NCT05090566

Brief Summary

The purpose of this study is to determine the Recommended Phase 2 Dose and clinical benefit of elranatamab in combination with other anti-cancer therapies in participants with multiple myeloma.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
46

participants targeted

Target at P50-P75 for phase_2 multiple-myeloma

Timeline
Completed

Started Oct 2021

Geographic Reach
2 countries

25 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 8, 2021

Completed
17 days until next milestone

First Posted

Study publicly available on registry

October 25, 2021

Completed
2 days until next milestone

Study Start

First participant enrolled

October 27, 2021

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 13, 2025

Completed
1 year until next milestone

Results Posted

Study results publicly available

February 23, 2026

Completed
16 days until next milestone

Study Completion

Last participant's last visit for all outcomes

March 11, 2026

Completed
Last Updated

April 24, 2026

Status Verified

April 1, 2026

Enrollment Period

3.3 years

First QC Date

October 8, 2021

Results QC Date

February 4, 2026

Last Update Submit

April 6, 2026

Conditions

Keywords

PF-06863135, Multiple Myeloma, BCMA, elranatamab, bispecific antibody, MagnetisMM-4

Outcome Measures

Primary Outcomes (2)

  • SSA: Number of Participants With Dose Limiting Toxicities (DLTs)- Phase 1b Dose Escalation

    DLT- Hematological:Grade (G)4 neutropenia \>5 days; febrile neutropenia; G\>=3 neutropenia, infection; G4 thrombocytopenia; G3 thrombocytopenia and G\>=2 bleeding. Non-hematological: G\>=4 adverse events(AEs); G3 cytokine release syndrome(CRS) \[except CRS not been maximally treated or improved to G\<=1 in 48 hours\]; G3 AEs (except AEs attributed to CRS, G3 nausea, vomiting, diarrhea that improve to G2\<=72 hours after maximal medical management has been initiated, G3 fatigue \< 1 week); confirmed drug-induced liver injury meeting Hy's law criteria; G3-4 laboratory abnormalities(except not associated with clinical sequelae and improve to G=\<2 in 72 hours); G2 clinically important/persistent AEs(cause significant dose delay/reduction) may be DLT; G3 injection site reaction, allergic reaction, anaphylaxis. Common Terminology Criteria for Adverse Events(CTCAE) version 5.0: G1:mild AE, G2:moderate, G3:severe, G4:life-threatening consequences; urgent intervention indicated, G5:death related to AE.

    From Cycle 0 Day 1 through Cycle 1 Day 28 (approximately up to 35 days)

  • SSB: Number of Participants With DLTs- Phase 1b

    Hematological: G4 neutropenia \>5 days; febrile neutropenia; G\>=3 neutropenia with infection; G4 thrombocytopenia; G3 thrombocytopenia with G\>=2 bleeding. Non-hematological: G\>=4 AEs; G3 CRS (except CRS events: not been maximally treated or improved to grade \<=1 within 48 hours); G3 AEs (except: AEs attributed to CRS, G3 nausea, vomiting and diarrhea that improve to G2\<=72 hours after maximal medical management has been initiated, G3 fatigue \< 1 week); confirmed drug-induced liver injury meeting Hy's law criteria; G 3-4 laboratory abnormalities (except: not associated with clinical sequelae and improve to G=\<2 within 72 hours); Other clinically important/persistent AEs (that cause significant dose delay/reduction) may be DLT; G3 injection site reaction. CTCAE version 5.0: G1: Mild AE, G2: Moderate, G3: Severe, G4: Life-threatening consequences; urgent intervention indicated, G5: Death related to AE.

    From Cycle 0 Day 1 through Cycle 1 Day 28 (approximately up to 42 days)

Secondary Outcomes (32)

  • SSA: Number of Participants With Treatment Emergent Adverse Events (TEAEs) and Treatment Related TEAEs- Phase 1b

    From treatment initiation till study completion

  • SSA: Number of Participants With Severity of AEs According to Cytokine Release Syndrome (CRS) Graded According to American Society for Transplantation and Cellular Therapy (ASTCT) Grading Criteria 2019- Phase 1b

    From treatment initiation till study completion

  • SSA: Number of Participants With Severity of AEs According to Immune Effector Cell-associated Neurotoxicity Syndrome ICANS Graded According to ASTCT Grading Criteria 2019- Phase 1b

    From treatment initiation till study completion

  • SSA: Number of Participants With Laboratory Abnormalities- Phase 1b

    From treatment initiation till study completion

  • SSA: Objective Response Rate (ORR) as Per International Myeloma Working Group (IMWG) Criteria as Determined by Investigator- Phase 1b

    From treatment initiation till study completion

  • +27 more secondary outcomes

Study Arms (2)

Sub-Study A

EXPERIMENTAL

BCMA-CD3 bispecific antibody + gamma secretase inhibitor

Drug: Elranatamab + Nirogacestat

Sub-Study B

EXPERIMENTAL

BCMA-CD3 bispecific antibody + immunomodulatory drug

Drug: Elranatamab + lenalidomide + dexamethasone

Interventions

BCMA-CD3 bispecific antibody + gamma secretase inhibitor

Also known as: PF-06863135, Ogsiveo
Sub-Study A

BCMA-CD3 bispecific antibody + immunomodulatory

Also known as: PF-06863135; Revlimid
Sub-Study B

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Relapsed/refractory multiple myeloma with at least 3 prior lines of therapy
  • Refractory to at least one IMiD, one proteasome inhibitor, and one anti-CD38 antibody
  • Measurable disease defined by at least one of the following:
  • Serum M-protein \>/= 0.5 g/dL by SPEP
  • Urinary M-protein excretion \>/= 200 mg/24 hours by UPEP
  • Serum immunoglobulin FLC \>/= 10 mg/dL (\>/= 100 mg/L) AND abnormal serum immunoglobulin kappa to lambda FLC ratio
  • ECOG performance status 0 -1
  • Resolved acute effects of any prior therapy to baseline severity or CTCAE Grade \</= 1

You may not qualify if:

  • Active plasma cell leukemia
  • Amyloidosis
  • Stem cell transplant with 12 weeks prior to enrollment, or active GVHD
  • POEMS syndrome
  • Any active uncontrolled bacterial, fungal, or viral infection
  • Impaired cardiovascular function or clinically significant cardiovascular diseases within 6 months prior to enrollment
  • Previous administration with an investigational drug within 30 days or 5 half-lives preceding the first dose of study treatment (whichever is longer)
  • Sub-Study A Only: Previous treatment with BCMA bispecific antibody
  • Sub-Study B Only: Previous treatment with BCMA directed therapy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

Banner Gateway Medical Center

Gilbert, Arizona, 85234, United States

Location

Banner Gateway Medical Pavilion

Gilbert, Arizona, 85234, United States

Location

Banner MD Anderson Cancer Center

Gilbert, Arizona, 85234, United States

Location

Banner Health d.b.a. Banner MD Anderson Cancer Center

Phoenix, Arizona, 85012, United States

Location

Beverly Hills Cancer Center

Beverly Hills, California, 90211, United States

Location

Clinical Research Advisors

Encino, California, 91316, United States

Location

Clinical Research Advisors

Los Angeles, California, 90020, United States

Location

Cedars Sinai Medical Center Oncology IDS Pharmacy Attn:Suwicha Limvorasak ,PharmaD

Los Angeles, California, 90048, United States

Location

Cedars Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Cedars-Sinai Medical Center, Samuel Oschin Comprehensive Cancer Institute (SOCCI)

Los Angeles, California, 90048, United States

Location

Clinical Research Advisors

Los Angeles, California, 90048, United States

Location

Cedars-Sinai Tarzana

Tarzana, California, 91356, United States

Location

Sylvester Comprehensive Cancer Center - The Lennar Foundation Medical Center

Coral Gables, Florida, 33146, United States

Location

University of Miami

Coral Gables, Florida, 33146, United States

Location

Sylvester Comprehensive Cancer Center- Deerfield Beach

Deerfield Beach, Florida, 33442, United States

Location

Sylvester Comprehensive Cancer Center

Miami, Florida, 33136, United States

Location

UHealth Tower

Miami, Florida, 33136, United States

Location

The Johns Hopkins University School of Medicine

Baltimore, Maryland, 21205, United States

Location

OIDS, The Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins

Baltimore, Maryland, 21231, United States

Location

The Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins (Also Imaging Facility)

Baltimore, Maryland, 21231, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Arthur J.E. Child Comprehensive Cancer Centre

Calgary, Alberta, T2N 5G2, Canada

Location

The Ottawa Hospital - General Campus

Ottawa, Ontario, K1H 8L6, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Related Links

MeSH Terms

Conditions

Multiple Myeloma

Interventions

nirogacestatLenalidomideDexamethasone

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

PhthalimidesPhthalic AcidsAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsPiperidonesPiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIsoindolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, Fluorinated

Limitations and Caveats

Phase 2 of SSA was not conducted, based on sponsor's decision.

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 8, 2021

First Posted

October 25, 2021

Study Start

October 27, 2021

Primary Completion

February 13, 2025

Study Completion

March 11, 2026

Last Updated

April 24, 2026

Results First Posted

February 23, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations