NCT04706923

Brief Summary

The purpose of this study is to determine the safety and tolerability of intravenous (IV) brincidofovir (BCV; SyB V-1901) 0.2 mg/kg, 0.3 mg/kg or 0.4 mg/kg dosed twice weekly (BIW) or 0.4 mg/kg dosed once weekly (QW) for 4 weeks in subjects with AdV, and IV BCV in subjects with CMV

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
52

participants targeted

Target at P25-P50 for phase_2

Timeline
4mo left

Started Aug 2021

Longer than P75 for phase_2

Geographic Reach
1 country

11 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress92%
Aug 2021Sep 2026

First Submitted

Initial submission to the registry

January 5, 2021

Completed
8 days until next milestone

First Posted

Study publicly available on registry

January 13, 2021

Completed
7 months until next milestone

Study Start

First participant enrolled

August 16, 2021

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 30, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 30, 2026

Last Updated

June 21, 2024

Status Verified

June 1, 2024

Enrollment Period

5.1 years

First QC Date

January 5, 2021

Last Update Submit

June 20, 2024

Conditions

Outcome Measures

Primary Outcomes (2)

  • Safety will be evaluated based on incidence and severity of Adverse Events, Serious Adverse Events and laboratory assessments.

    Safety will be evaluated based on incidence and severity of Adverse Events, Serious Adverse Events and laboratory assessments.

    From initiation of BCV administration up to 19 weeks

  • Antiviral Effects

    Change from baseline AdV viremia in plasma measured on Day 1 and weekly throughout the study.

    From initiation of BCV administration up to 9 weeks

Study Arms (4)

BCV 0.2mg/kg BIW

EXPERIMENTAL

BCV: 0.2 mg/kg administered as a continuous IV infusion over 2 hours

Drug: BCV

BCV 0.3mg/kg BIW

EXPERIMENTAL

BCV: 0.3 mg/kg administered as a continuous IV infusion over 2 hours

Drug: BCV

BCV 0.4 mg/kg BIW

EXPERIMENTAL

BCV: 0.4 mg/kg administered as a continuous IV infusion over 2 hours

Drug: BCV

BCV 0.4 mg/kg QW

EXPERIMENTAL

BCV: 0.4 mg/kg administered as a continuous IV infusion over 2 hours

Drug: BCV

Interventions

BCVDRUG

Brincidofovir (BCV) is a lipid conjugate of the antiviral cidofovir that enables optimal intracellular levels of the active drug.

BCV 0.2mg/kg BIWBCV 0.3mg/kg BIWBCV 0.4 mg/kg BIWBCV 0.4 mg/kg QW

Eligibility Criteria

Age2 Months+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female, aged 2 months and older at the time of informed consent.
  • AdV DNA viremia \>10,000 copies/mL from a single sample, or 2 samples greater than 48 hours apart with the second result higher than the first and both greater than 1000 copies/mL, from the data obtained from the designated central virology laboratory of the local laboratory using the blood sample(s) collected informed consent has been obtained and within 7 days prior to Day 1 (AdV DNA viremia results collected within the 7 day window, but prior to consent may be used if the Informed Consent Form (ICF) signed by the subject provides approval) . CMV viremia with or without evidence of tissue invasive CMV disease. For laboratory results that are generated in units other than copies/mL or IU/mL, please refer to the testing laboratory for guidance on the appropriate conversion calculation.
  • Either (a) have disseminated AdV disease or (b) have an underlying immunocompromised state, and have asymptomatic AdV infection or localized AdV disease.
  • In the judgment of the investigator, be in a serious condition to be treated with intravenous cidofovir for AdV.

You may not qualify if:

  • Subjects who weigh ≥120 kg.
  • NIH/NCI CTCAE (United States \[US\] National Institutes of Health \[NIH\]/National Cancer Institute) Grade 2 or higher diarrhea (i.e., increase of ≥ 4 stools per day over usual pre-transplant stool output) within 7 days prior to Day 1.
  • NIH Stage 4 acute GVHD of the skin (i.e., generalized erythroderma with bullous formation) within 7 days prior to Day 1.
  • NIH Stage 2 or higher acute GVHD of the liver function (i.e., bilirubin \>3 mg/dL \[SI: \>51 μmol/L\]) within 7 days prior to Day 1.
  • NIH Stage 2 or higher acute GVHD of the gut (i.e., diarrhea \>556 mL/m2/day for pediatric subjects \[or \>1000 mL/day for young adults as applicable, at centers in the United States only\], or severe abdominal pain with or without ileus) within 7 days prior to Day 1.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Research Site

Los Angeles, California, 90027, United States

RECRUITING

Research Site

Los Angeles, California, 90095, United States

COMPLETED

Research Site

San Francisco, California, 94158, United States

COMPLETED

Research Site

Chicago, Illinois, 60637, United States

RECRUITING

University of Nebraska Medical Center

Omaha, Nebraska, 68198, United States

RECRUITING

Research Site

Durham, North Carolina, 27710, United States

RECRUITING

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, 45229, United States

RECRUITING

Research Site

Philadelphia, Pennsylvania, 19104, United States

RECRUITING

St. Jude Children's Research Hospital

Memphis, Tennessee, 38105, United States

RECRUITING

MD Anderson Cancer Center

Houston, Texas, 77030, United States

RECRUITING

Research Site

Seattle, Washington, 98109, United States

RECRUITING

Related Links

MeSH Terms

Conditions

Adenoviridae InfectionsCytomegalovirus Infections

Condition Hierarchy (Ancestors)

DNA Virus InfectionsVirus DiseasesInfectionsHerpesviridae Infections

Central Study Contacts

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 5, 2021

First Posted

January 13, 2021

Study Start

August 16, 2021

Primary Completion (Estimated)

September 30, 2026

Study Completion (Estimated)

September 30, 2026

Last Updated

June 21, 2024

Record last verified: 2024-06

Data Sharing

IPD Sharing
Will not share

Locations