NCT04743141

Brief Summary

The purpose of this study is to test the long-term safety of rimegepant in the acute treatment of migraine in children and adolescents (≥ 6 to \< 18 years of age).

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
600

participants targeted

Target at P75+ for phase_3

Timeline
52mo left

Started Apr 2021

Longer than P75 for phase_3

Geographic Reach
3 countries

126 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress54%
Apr 2021Jul 2030

First Submitted

Initial submission to the registry

February 4, 2021

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 8, 2021

Completed
3 months until next milestone

Study Start

First participant enrolled

April 28, 2021

Completed
9.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 31, 2030

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 31, 2030

Last Updated

April 16, 2026

Status Verified

April 1, 2026

Enrollment Period

9.3 years

First QC Date

February 4, 2021

Last Update Submit

April 15, 2026

Conditions

Keywords

Long-term safety, acute treatment, migraine, phonophobia, photophobia, nausea, pediatric, children, adolescent

Outcome Measures

Primary Outcomes (1)

  • The frequency and severity of on-treatment and treatment-emergent adverse events, serious adverse events, adverse events leading to discontinuation, clinically significant lab abnormalities

    To evaluate the safety and tolerability of rimegepant in children and adolescents (6 to \< 18 years of age).

    58 weeks

Secondary Outcomes (1)

  • The frequency and severity of hepatic-related adverse events and frequency of hepatic-related adverse events leading to treatment discontinuation

    58 weeks

Study Arms (1)

Active

EXPERIMENTAL

rimegepant 75 mg, 50 mg or 35 mg ODT

Drug: Rimegepant (PF-07899801)

Interventions

Rimegepant 75 mg, 50 mg or 35 mg ODT

Active

Eligibility Criteria

Age6 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • History of migraine (with or without aura) for ≥ 6 months before Screening.
  • History of 1 to 8 moderate or severe attacks per month during the 2 months prior to screening.
  • or more migraine days requiring treatment during the Observation Phase.
  • Prophylactic migraine medication is permitted if the dose has been stable for at least 12 weeks prior to the Screening Visit.
  • Ability to distinguish between migraine and other types of headaches.
  • Weight \> 15 kg. For EU countries only: Participants 12 to \< 18 years of age must have a body weight of \>25kg.
  • Adequate venous access for blood sampling.
  • Male and female participants 6 to \< 18 years of age (participants must not reach their 18th birthday on or before the Baseline visit).

You may not qualify if:

  • History of cluster headache or hemiplegic migraine headache.
  • Confounding and clinically significant pain syndrome.
  • Current uncontrolled and/or untreated psychiatric condition for a minimum of 6 months prior to the Screening Visit (lifetime history of psychosis and/or mania are excluded).
  • History of suicidal behavior or at risk of self-harm/harm to others.
  • History of major psychiatric disorder.
  • Current diagnosis or history of substance abuse
  • Reported current use of or tested positive at Screening for drugs of abuse.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (126)

Perseverance Research Center, LLC

Scottsdale, Arizona, 85253, United States

RECRUITING

Physicians Research Group

Tempe, Arizona, 85284, United States

ACTIVE NOT RECRUITING

Advanced Research Center, Inc.

Anaheim, California, 92805, United States

RECRUITING

ProScience Research Group

Culver City, California, 90230, United States

RECRUITING

Neuro-Pain Medical Center

Fresno, California, 93710, United States

RECRUITING

Regents of the University of California (UC San Diego)

La Jolla, California, 92093, United States

RECRUITING

Adult & Child Neurology Medical Associates

Long Beach, California, 90806, United States

RECRUITING

Memorialcare Miller Children's & Women's Hospital Long Beach

Long Beach, California, 90806, United States

RECRUITING

Velocity Clinical Research - North Hollywood

North Hollywood, California, 91606, United States

ACTIVE NOT RECRUITING

The Neurology Group

Pomona, California, 91767, United States

RECRUITING

UC Davis Medical Center, Investigational Drug Service (IDS) Pharmacy

Sacramento, California, 95817, United States

ACTIVE NOT RECRUITING

University of California, Davis Clinical and Translational Science Center Clinical Research Center

Sacramento, California, 95817, United States

ACTIVE NOT RECRUITING

University of California, Davis Midtown Clinic

Sacramento, California, 95817, United States

ACTIVE NOT RECRUITING

Velocity Clinical Research- Banning

San Bernardino, California, 92408, United States

RECRUITING

Pacific Clinical Research Management Group LLC

Upland, California, 91786, United States

ACTIVE NOT RECRUITING

Sunwise Clinical Research

Walnut Creek, California, 94596, United States

RECRUITING

Children's Hospital Colorado- Investigational Drug Services

Aurora, Colorado, 80045, United States

RECRUITING

Children's Hospital Colorado

Aurora, Colorado, 80045, United States

RECRUITING

Colorado Springs Neurological Associates, PC

Colorado Springs, Colorado, 80907, United States

ACTIVE NOT RECRUITING

Colorado Springs Neurological Associates, PC

Colorado Springs, Colorado, 80919, United States

ACTIVE NOT RECRUITING

Boeson Research GJT

Grand Junction, Colorado, 81501, United States

TERMINATED

Dinosaur Pediatrics

Grand Junction, Colorado, 81501, United States

TERMINATED

Boeson Research GJT

Grand Junction, Colorado, 81505, United States

TERMINATED

CT Clinical Research

Cromwell, Connecticut, 06416, United States

RECRUITING

Ki Health Partners, LLc, dba New England Institute for Clinical Research

Stamford, Connecticut, 06905, United States

RECRUITING

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

RECRUITING

AppleMed Research Group, LLC

Miami, Florida, 33126, United States

ACTIVE NOT RECRUITING

Medical Research Center of Miami II, Inc

Miami, Florida, 33134, United States

ACTIVE NOT RECRUITING

South Florida Research Phase I-IV, Inc

Miami, Florida, 33166, United States

RECRUITING

Physicians Group Services, PA d/b/a Coastal Health Research

Orange Park, Florida, 32073, United States

ACTIVE NOT RECRUITING

Clinical Associates of Orlando, LLC

Orlando, Florida, 32819, United States

RECRUITING

ForCare Clinical Research

Tampa, Florida, 33613, United States

RECRUITING

Premiere Research Institute at Palm Beach Neurology

West Palm Beach, Florida, 33407, United States

ACTIVE NOT RECRUITING

Childrens Healthcare of Atlanta

Atlanta, Georgia, 30329, United States

RECRUITING

Rare Disease Research LLC

Atlanta, Georgia, 30329, United States

ACTIVE NOT RECRUITING

Pivotal Clinical Research & Associates, LLC

Brunswick, Georgia, 31520, United States

RECRUITING

CenExel iResearch, LLC

Decatur, Georgia, 30030, United States

RECRUITING

Chicago Headache Center & Research Institute

Chicago, Illinois, 60657, United States

RECRUITING

AMR-Baber Research Inc

Naperville, Illinois, 60563, United States

RECRUITING

Options Research Group, LLC

Westfield, Indiana, 46074, United States

RECRUITING

Integrated Clinical Trial Services

West Des Moines, Iowa, 50265, United States

RECRUITING

Clinical Associates Midwest, LLC

Kansas City, Kansas, 66214, United States

RECRUITING

University of Kentucky Hospital

Lexington, Kentucky, 40536, United States

ACTIVE NOT RECRUITING

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

TERMINATED

MedVadis Research Corporation

Waltham, Massachusetts, 02451, United States

ACTIVE NOT RECRUITING

Michigan Head Pain and Neurological Institute

Ann Arbor, Michigan, 48104, United States

RECRUITING

Corewell Health, for and on behalf of Spectrum Health Hospital and Corewell Health Medical Group

Grand Rapids, Michigan, 49503, United States

RECRUITING

Corewell Health, Helen DeVos Children's Hospital

Grand Rapids, Michigan, 49503, United States

RECRUITING

Wellnow Urgent Care and Research

Kalamazoo, Michigan, 49048, United States

TERMINATED

Beaumont Hospital, Royal Oak Campus

Royal Oak, Michigan, 48073, United States

RECRUITING

Sharlin Health Neuroscience Research Center

Ozark, Missouri, 65721, United States

RECRUITING

Clinvest Research, LLC

Springfield, Missouri, 65807, United States

ACTIVE NOT RECRUITING

Boeson Research

Great Falls, Montana, 59405, United States

RECRUITING

Heart & Hands Midwifery

Kalispell, Montana, 59901, United States

ACTIVE NOT RECRUITING

Blue Moose Pediatrics

Missoula, Montana, 59804, United States

RECRUITING

Boeson Research Laboratory

Missoula, Montana, 59804, United States

RECRUITING

Boeson Research

Missoula, Montana, 59804, United States

RECRUITING

Alivation Research, LLC

Lincoln, Nebraska, 68526, United States

TERMINATED

Children's Hospital & Medical Center

Omaha, Nebraska, 68114, United States

RECRUITING

HMH Jersey Shore University Medical Center

Neptune City, New Jersey, 07753, United States

NOT YET RECRUITING

Dent Neurosciences Research Center

Amherst, New York, 14226, United States

RECRUITING

True North Neurology

Commack, New York, 11725, United States

RECRUITING

New York Neurology Associates

New York, New York, 10003, United States

RECRUITING

Mount Sinai Hospital - Pharmacy Department

New York, New York, 10029, United States

ACTIVE NOT RECRUITING

Columbia University Irving Medical Center

New York, New York, 10032, United States

ACTIVE NOT RECRUITING

Irving Center for Clinical and Translational Research, Outpatient Clinical Research Unit

New York, New York, 10032, United States

ACTIVE NOT RECRUITING

The Neurological Institute of New York

New York, New York, 10032, United States

ACTIVE NOT RECRUITING

North Suffolk Neurology

Port Jefferson Station, New York, 11776, United States

ACTIVE NOT RECRUITING

OnSite Clinical Solutions, LLC

Charlotte, North Carolina, 28277, United States

RECRUITING

Headache Wellness Center, PC

Greensboro, North Carolina, 27405, United States

RECRUITING

WellNow Urgent Care and Research

Cincinnati, Ohio, 45215, United States

ACTIVE NOT RECRUITING

Cincinnati Children's Hospital

Cincinnati, Ohio, 45229, United States

RECRUITING

Velocity Clinical Research - Cincinnati

Cincinnati, Ohio, 45242, United States

RECRUITING

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

RECRUITING

Wellnow Urgent Care and Research

Dayton, Ohio, 45424, United States

ACTIVE NOT RECRUITING

IPS Research Company

Oklahoma City, Oklahoma, 73106, United States

ACTIVE NOT RECRUITING

Velocity Clinical Research, Grants Pass

Grants Pass, Oregon, 97527, United States

ACTIVE NOT RECRUITING

Providence Investigational Drug Service - Westside

Portland, Oregon, 97225, United States

RECRUITING

Providence Neuroscience Institute: Research Coordinators' Office

Portland, Oregon, 97225, United States

RECRUITING

Providence Pediatric Specialty Clinic

Portland, Oregon, 97225, United States

RECRUITING

Clario

Philadelphia, Pennsylvania, 19103, United States

RECRUITING

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19104, United States

ACTIVE NOT RECRUITING

Velocity Clinical Research-Providence

East Greenwich, Rhode Island, 02818, United States

RECRUITING

Velocity Clinical Research- Greenville

Greenville, South Carolina, 29615, United States

ACTIVE NOT RECRUITING

Premier Neurology

Greer, South Carolina, 29650, United States

ACTIVE NOT RECRUITING

Novaceut Clinical Research

Clarksville, Tennessee, 37043, United States

ACTIVE NOT RECRUITING

Le Bonheur Children's Hospital

Memphis, Tennessee, 38103, United States

RECRUITING

Le Bonheur Childrens Hospital - Childrens Foundation Research Institute

Memphis, Tennessee, 38103, United States

RECRUITING

Le Bonheur Childrens Hospital - Outpatient Building

Memphis, Tennessee, 38103, United States

RECRUITING

Access Clinical Trials, Inc.

Nashville, Tennessee, 37203, United States

TERMINATED

Dell Children's Medical Center

Austin, Texas, 78723, United States

RECRUITING

Child Neurology Consultants of Austin - South Austin

Austin, Texas, 78749, United States

RECRUITING

Child Neurology Consultants of Austin - Central Austin

Austin, Texas, 78757, United States

RECRUITING

Houston Clinical Trials, LLC

Bellaire, Texas, 77401, United States

RECRUITING

Infinite Research Group, LLC

Dallas, Texas, 75201, United States

RECRUITING

Cedar Health Research

Dallas, Texas, 75251, United States

RECRUITING

ANESC Research

El Paso, Texas, 79912, United States

RECRUITING

North Texas Institute of Neurology and Headache

Frisco, Texas, 75034, United States

ACTIVE NOT RECRUITING

Trio Clinical Trials, LLC.

Houston, Texas, 77008, United States

ACTIVE NOT RECRUITING

Pain and Headache Centers of Texas

Houston, Texas, 77054, United States

RECRUITING

SCLA Management

Houston, Texas, 77077, United States

RECRUITING

Houston Clinical Research,LLC.

Houston, Texas, 77081, United States

TERMINATED

NeuroCare Plus

Houston, Texas, 77094, United States

RECRUITING

AIM Trials, LLC

Plano, Texas, 75093, United States

RECRUITING

JBR Clinical Research

Salt Lake City, Utah, 84107, United States

RECRUITING

Wasatch Clinical Research , LLC(Administrative Location)

Salt Lake City, Utah, 84107, United States

RECRUITING

Pediatric Associates of Charlottesville, PLC (Private Pediatric Practice)

Charlottesville, Virginia, 22902, United States

RECRUITING

Pediatric Research of Charlottesville, LLC (Regulatory Only)

Charlottesville, Virginia, 22902, United States

RECRUITING

Pediatric Research of Charlottesville, LLC

Charlottesville, Virginia, 22902, United States

RECRUITING

Children's Hospital of The King's Daughters

Norfolk, Virginia, 23507, United States

RECRUITING

Children's Specialty Group, PLLC , Division of Childhood & Adolescent Neurology

Norfolk, Virginia, 23510, United States

RECRUITING

National Clinical Research, Inc.

Richmond, Virginia, 23294, United States

TERMINATED

Northwest Clinical Research Center

Bellevue, Washington, 98007, United States

RECRUITING

Seattle Children's Hospital Investigational Drug Services

Seattle, Washington, 98105, United States

RECRUITING

Seattle Children's Hospital

Seattle, Washington, 98105, United States

RECRUITING

University Hospital

Madison, Wisconsin, 53792, United States

RECRUITING

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS, Lech Szczechowski

Katowice, 40-123, Poland

TERMINATED

Centrum Medyczne Plejady

Krakow, 30-363, Poland

RECRUITING

Wojewodzki Specjalistyczny Szpital Dzieciecy im. Sw. Ludwika w Krakowie Oddzial Kliniczny Dzieci

Krakow, 31-503, Poland

RECRUITING

Clinical Research Center Sp. z o.o.

Poznan, 60-848, Poland

RECRUITING

Pracownia Badan Klinicznych SALUS

Wroclaw, 52-210, Poland

RECRUITING

Centrum Medyczne Oporow

Wroclaw, 52-416, Poland

ACTIVE NOT RECRUITING

Centre Atencio Primaria (CAP) Balenya

Balenya, Barcelona, 08550, Spain

ACTIVE NOT RECRUITING

Hospital Universitario Vall d'Hebron

Barcelona, 08035, Spain

RECRUITING

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

RECRUITING

Hospital Clinico Universitario de Valladolid

Valladolid, 47003, Spain

RECRUITING

Related Links

MeSH Terms

Conditions

Migraine DisordersHyperacusisPhotophobiaNausea

Interventions

rimegepant sulfate

Condition Hierarchy (Ancestors)

Headache Disorders, PrimaryHeadache DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesHearing DisordersEar DiseasesOtorhinolaryngologic DiseasesSensation DisordersNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsVision DisordersEye DiseasesSigns and Symptoms, Digestive

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Central Study Contacts

Pfizer Pfizer CT.gov Call Center

CONTACT

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 4, 2021

First Posted

February 8, 2021

Study Start

April 28, 2021

Primary Completion (Estimated)

July 31, 2030

Study Completion (Estimated)

July 31, 2030

Last Updated

April 16, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations