NCT04753970

Brief Summary

Cerebral small vessel disease (SVD), present in 80-94% of adults over age 65 years, increases the risk of stroke by 2-fold, and dementia by 2.3-fold. There is currently no treatment to slow SVD progression. This study aims to test whether impaired cerebral and retinal vasoreactivity may serve as biomarker for SVD progression, and to evaluate the safety and efficacy of cilostazol (antiplatelet agent with vasodilatory and anti-inflammatory properties) for the treatment of SVD.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
100

participants targeted

Target at P75+ for phase_1

Timeline
1mo left

Started Feb 2021

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Progress99%
Feb 2021Jun 2026

First Submitted

Initial submission to the registry

February 9, 2021

Completed
Same day until next milestone

Study Start

First participant enrolled

February 9, 2021

Completed
6 days until next milestone

First Posted

Study publicly available on registry

February 15, 2021

Completed
5.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2026

Last Updated

July 23, 2025

Status Verified

July 1, 2025

Enrollment Period

5.3 years

First QC Date

February 9, 2021

Last Update Submit

July 21, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • white matter disease volume

    change in total white matter disease volume

    1 year

Secondary Outcomes (4)

  • cognition

    1 year

  • stroke

    1 year

  • cerebrovasoreactivity

    1 year

  • retinal vasoreactivity

    1 year

Study Arms (2)

Cilostazol

EXPERIMENTAL

Cilostazol 100mg BID

Drug: Cilostazol

No intervention

NO INTERVENTION

Interventions

Cilostazol 100mg BID

Cilostazol

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥18 yo.
  • Diagnosis of CADASIL, sporadic WMD or lobar CMB and age-matched healthy controls (eg. patient's spouse or unrelated friends without SVD)

You may not qualify if:

  • Age\<18yo
  • Pregnant
  • Breast feeding
  • Unable to follow commands
  • Unable to tolerate MRI

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Mayo Clinic Florida

Jacksonville, Florida, 32224, United States

RECRUITING

MeSH Terms

Conditions

Cerebral Small Vessel DiseasesCADASIL

Interventions

Cilostazol

Condition Hierarchy (Ancestors)

Cerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesVascular DiseasesCardiovascular DiseasesCerebral InfarctionBrain InfarctionBrain IschemiaDementia, VascularCerebral Arterial DiseasesIntracranial Arterial DiseasesStrokeDementiaGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesInfarctionIschemiaPathologic ProcessesPathological Conditions, Signs and SymptomsNecrosis

Intervention Hierarchy (Ancestors)

TetrazolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-Ring

Study Officials

  • Michelle P Lin, MD, MPH

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

February 9, 2021

First Posted

February 15, 2021

Study Start

February 9, 2021

Primary Completion (Estimated)

June 1, 2026

Study Completion (Estimated)

June 1, 2026

Last Updated

July 23, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will not share

Locations