient-level data in an approved sponsored tool. Signed Data Sharing Agreement (non-negotiable contract for data accessors) must be in place before accessing requested information. Additionally, all users will need to accept the terms and conditions of the SAS MSE to gain access. For additional details, please review the Disclosure Statements at https://astrazenecagrouptrials.pharmacm.com/ST/Submission/Disclosure.
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