NCT04942080

Brief Summary

Prospective study to evaluate the relevance of CALR allele burden monitoring as a molecular marker of disease progression.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
260

participants targeted

Target at P75+ for not_applicable

Timeline
48mo left

Started Oct 2021

Longer than P75 for not_applicable

Geographic Reach
1 country

10 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress53%
Oct 2021Apr 2030

First Submitted

Initial submission to the registry

June 9, 2021

Completed
19 days until next milestone

First Posted

Study publicly available on registry

June 28, 2021

Completed
4 months until next milestone

Study Start

First participant enrolled

October 28, 2021

Completed
5.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 28, 2027

Expected
3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

April 28, 2030

Last Updated

March 6, 2026

Status Verified

March 1, 2026

Enrollment Period

5.5 years

First QC Date

June 9, 2021

Last Update Submit

March 5, 2026

Conditions

Keywords

CALRMyeloproliferative NeoplasmEssential ThrombocythemiaPrimary MyelofibrosisThrombocytosis

Outcome Measures

Primary Outcomes (1)

  • For each disease, Hazard Ratio of the different trajectories of CALR allele burden to explain the time to onset of disease progression by the clinicobiological score.

    Clinicobiological score : For ET, disease progression if ≥ 1 of: * leukocytosis \> 12 G/L or myelemia \> 10% or erythroblasts \> 1%, * anemia or thrombocytopenia not related to drug toxicity, * development or worsening of splenomegaly, * development of thrombocytosis (platelets \> 450 G/L) on cytoreductive therapy, * poor disease control (at least one change in therapy for reasons other than adverse events), * hematologic transformation or death related to hematologic pathology. For MF, disease progression if ≥ 1 of: * anemia \< 100 g/L, neutropenia \< 1 G/L, thrombocytopenia \< 100 G/L and/or development of general signs not previously present or recurring after improvement, * increase in leukocytosis \> 25 G/L not previously present, * appearance or aggravation of transfusion dependence, * appearance (\> 5 cm) or aggravation (\> 50%) of splenomegaly, * leukemic transformation or death related to the hematologic pathology.

    3 years follow-up

Secondary Outcomes (1)

  • A multinomial logistic model will be performed to identify the characteristics associated with the different trajectories of CALR allele burden (pathology, treatment, additional mutations, type of CALR mutation).

    3 years follow-up

Study Arms (1)

CALRSUIVI cohort

EXPERIMENTAL
Biological: CALR allele burden quantification

Interventions

* DNA extraction from blood sample for CALR mutation quantification (fragment analysis) * at diagnosis and follow-up (inclusion period: 3 years) * max 1 sample/year * secondary outcome: mutational landscape by Next Generation Sequencing (NGS) analysis at diagnosis

CALRSUIVI cohort

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • adults (age ≥18 years),
  • affiliated to the national social security system,
  • with CALR mutated myeloproliferative neoplasm diagnosed between 2006 - 2020,
  • for which at least one sample is available at the time of diagnosis or before cytoreductive treatment,
  • who signed the consent to participate in the study,
  • included, or consenting to be included, in the national clinical-biological database of France Intergroupe Syndrome Myéloprolifératifs (FIM).

You may not qualify if:

  • patient with another active hematological disease or cancer at the time of diagnosis,
  • person subject to legal protection scheme or incapable of giving consent.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

CHU Angers

Angers, France

RECRUITING

Chu Bordeaux

Bordeaux, 33604, France

RECRUITING

Chu Brest

Brest, 29200, France

RECRUITING

Ch Cholet

Cholet, 49300, France

RECRUITING

Ch Le Mans

Le Mans, 72037, France

RECRUITING

Ch Morlaix

Morlaix, 29672, France

RECRUITING

AP-HP Henri Mondor

Paris, 94010, France

RECRUITING

Chu Poitiers

Poitiers, 86021, France

RECRUITING

Ch Quimper

Quimper, 29107, France

RECRUITING

Chu Tours

Tours, 37000, France

RECRUITING

Related Publications (1)

  • Cottin L, Riou J, Orvain C, Ianotto JC, Boyer F, Renard M, Truchan-Graczyk M, Murati A, Jouanneau-Courville R, Allangba O, Mansier O, Burroni B, Rousselet MC, Quintin-Roue I, Martin A, Sadot-Lebouvier S, Delneste Y, Chretien JM, Hunault-Berger M, Blanchet O, Lippert E, Ugo V, Luque Paz D. Sequential mutational evaluation of CALR -mutated myeloproliferative neoplasms with thrombocytosis reveals an association between CALR allele burden evolution and disease progression. Br J Haematol. 2020 Mar;188(6):935-944. doi: 10.1111/bjh.16276. Epub 2019 Nov 11.

    PMID: 31710700BACKGROUND

MeSH Terms

Conditions

Myeloproliferative DisordersThrombocythemia, EssentialPrimary MyelofibrosisThrombocytosis

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesBlood Coagulation DisordersBlood Platelet DisordersHemorrhagic Disorders

Central Study Contacts

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
OTHER
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER GOV
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 9, 2021

First Posted

June 28, 2021

Study Start

October 28, 2021

Primary Completion (Estimated)

April 28, 2027

Study Completion (Estimated)

April 28, 2030

Last Updated

March 6, 2026

Record last verified: 2026-03

Locations