NCT05043506

Brief Summary

A retrospective observational analysis of de-identified data from a multinational medical record review to describe patient characteristics, treatment patterns, and effectiveness of palbociclib + AI as first-line therapy among adult patients with HR+/HER2- advanced breast cancer (ABC) in Europe

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,939

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Feb 2022

Geographic Reach
7 countries

64 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 7, 2021

Completed
7 days until next milestone

First Posted

Study publicly available on registry

September 14, 2021

Completed
5 months until next milestone

Study Start

First participant enrolled

February 8, 2022

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 2, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 2, 2023

Completed
Last Updated

March 27, 2024

Status Verified

March 1, 2024

Enrollment Period

1.7 years

First QC Date

September 7, 2021

Last Update Submit

March 25, 2024

Conditions

Keywords

breast cancerPalbociclibReal-world dataCDK4/6effectiveness

Outcome Measures

Primary Outcomes (1)

  • Real-world progression free survival

    Total time from the treatment line start date to the date of disease progression confirmed by clinician assessment or the date of censoring, as measured in months

    Time from treatment line start date to clinician assessed date of disease progression, date of death, or date of censoring

Secondary Outcomes (2)

  • Overall survival

    Time from treatment line start date to clinician assessed date of death, or date of censoring

  • Time to first objective tumor response

    Time from treatment line start date to clinician-assessed first date of objective response or date of censoring

Study Arms (2)

Palbociclib + aromatase inhibitor

Adult patients with advanced breast cancer patients who initiated Palbociclib + an aromatase inhibitor as first line therapy between September 1, 2016, and July 31, 2020.

Drug: Palbociclib + aromatase inhibitor

Aromatase inhibitor

Adult patients with advanced breast cancer patients who initiated an aromatase inhibitor as first line therapy between January 1, 2010,, and July 31, 2020

Drug: Aromatase inhibitor

Interventions

Palbociclib + an aromatase inhibitor therapy

Also known as: Palbociclib + an aromatase inhibitor therapy
Palbociclib + aromatase inhibitor

Aromatase inhibitor monotherapy

Also known as: Aromatase inhibitor monotherapy
Aromatase inhibitor

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Adult patients with HR+/HER2- advanced breast cancer treated with palbociclib + an aromatase inhibitor or an aromatase inhibitor alone between January 1, 2010 to July 31, 2020

You may qualify if:

  • Is male or female
  • Has histologically or cytologically confirmed breast cancer diagnosis (HR+/HER2- breast cancer)
  • Has received a diagnosis of locally advanced breast cancer not amenable to curative radiation or surgical cure or of metastatic breast cancer (i.e., advanced breast cancer \[ABC\]); diagnosis may be de novo (initial diagnosis at ABC stage) or recurrent from earlier-stage disease (initial diagnosis of earlier-stage disease with subsequent progression to advanced disease)
  • Has initiated a required first-line therapy of interest: Palbociclib plus AI as first-line therapy for ABC between September 1, 2016, and July 31, 2020, or AI monotherapy as first-line therapy for ABC between January 1, 2010,, and July 31, 2020
  • Was aged 18 years or older at the time of diagnosis of ABC
  • Is living or deceased at the time of record abstraction
  • Has a complete medical record, covering treatment for ABC, including any transfer record from other facilities (if applicable) that is available to the abstractor for data abstraction

You may not qualify if:

  • The patient's first treatment after ABC diagnosis was chemotherapy (including induction chemotherapy)
  • The patient has evidence of other active malignant neoplasms within 3 years (except nonmelanoma skin cancer or carcinoma in situ) prior to diagnosis of ABC; patients diagnosed with second primary cancer after ABC diagnosis will not be excluded
  • The patient has evidence of prior treatment with any CDK4/6 inhibitor (i.e. palbociclib, abemaciclib, ribociclib) in the early-stage breast cancer setting or treatment with abemaciclib or ribociclib in the ABC setting
  • The patient has participated in a clinical trial related to treatment of ABC (including after first-line therapy \[i.e., palbociclib plus AI or AI monotherapy\])

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (64)

Sankt Josef Hospital Braunau

Braunau am Inn, 5280, Austria

Location

Landesklinikum Krems

Krems, 3500, Austria

Location

Universitaetsklinikum Sankt Poelten

Sankt Pölten, 3100, Austria

Location

Priv. Doz. OA Dr. Michael Hubalek

Schwaz, 6130, Austria

Location

UZ Leuven

Leuven, 3000, Belgium

Location

Universitätsklinikum Würzburg Frauenklinik und Poliklinik

Würzburg, Bavaria, 97080, Germany

Location

MediOnko-Institut GbR

Berlin, Brandenburg, 13597, Germany

Location

Kreisklinikum Böblingen gGmbH, Frauenklinik Böblingen

Sindelfingen, Landkreis Boblingen, 71065, Germany

Location

Universitatsklinikum Essen

Essen, North Rhine-Westphalia, 45147, Germany

Location

Ruppiner Kliniken GmbH

Neuruppin, Ostprignitz-ruppin, 16816, Germany

Location

Frauenarztpraxis

Ilsede, Peine, D-31241, Germany

Location

Institut für Versorgungsforschung GbR

Mainz, Rhineland-Palatinate, 55116, Germany

Location

Universität des Saarlandes

Saarbrücken, Saarland, 66123, Germany

Location

Studienzentrum UnterEms

Emden, Saxony, 26721, Germany

Location

Universitätsklinikum Leipzig

Leipzig, Saxony, 04103, Germany

Location

Group practice Goehler

Dresden, 01127, Germany

Location

Bethanien Center for Hematology and Oncology

Frankfurt, 60389, Germany

Location

Überörtliche Gemeinschaftspraxis

Hamburg, 48415, Germany

Location

St. Vincenz-Krankenhaus GmbH

Paderborn, 33098, Germany

Location

Gynäkologie Kompetenzzentrum Praxis Dr. med. Carsten Hielscher

Stralsund, 18439, Germany

Location

Medizinische Studiengesellschaft NORD-WEST GmbH

Westerstede, 26655, Germany

Location

Hospital Universitario de Puerto Real

Cadiz, Andalusia, 11510, Spain

Location

Institut Catalâ Oncologia-L'Hospitalet

L'Hospitalet de Llobregat, Barcelona [barcelona], 08908, Spain

Location

Hospital Universitario de Basurto

Bilbao, Bizkaia, 48013, Spain

Location

Complejo Hospitalario Universitario de Vigo. Area Sanitaria de Vigo. Hospital Alvaro Cunqueiro

Vigo, Pontevedra, Cantabria Castilla Y LEON, 36211, Spain

Location

Hospital General Universitario Morales Meseguer

Murcia, Comunidad de Murcia, 30008, Spain

Location

Hospital San Jorge Huesca

Zaragoza, Huesca/ Aragon, 50009, Spain

Location

Hospital Puerta de Hierro

Majadahonda, Madrid, 28222, Spain

Location

Hospital Universitario Quiron Madrid

Pozuelo de Alarcón, Madrid, 28223, Spain

Location

Hospital nuestra señora del prado de Toledo

Talavera de La Reina, Toledo, Madrid/castilla LA Mancha, 45600, Spain

Location

Complejo Hospitalario de Navarra

Pamplona, Navarre, 31008, Spain

Location

Hospital Clínico de Santiago de Compostela

Santiago de Compostela, Santiago de Compostela/cantabria, 15706, Spain

Location

Hospital Universitario Virgen Del Rocio

Seville, Sevila, 41013, Spain

Location

Hospital de Sagunto

Sagunto, Valencia, Valencia/madrid Castilla LA Mancha, 46520, Spain

Location

Complejo Universitario de Albacete

Albacete, 02006, Spain

Location

Hospital Universitario Virgen de Las Nieves

Granada, 18014, Spain

Location

Complejo Asistencial Universitario de Leon

León, 24007, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Universitario Marques de Valdecilla

Santander, 39008, Spain

Location

Hospital de Sant Pau i Santa Tecla

Tarragona, 43003, Spain

Location

Hospital Universitario Dr. Peset

Valencia, 46017, Spain

Location

Mälarsjukhuset

Eskilstuna, Södermanlands LÄN [se-04], 631 88, Sweden

Location

St Goran Hospital

Bromma, 167 56, Sweden

Location

Örebro University Hospital

Örebro, 70286, Sweden

Location

Uppsala University Hospital

Uppsala, 751 85, Sweden

Location

Kantonsspital Baden AG

Baden, 5404, Switzerland

Location

Kantonsspital Baselland

Liestal, Switzerland

Location

Buckinghamshire Healthcare NHS Trust, Stoke Mandeville Hospital

Buckinghamshire, Buckinghamshire, HP7 0JD, United Kingdom

Location

Glan Clwyd Hospital

Rhyl, Denbighshire, LL18 5UJ, United Kingdom

Location

Western General Hospital

Waterloo Place, Edinburgh, EH1 3EG, United Kingdom

Location

Beatson West of Scotland Cancer Centre

Glasglow, Glasglow City, Scotland, G12 0YH, United Kingdom

Location

Ysbyty Gwynedd Hospital

Bangor, Gwynedd, LL57 2PW, United Kingdom

Location

Queen Elizabeth Hospital

Kings Lynn, Norfolk, PE30 4ET, United Kingdom

Location

Borders General Hospital

Roxburghshire, Scotland, TD6 9BS, United Kingdom

Location

Forth Valley Royal Hospital

Stirling, Scotland, FK9 4SW, United Kingdom

Location

Shrewsbury and Telford Hospital NHS Trust

Shrewsbury, Shropshire, SY3 8XQ, United Kingdom

Location

Wrexham Maelor Hospital

Wrexham, Wales, LL13 7TD, United Kingdom

Location

Bradford Teaching Hospitals NHS Foundation Trust

Bradford, WEST Yorkshire, BD9 6RJ, United Kingdom

Location

Airedale NHS Foundation Trust

Keighley, WEST Yorkshire, BD20 6TD, United Kingdom

Location

Royal United Hospital Bath NHS Trust

Bath, BA1 3NG, United Kingdom

Location

Royal Blackburn Hospital

Blackburn, BB2 3HH, United Kingdom

Location

Royal Bournemouth Hospital

Bournemouth, BH7 7DW, United Kingdom

Location

Royal Cornwall Hospital

Cornwall, TR1 3LJ, United Kingdom

Location

Nottingham University Hospitals NHS Trust

Nottingham, GGS 1PB, United Kingdom

Location

Related Links

MeSH Terms

Conditions

Breast Neoplasms

Interventions

palbociclibAromatase Inhibitors

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsBreast DiseasesSkin DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Steroid Synthesis InhibitorsEnzyme InhibitorsMolecular Mechanisms of Pharmacological ActionPharmacologic ActionsChemical Actions and UsesEstrogen AntagonistsHormone AntagonistsHormones, Hormone Substitutes, and Hormone AntagonistsPhysiological Effects of Drugs

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
RETROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 7, 2021

First Posted

September 14, 2021

Study Start

February 8, 2022

Primary Completion

November 2, 2023

Study Completion

November 2, 2023

Last Updated

March 27, 2024

Record last verified: 2024-03

Data Sharing

IPD Sharing
Will not share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

Locations