NCT05076838

Brief Summary

This is a Phase 1/2a, open-label, single-dose, PK study of VALTOCO with open-label safety period in pediatric epilepsy subjects age 2 to 5 years.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
35

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Nov 2021

Typical duration for phase_1

Geographic Reach
1 country

13 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 15, 2021

Completed
28 days until next milestone

First Posted

Study publicly available on registry

October 13, 2021

Completed
26 days until next milestone

Study Start

First participant enrolled

November 8, 2021

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 11, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 11, 2025

Completed
Last Updated

August 11, 2025

Status Verified

August 1, 2025

Enrollment Period

3.3 years

First QC Date

September 15, 2021

Last Update Submit

August 5, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Maximum Plasma Concentration (Cmax) of diazepam after intranasal VALTOCO administered to subjects with epilepsy 2 to 5 years of age

    0-6 hours

Study Arms (1)

Valtoco In Pediatric Subjects with Epilepsy

EXPERIMENTAL

5 mg, 10 mg, or 15 mg dose of intranasal VALTOCO will be administered based on the subject's body weight.

Drug: Diazepam Nasal Spray [Valtoco]

Interventions

5 mg, 10 mg, or 15 mg dose of intranasal VALTOCO will be administered based on the subject's body weight.

Valtoco In Pediatric Subjects with Epilepsy

Eligibility Criteria

Age2 Years - 5 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Subject has a clinical diagnosis of epilepsy and, in the opinion of the Investigator, may need benzodiazepine intervention for seizure control.
  • Subjects having either partial or generalized epilepsy with motor seizures or seizures with clear alteration of awareness, for which rescue medications have been used at least once in the last 3 months or in the opinion of the investigator, may need a benzodiazepine intervention for seizure control 1-2 times every 3 months on average.

You may not qualify if:

  • Subjects whose body weight are \< 6 kg or \> 33 kg.
  • Subject is undergoing intracranial electroencephalogram (EEG) monitoring.
  • In the opinion of the investigator, a history of clinically significant medical history that would jeopardize the safety of the subject or impact the validity of the study results (such as significant gastrointestinal, renal, nasal polyps or any nasal passage abnormality that could interfere with nasal spray administration.
  • Subject has had significant traumatic injury, major surgery or open biopsy within 30 days prior to study screening.
  • Participation in a clinical trial within 30 days prior to the first dose of study drug.
  • Inadequate or difficult venous access that may jeopardize the quality or timing of the PK samples.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Northwest Florida Clinical Research Group, LLC.

Gulf Breeze, Florida, 32561, United States

Location

Nicklaus Children's Hospital

Miami, Florida, 33155, United States

Location

AdventHealth Research Institute

Orlando, Florida, 32803, United States

Location

Center for Rare Neurological Diseases

Norcross, Georgia, 30093, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

University of Missouri Women & Children's Hospital

Columbia, Missouri, 65201, United States

Location

Northeast Regional Epilepsy Group

Hackensack, New Jersey, 07601, United States

Location

Boston Children's Health Physicians

Hawthorne, New York, 10532, United States

Location

University of Rochester

Rochester, New York, 14623, United States

Location

Duke University Hospital

Durham, North Carolina, 27710, United States

Location

Le Bonheur Children's Hospital

Memphis, Tennessee, 38105, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75225, United States

Location

Children's Hospital of the King's Daughters

Norfolk, Virginia, 23507, United States

Location

MeSH Terms

Conditions

Epilepsy

Interventions

Diazepam

Condition Hierarchy (Ancestors)

Brain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

BenzodiazepinonesBenzodiazepinesBenzazepinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 15, 2021

First Posted

October 13, 2021

Study Start

November 8, 2021

Primary Completion

March 11, 2025

Study Completion

March 11, 2025

Last Updated

August 11, 2025

Record last verified: 2025-08

Locations