NCT04446377

Brief Summary

This is a clinical trial to evaluate the efficacy of LAM-002A compared to placebo treatment in adults with a confirmed SARS-CoV-2 infection who are receiving standards supportive care in an outpatient setting.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
142

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2020

Shorter than P25 for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 23, 2020

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 24, 2020

Completed
21 days until next milestone

Study Start

First participant enrolled

July 15, 2020

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 24, 2021

Completed
26 days until next milestone

Study Completion

Last participant's last visit for all outcomes

April 19, 2021

Completed
2.3 years until next milestone

Results Posted

Study results publicly available

August 8, 2023

Completed
Last Updated

August 8, 2023

Status Verified

August 1, 2023

Enrollment Period

8 months

First QC Date

June 23, 2020

Results QC Date

May 19, 2023

Last Update Submit

August 4, 2023

Conditions

Keywords

COVID-19SARS-CoV-2Apilimod DimesylateLAM-002ACoronavirusAI Therapeutics

Outcome Measures

Primary Outcomes (1)

  • Viral Load Change

    The primary efficacy outcome measure evaluated change in SARS-CoV-2 viral load at Day 4 from Day 1, of LAM-002A or placebo-treated participants. SARS-CoV-2 viral load was measured by a real-time quantitative reverse transcription polymerase chain reaction (qRT-PCR) test of nasopharyngeal samples. Analysis focused on log10 viral load on Day 4 compared to baseline viral load at Day 1 in participants with baseline viral load \>100,000 copies/mL

    4 Days

Secondary Outcomes (4)

  • Number of Participants With Treatment-emergent Adverse Events (TEAEs)

    28 Days

  • Clinical Efficacy

    28 Days

  • Change in COVID-19 Clinical Status

    28 Days

  • Oxygen Saturation

    Baseline, Day 1, Day 4, Day 11, Day28

Other Outcomes (1)

  • Number and Percentage of Participants With Viral Load < Lower Limit of Quantification (LLOQ)

    4 Days

Study Arms (2)

LAM-002A

EXPERIMENTAL

LAM-002A (Apilimod Dimesylate) 125mg in five 25-mg capsules BID for 10 days

Drug: Apilimod Dimesylate Capsule

Placebo

PLACEBO COMPARATOR

(microcrystalline cellulose) in 5 capsules BID for 10 days

Other: Placebo

Interventions

LAM-002A is formulated in capsules containing 25 mg of apilimod dimesylate. The capsule is Swedish orange, Size 0.

LAM-002A
PlaceboOTHER

Microcrystalline cellulose in Swedish orange, Size 0 capsules

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Written documentation of SARS-CoV-2 infection confirmed by a validated test.
  • Presence of greater than or equal to ≥1 of the following COVID-19-related symptoms indicating mild disease: fever (temperature ≥100.4), anosmia (loss of taste or smell), cough, sore throat, gastrointestinal complaints (e.g. nausea, vomiting, or diarrhea), chills, congestion, or runny nose, headaches, muscle or body aches, fatigue, or asymptomatic patients who have tested positive for COVID-19 via a validated test within the past 4 days.
  • If symptomatic, symptom onset less than or equal to ≤ 8 days.
  • For female participants of childbearing potential, a negative urine (or serum) pregnancy test.
  • For female participants of childbearing potential, willingness to use a protocol-recommended method of contraception from the start of the screening period until greater than or equal to ≥30 days after the final dose of study therapy. Note: A female subject is considered to be of childbearing potential unless she has had a hysterectomy, bilateral tubal ligation, or bilateral oophorectomy; has medically documented ovarian failure (with serum estradiol and follicle-stimulating hormone \[FSH\] levels within the institutional laboratory postmenopausal range and a negative serum or urine beta human chorionic gonadotropin \[βHCG\]); or is menopausal (age ≥50 years with amenorrhea for ≥6 months).
  • For male participants who can father a child and are having intercourse with females of childbearing potential who are not using adequate contraception, willingness to use a protocol-recommended method of contraception from the start of study therapy until ≥30 days after the final dose of study therapy and to refrain from sperm donation from the start of study therapy until ≥90 days after administration of the final dose of study therapy. Note: A male subject is considered able to father a child unless he has had a bilateral vasectomy with documented aspermia or a bilateral orchiectomy.
  • Willingness and ability of the participant to ingest study drug capsules.
  • Willingness of the participant to comply with scheduled visits, drug administration plan, protocol-specified laboratory tests, study procedures, and study restrictions.
  • Evidence of a personally signed informed consent indicating that the participant is aware of the nature of the disease and has been informed of the procedures to be followed, the experimental nature of the therapy, alternatives, potential risks and discomforts, potential benefits, and other pertinent aspects of study participation.

You may not qualify if:

  • Respiratory rate greater than or equal to ≥20 breaths per minute.
  • Oxygen saturation by pulse oximetry less than or equal to ≤93 percent % on room air or requirement for supplemental oxygen to maintain oxygen saturation greater than \>93 percent %.
  • Total NEWS score greater than or equal to ≥6 or presence of a score of 3 on any of the individual NEWS parameters.
  • Radiographic evidence of pulmonary infiltrates (clinical X-ray within 2 days of referral)
  • Hepatic profile showing any of the following:
  • Serum alanine aminotransferase (ALT) greater than \>5 × upper limit of normal (ULN) (CTCAE Grade greater than or equal to ≥3).
  • Serum aspartate aminotransferase (AST) greater than \>5 × ULN (CTCAE Grade greater than or equal to ≥3).
  • Serum bilirubin greater than \>1.5 × ULN (CTCAE Grade greater than or equal to ≥2).
  • Renal profile showing an estimated creatinine clearance (eClCR) less than \<30 mL/minute (with eClCR to be calculated by the method at the laboratory performing the serum creatinine test).
  • Presence of a cancer with disease manifestations or therapy that could adversely affect subject safety or longevity, create the potential for drug-drug interactions, or compromise the interpretation of study results.
  • Significant cardiovascular disease (e.g. myocardial infarction, arterial thromboembolism, cerebrovascular thromboembolism) within 1 month prior to start of study therapy; unstable angina; symptomatic peripheral vascular disease; CTCAE Grade greater than or equal to ≥2 congestive heart failure; or uncontrolled CTCAE Grade greater than or equal to ≥3 hypertension (diastolic blood pressure greater than or equal to ≥100 mmHg or systolic blood pressure greater than or equal to ≥160 mmHg) despite antihypertensive therapy.
  • Significant screening ECG abnormalities, including atrial fibrillation/flutter, 2nd degree atrioventricular (AV) block type II, 3rd-degree AV block, Grade greater than or equal to ≥2 bradycardia, or corrected QT (QTc by Fridericia \[QTcF\]) greater than \>480 msec (Grade greater than \>1).
  • Gastrointestinal disease (e.g. gastric or intestinal bypass surgery, pancreatic enzyme insufficiency, malabsorption syndrome, symptomatic inflammatory bowel disease, chronic diarrheal illness, bowel obstruction) that might interfere with drug absorption or with interpretation of gastrointestinal AEs.
  • Pregnancy or breastfeeding.
  • Prior solid organ transplantation.
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Yale University

New Haven, Connecticut, 06510, United States

Location

Related Publications (1)

  • Kumar P, Mathayan M, Smieszek SP, Przychodzen BP, Koprivica V, Birznieks G, Polymeropoulos MH, Prabhakar BS. Identification of potential COVID-19 treatment compounds which inhibit SARS Cov2 prototypic, Delta and Omicron variant infection. Virology. 2022 Jul;572:64-71. doi: 10.1016/j.virol.2022.05.004. Epub 2022 May 16.

MeSH Terms

Conditions

COVID-19Coronavirus Infections

Interventions

apilimod

Condition Hierarchy (Ancestors)

Pneumonia, ViralPneumoniaRespiratory Tract InfectionsInfectionsVirus DiseasesCoronaviridae InfectionsNidovirales InfectionsRNA Virus InfectionsLung DiseasesRespiratory Tract Diseases

Limitations and Caveats

The study was potentially limited in its ability to discern a benefit of LAM-002A on viral and clinical endpoints due to the number of participants enrolled, the low baseline viral loads, and the short (4-day) duration of viral load evaluation.

Results Point of Contact

Title
Peter R. Young/Chief Scientific Officer
Organization
AI Therapeutics

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Double-blinded
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 23, 2020

First Posted

June 24, 2020

Study Start

July 15, 2020

Primary Completion

March 24, 2021

Study Completion

April 19, 2021

Last Updated

August 8, 2023

Results First Posted

August 8, 2023

Record last verified: 2023-08

Data Sharing

IPD Sharing
Will not share

Locations