NCT04804033

Brief Summary

The purpose of this is study is to compare the efficacy of BHV-3500 (zavegepant) to placebo as a preventive treatment for migraine, as measured by the reduction in the number of migraine days per month.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,753

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2021

Typical duration for phase_2

Geographic Reach
1 country

116 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 5, 2021

Completed
13 days until next milestone

First Posted

Study publicly available on registry

March 18, 2021

Completed
8 days until next milestone

Study Start

First participant enrolled

March 26, 2021

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 21, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 21, 2024

Completed
1 year until next milestone

Results Posted

Study results publicly available

March 27, 2025

Completed
Last Updated

March 27, 2025

Status Verified

March 1, 2025

Enrollment Period

3 years

First QC Date

March 5, 2021

Results QC Date

March 6, 2025

Last Update Submit

March 25, 2025

Conditions

Keywords

Migraine PreventionPhonophobiaPhotophobiaNausea

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Observation Phase (OP) in the Number of Migraine Days Per Month Over Entire DBT Phase (Weeks 1 to 12)

    A migraine day was defined as any calendar day in which participant experienced a qualified migraine headache (onset, continuation or recurrence of migraine headache). A qualified migraine headache was defined as migraine with or without aura, lasting for greater than or equal to (\>=) 30 minutes, and met at least one of the following criteria (A and/or B): A. \>=2 of the following pain features: a. Unilateral location, b. Pulsating quality (throbbing), c. Moderate or severe pain intensity, d. Aggravation by or causing avoidance of routine physical activity (e.g. walking or climbing stairs) B. \>= 1 of following associated symptoms: a. Nausea and/or vomiting b. Photophobia and phonophobia. The number of migraine days per month were prorated to 28 days and derived as follows: 28\*(total number of migraine days through Month 3\[Weeks 1 to 12\] in on-DBT efficacy analysis period)/ (total number of eDiary efficacy data days through Month 3\[Weeks 1 to 12\] in the on-DBT efficacy analysis period).

    Observation Phase: 28 days prior to randomization and baseline; Entire DBT Phase: 12 weeks (Week 1 through 12)

Secondary Outcomes (20)

  • Percentage of Participants With >= 50 % Reduction in Number of Moderate to Severe Migraine Days Per Month Over Entire DBT Phase (Weeks 1 to 12)

    Entire DBT Phase: 12 weeks (Week 1 through 12)

  • Mean Change From Observation Phase in the Number of Migraine Days Per Month in the Last 4 Weeks (Weeks 9 to 12) of DBT Phase

    Observation Phase: 28 days prior to randomization and baseline; DBT Phase: last 4 weeks (Week 9 through 12)

  • Mean Change From Observation Phase in the Number of Migraine Days Per Month in the First 4 Weeks (Weeks 1 to 4) of DBT Phase

    Observation Phase: 28 days prior to randomization and baseline; DBT Phase: first 4 weeks (Week 1 through 4)

  • Mean Number of Acute Migraine -Specific Medication Days Per Month Over Entire DBT Phase (Weeks 1 to 12)

    Entire DBT Phase: 12 weeks (Week 1 through 12)

  • Mean Change From Baseline in the Migraine-specific Quality of Life Questionnaire (MSQ) v 2.1 Restrictive Role Function Domain Score at Week 12

    DBT Phase: Baseline (before dose on Day 1), Week 12

  • +15 more secondary outcomes

Study Arms (4)

BHV-3500 200mg

ACTIVE COMPARATOR

Zavegepant 200mg oral soft gel capsule.

Drug: BHV-3500 (zavegepant)

Placebo 200mg

PLACEBO COMPARATOR

Matching placebo 200mg oral soft gel capsule.

Drug: Placebo

BHV-3500 100mg

ACTIVE COMPARATOR

Zavegepant 100mg oral soft gel capsule.

Drug: BHV-3500 (zavegepant)

Placebo 100mg

PLACEBO COMPARATOR

Matching placebo 100mg oral soft gel capsule.

Drug: Placebo

Interventions

BHV-3500 (zavegepant) softgel capsule.

BHV-3500 100mgBHV-3500 200mg

Matching placebo softgel capsule.

Placebo 100mgPlacebo 200mg

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Subject has at least 1 year history of migraine (with or without aura) consistent with a diagnosis according to the International Classification of
  • Headache Disorders, 3rd Edition, including the following:
  • Age of onset of migraines prior to 50 years of age
  • Migraine attacks, on average, lasting 4 - 72 hours if untreated
  • Per subject report, at least 15 headache days per month, at lest 8 migraine days per month, and at least 1 headache-free day per month within the last 3 months prior to the Screening Visit
  • Eight or more migraine days during the Observation Period
  • or more headache days during the Observation Period
  • One or more non-headache days during the Observation Period
  • Ability to distinguish migraine attacks from tension/cluster headaches
  • Subjects on prophylactic migraine medication are permitted to remain on 1 medication with possible migraine-prophylactic effects if the dose has been stable for at least 3 months prior to the Screening Visit, and the dose is not expected to change during the course of the study.

You may not qualify if:

  • Subject with a history of HIV disease
  • Subject history with current evidence of uncontrolled, unstable or recently diagnosed cardiovascular disease, such as ischemic heart disease, coronary artery vasospasm, and cerebral ischemia. Subjects with Myocardial Infarction (MI), Acute Coronary Syndrome (ACS), Percutaneous Coronary Intervention (PCI), cardiac surgery, stroke or transient ischemic attack (TIA) during the 6 months prior to screening
  • Uncontrolled hypertension (high blood pressure), or uncontrolled diabetes (however subjects can be included who have stable hypertension and/or diabetes for at least 3 months prior to screening).
  • Subjects with major depressive episode or anxiety disorder which require more than 1 daily medication for each disorder or subjects with a major depressive episode within the last 12 months. Medications to treat major depressive disorder or an anxiety disorder must have been at a stable dose for at least 3 months prior to the Screening Visit.
  • Subjects with active chronic pain syndromes, other pain syndromes (including trigeminal neuralgia), psychiatric conditions, dementia, or significant neurological disorders (other than migraine) that, in the Investigator's opinion interfere with study assessments of safety or efficacy.
  • Subject has a history of gastric, or small intestinal surgery (including Gastric Bypass, Gastric Banding, Gastric Sleeve, Gastric Balloon, etc.), or has disease or condition (e.g. chronic pancreatitis, ulcerative colitis, etc.) that causes malabsorption.
  • Body mass index \> 33 kg/m2
  • History of gallstones or cholecystectomy.
  • The subject has a history or current evidence of any unstable medical conditions (e.g., history of congenital heart disease or arrhythmia, known or suspected infection, hepatitis B or C, or cancer) that, in the investigator's opinion, would expose them to undue risk of a significant adverse event (AE) or interfere with assessments of safety or efficacy during the course of the trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (116)

Xenoscience, Inc

Phoenix, Arizona, 85004, United States

Location

Tucson Neuroscience Research

Tucson, Arizona, 85710, United States

Location

Hope Clinical Research

Canoga Park, California, 91303, United States

Location

Axiom Research, Llc

Colton, California, 92324, United States

Location

Wr-Pri, Llc

Encino, California, 91316, United States

Location

eStudySite

La Mesa, California, 91942, United States

Location

Synergy San Diego

Lemon Grove, California, 91945, United States

Location

Collaborative Neuroscience Research, LLC.

Long Beach, California, 90806, United States

Location

Clinical Research Institute

Los Angeles, California, 90048, United States

Location

Wr-Pri, Llc

Newport Beach, California, 92660, United States

Location

Artemis Institute for Clinical Research

San Diego, California, 92103, United States

Location

California Neuroscience Research Medical Group, inc.

Sherman Oaks, California, 91403, United States

Location

CMR of Greater New Haven, LLC

Hamden, Connecticut, 06517, United States

Location

Ki Health Partners, LLc, dba New England Institute for Clinical Research

Stamford, Connecticut, 06905, United States

Location

Chase Medical Research, LLC

Waterbury, Connecticut, 06708, United States

Location

Neurology Offices of South Florida

Boca Raton, Florida, 33428, United States

Location

Accel Research Sites Network - Edgewater Clinical Research Unit

Edgewater, Florida, 32132, United States

Location

Complete Health Research

Edgewater, Florida, 32132, United States

Location

Sarkis Clinical Trials

Gainesville, Florida, 32607, United States

Location

Clinical Neuroscience Solutions, Inc.

Jacksonville, Florida, 32256, United States

Location

Multi-Specialty Research Associates, Inc.

Lake City, Florida, 32055, United States

Location

AppleMed Research Group, LLC

Miami, Florida, 33126, United States

Location

AppleMed Research Group, LLC

Miami, Florida, 33155, United States

Location

Brainstorm Research

Miami, Florida, 33176, United States

Location

The Neurology Research Group

Miami, Florida, 33176, United States

Location

Clinical Neuroscience Solutions, Inc.

Orlando, Florida, 32801, United States

Location

Complete Health Research

Ormond Beach, Florida, 32174, United States

Location

Ideal Clinical Research

Pembroke Pines, Florida, 33026, United States

Location

Clinical Research Center of Florida

Pompano Beach, Florida, 33060, United States

Location

Clin-Med Research & Development LLC

South Miami, Florida, 33143, United States

Location

Accel Research Sites Network - St. Petersburg Clinical Research Unit

St. Petersburg, Florida, 33709, United States

Location

ForCare Clinical Research

Tampa, Florida, 33613, United States

Location

JSV Clinical Research Study Inc

Tampa, Florida, 33634, United States

Location

CenExel iResearch, LLC

Decatur, Georgia, 30030, United States

Location

iResearch Atlanta LLC

Decatur, Georgia, 30030, United States

Location

Cedar Crosse Research Center

Chicago, Illinois, 60607, United States

Location

Clinical Investigation Specialists, Inc.

Gurnee, Illinois, 60031, United States

Location

Clinical Investigation Specialists, Inc

Gurnee, Illinois, 60031, United States

Location

MediSphere Medical Research Center, LLC.

Evansville, Indiana, 47714, United States

Location

MediSphere Medical Research Center, LLC

Evansville, Indiana, 47714, United States

Location

Meridian Clinical Research, LLC

Sioux City, Iowa, 51106, United States

Location

Alliance for Multispecialty Reseach, LLC

El Dorado, Kansas, 67042, United States

Location

Alliance for Multispecialty Research, LLC

Newton, Kansas, 67114, United States

Location

Collevtive Medical Research

Overland Park, Kansas, 66210, United States

Location

Kansas Institute of Research

Overland Park, Kansas, 66211, United States

Location

The Research Group of Lexington, Llc.

Lexington, Kentucky, 40503, United States

Location

The Research Group of Lexington, Llc

Lexington, Kentucky, 40503, United States

Location

L-MARC Research Center

Louisville, Kentucky, 40213, United States

Location

Crescent City Headache and Neurology Center

Chalmette, Louisiana, 70043, United States

Location

Alliance for Multispecialty Research, LLC.

New Orleans, Louisiana, 70119, United States

Location

DelRicht Research

New Orleans, Louisiana, 70124, United States

Location

Boston Clinical Trials

Boston, Massachusetts, 02131, United States

Location

Neurology Center of New England P.C.

Foxborough, Massachusetts, 02035, United States

Location

Community Clinical Research Network Inc

Marlborough, Massachusetts, 01752, United States

Location

MedVadis Research Corporation

Waltham, Massachusetts, 02451, United States

Location

Michigan Head Pain & Neurological Institute

Ann Arbor, Michigan, 48104, United States

Location

Romedica LLC

Rochester, Michigan, 48307, United States

Location

StudyMetrix Research

City of Saint Peters, Missouri, 63303, United States

Location

Alliance for Multispecialty Reseach, LLC

Kansas City, Missouri, 64114, United States

Location

Clinvest Research, LLC

Springfield, Missouri, 65807, United States

Location

Clinvest Research, LLC

Springfield, Missouri, 65810, United States

Location

Meridian Clinical Research, LLC

Norfolk, Nebraska, 68701, United States

Location

Excel Clinical research

Las Vegas, Nevada, 89109, United States

Location

Wr-Crcn, Llc

Las Vegas, Nevada, 89118, United States

Location

Albuquerque Clinical Trials, Inc.

Albuquerque, New Mexico, 87102, United States

Location

Dent Neurosciences Research Center, Inc.

Amherst, New York, 14226, United States

Location

Central New York Clinical Research

Manlius, New York, 13104, United States

Location

New York Neurology Associates

New York, New York, 10003, United States

Location

Fieve Clinical Research, Inc

New York, New York, 10017, United States

Location

North Suffolk Neurology, PC

Port Jefferson Station, New York, 11776, United States

Location

Montefiore Medical Center

The Bronx, New York, 10461, United States

Location

Upstate Clinical Research Associates, LLC

Williamsville, New York, 14221, United States

Location

Headache Wellness Center

Greensboro, North Carolina, 27405, United States

Location

Accellacare

Raleigh, North Carolina, 27609, United States

Location

M3 Wake Research, Inc.

Raleigh, North Carolina, 27612, United States

Location

Carolina Research Center, Inc.

Shelby, North Carolina, 28150, United States

Location

Accellacare

Wilmington, North Carolina, 28401, United States

Location

CTI Clinical Research Center

Cincinnati, Ohio, 45212, United States

Location

WellNow Urgent Care and Research

Cincinnati, Ohio, 45215, United States

Location

Wellnow Urgent Care

Cincinnati, Ohio, 45215, United States

Location

Hometown Urgent Care and Research

Columbus, Ohio, 43214, United States

Location

Wellnow Urgent Care and Research

Columbus, Ohio, 43214, United States

Location

Hometown Urgent Care and Research

Dayton, Ohio, 45424, United States

Location

WellNow Urgent Care and Research

Dayton, Ohio, 45424, United States

Location

Neuro-Behavioral Clinical Research, Inc.

North Canton, Ohio, 44720, United States

Location

WellNow Urgent Care and Research

Troy, Ohio, 45373, United States

Location

Hightower Clinical

Oklahoma City, Oklahoma, 73102, United States

Location

Hightower Clinical

Oklahoma City, Oklahoma, 73134, United States

Location

Summit Headlands LLC, dba Summit Research

Portland, Oregon, 97210, United States

Location

Clinical Research Philadelphia, LLC

Philadelphia, Pennsylvania, 19114, United States

Location

Preferred Primary Care Physicians, Inc.

Pittsburgh, Pennsylvania, 15236, United States

Location

Preferred Primary Care Physicians

Uniontown, Pennsylvania, 15401, United States

Location

Reading Hospital Clinical Trials Office

West Reading, Pennsylvania, 19611, United States

Location

Tower Health Medical Group - Neurology

West Reading, Pennsylvania, 19611, United States

Location

Coastal Carolina Research Center

North Charleston, South Carolina, 29405, United States

Location

Accellacare (Administrative Only)

Bristol, Tennessee, 37620, United States

Location

Internal Medicine and Pediatric Associates of Bristol, PC

Bristol, Tennessee, 37620, United States

Location

WR-ClinSearch, LLC

Chattanooga, Tennessee, 37421, United States

Location

KCA Neurology, PLLC

Franklin, Tennessee, 37067, United States

Location

Clinical Neuroscience Solutions, Inc.

Memphis, Tennessee, 38119, United States

Location

FutureSearch Trials of Neurology

Austin, Texas, 78731, United States

Location

FutureSearch Trials of Dallas, LP

Dallas, Texas, 75231, United States

Location

North Texas Institute of Neurology and Headache - NextStage Clinical Research

Frisco, Texas, 75034, United States

Location

North Texas Institute of Neurology and Headache

Frisco, Texas, 75034, United States

Location

Texas Center for Drug Development, Inc.

Houston, Texas, 77081, United States

Location

Red Star Research. LLC

Lake Jackson, Texas, 77566, United States

Location

FMC Science

Lampasas, Texas, 76550, United States

Location

Radiance Clinical Research

Lampasas, Texas, 76550, United States

Location

DM Clinical Research

Tomball, Texas, 77375, United States

Location

Wasatch Clinical Research , LLC(Administrative Location)

Salt Lake City, Utah, 84107, United States

Location

Charlottesville Medical Research Center, LLC

Charlottesville, Virginia, 22911, United States

Location

Health Research of Hampton Roads, Inc.

Newport News, Virginia, 23606, United States

Location

Meridian Clinical Research, LLC

Norfolk, Virginia, 23502, United States

Location

Northwest Clinical Research Center

Bellevue, Washington, 98007, United States

Location

Seattle Clinical Research Center

Seattle, Washington, 98105, United States

Location

Seattle Women's: Health, Research, Gynecology

Seattle, Washington, 98105, United States

Location

Related Links

MeSH Terms

Conditions

Migraine DisordersHyperacusisPhotophobiaNausea

Condition Hierarchy (Ancestors)

Headache Disorders, PrimaryHeadache DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesHearing DisordersEar DiseasesOtorhinolaryngologic DiseasesSensation DisordersNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsVision DisordersEye DiseasesSigns and Symptoms, Digestive

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 5, 2021

First Posted

March 18, 2021

Study Start

March 26, 2021

Primary Completion

March 21, 2024

Study Completion

March 21, 2024

Last Updated

March 27, 2025

Results First Posted

March 27, 2025

Record last verified: 2025-03

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations