NCT04583878

Brief Summary

This is a multi-center prospective cohort study of patients with first-episode deep venous thrombosis and pulmonary embolism.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
115

participants targeted

Target at P50-P75 for all trials

Timeline
7mo left

Started Dec 2020

Longer than P75 for all trials

Geographic Reach
1 country

14 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress90%
Dec 2020Dec 2026

First Submitted

Initial submission to the registry

September 22, 2020

Completed
20 days until next milestone

First Posted

Study publicly available on registry

October 12, 2020

Completed
2 months until next milestone

Study Start

First participant enrolled

December 22, 2020

Completed
5.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2026

Expected
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2026

Last Updated

February 2, 2026

Status Verified

January 1, 2026

Enrollment Period

5.4 years

First QC Date

September 22, 2020

Last Update Submit

January 29, 2026

Conditions

Outcome Measures

Primary Outcomes (2)

  • Change in exercise capacity

    Measured objectively by peak oxygen uptake (VO2) as a percent predicted based on ml/min/kg of lean body mass during cardiopulmonary exercise testing (CPET)

    3 months and 12 months post-diagnosis

  • Change in dyspnea on exertion (DOE)

    measured using Borg questionnaire and defined as a mean difference of \> 1 between those with and without exercise intolerance at the end of the warm-up and submaximal work rates during CPET

    3 months and 12 months post-diagnosis

Secondary Outcomes (15)

  • Change in cardiac maladaptation

    3 months and 12 months post-diagnosis

  • Change in pulmonary/ventilatory limitations

    3 months and 12 months post-diagnosis

  • Change in muscle metabolic aberrations

    3 months and 12 months post-diagnosis

  • Change in pulmonary vascular obstruction score in participants with and without exercise intolerance (Quantitative assessment)

    At diagnosis, 3 months and 12 months post-diagnosis

  • Change in pulmonary vascular obstruction score in participants with and without exercise intolerance (Qualitative assessment)

    At diagnosis, 3 months and 12 months post-diagnosis

  • +10 more secondary outcomes

Study Arms (2)

Participants with Pulmonary Embolism

The target accrual is based on the primary endpoint (exercise intolerance and dyspnea on exertion). To achieve adequate power and precision in the primary analysis, the target enrollment is 80 children. Both males and females of all races and ethnic groups are eligible for this study.

Diagnostic Test: Blood draw (Visit 1)Diagnostic Test: Blood draw (Visits 2 and 3)

Control Group

A positive control group that has not had pulmonary embolism (PE) but is prescribed physical activity restrictions expected to produce a similar deconditioning effect as patients with PE will be enrolled from UT Southwestern only (cohort 1) or children who are no prescribed physical activity restrictions and are otherwise considered healthy (cohort 2). The target accrual of the positive control group is based on feasibility and availability of funds and will be limited to 25 controls.

Diagnostic Test: Blood draw (Visits 2 and 3)

Interventions

Blood draw (Visit 1)DIAGNOSTIC_TEST

Labs will be drawn at Visit 1, also referred to as screening (within 60 days of diagnosis) with the standard of care labs drawn.

Participants with Pulmonary Embolism

Labs will be drawn at Visit 2 (12 weeks post-diagnosis with a range of 10-16 weeks) and Visit 3 (12 months ± 30 days) for research purposes only and will be collected at Children's Medical Center and processed at UT Southwestern Medical Center.

Control GroupParticipants with Pulmonary Embolism

Eligibility Criteria

Age8 Years - 21 Years
Sexall
Healthy VolunteersYes
Age GroupsChild (0-17), Adult (18-64)
Sampling MethodProbability Sample
Study Population

Study population will include children (defined as persons who have not attained the legal age for consent to treatments or procedures involved in the research, under the applicable law of the jurisdiction in which the research will be conducted), and patients (defined as individuals in a clinical setting with whom there is a treatment relationship). Participants must meet the eligibility criteria in order to participate in this trial.

You may qualify if:

  • Ages 8 to ≤ 21 years
  • Participant must be able to speak and understand English
  • Be willing to participate and able to comply with the study protocol
  • For participants with PE: Children with acute, radiologically confirmed pulmonary embolism (PE) with our without DVT
  • For control group: Cohort 1: Children who are prescribed physical activity restrictions for 2 up to 12 weeks following any minor outpatient surgery or, minor injury (surgery or injury is referred to as "diagnosis" hereafter) Cohort 2: Children who are not prescribed physical activity restrictions and are otherwise considered to be healthy.

You may not qualify if:

  • Congenital heart disease with abnormal pulmonary circulation or with in-situ pulmonary artery thrombosis
  • Chronic kidney disease
  • Chronic inflammatory or an autoimmune disorder (such as systemic lupus erythematosus, juvenile rheumatoid disorder, inflammatory bowel disease, and sickle cell disease)
  • A metabolic or endocrinological disorder such as diabetes mellitus or thyroid disorder
  • History of or active cancer
  • Pregnant
  • Musculoskeletal limitations to exercise expected to be present uptil 4 months post-diagnosis
  • Weight ≥ 300 lbs
  • Contraindications to magnetic resonance imaging
  • Has any other medical condition, which in the opinion of the investigator may potentially compromise the safety or compliance of the patient or may preclude the patient's successful completion of the clinical study
  • Lack of anticoagulant treatment for the acute VTE due to contraindications

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (14)

Arkansas Childrens Research Institute (ACRI)

Little Rock, Arkansas, 72202, United States

Location

Johns Hopkins All Childrens Hospital

St. Petersburg, Florida, 33701, United States

Location

Emory University / Children's Heathcare Atlanta

Atlanta, Georgia, 30329, United States

Location

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02115, United States

Location

Central Michigan University

Mount Pleasant, Michigan, 48859, United States

Location

Childrens Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

Cincinnati Childrens Hospital

Cincinnati, Ohio, 45229, United States

Location

Nationwide Children's Hospital

Columbus, Ohio, 43205, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, 19146, United States

Location

UT Southwestern Medical Center / Children's Medical Center

Dallas, Texas, 75235, United States

Location

Cook Childrens Medical Center

Fort Worth, Texas, 76104, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Related Links

Biospecimen

Retention: SAMPLES WITH DNA

Research Biomarkers: blood for inflammatory markers, thrombin generation and fibrinolysis assays are required for all participants. Research Blood for DNA/RNA only collected for those participants who consent to genetic material.

MeSH Terms

Conditions

Venous ThrombosisPulmonary Embolism

Interventions

Blood Specimen Collection

Condition Hierarchy (Ancestors)

ThrombosisEmbolism and ThrombosisVascular DiseasesCardiovascular DiseasesLung DiseasesRespiratory Tract DiseasesEmbolism

Intervention Hierarchy (Ancestors)

Specimen HandlingClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisPuncturesSurgical Procedures, OperativeInvestigative Techniques

Study Officials

  • Ayesha Zia, MD, MSCS

    University of Texas Southwestern Medical Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Associate Professor of Pediatrics

Study Record Dates

First Submitted

September 22, 2020

First Posted

October 12, 2020

Study Start

December 22, 2020

Primary Completion (Estimated)

June 1, 2026

Study Completion (Estimated)

December 1, 2026

Last Updated

February 2, 2026

Record last verified: 2026-01

Locations