NCT04380220

Brief Summary

This is a multi-center, prospective, controlled study. MS patients (1° group: 30 patients in relapse; 2° group: 30 patients in remission) and age/sex-matched healthy controls (3° group: 30 subjects) will be enrolled in the study. Patients' disability level will be evaluated by EDSS and MSFC. Patients and controls will be tested for either coagulation/complement (C3, C4, C4a, C9, fibrinogen, factor VIII and X, D-dimer, protein C, protein S, antithrombin, factor II, aPTT, von-Willebrand factor), soluble markers of endothelial damage (thrombomodulin, Endothelial Protein C Receptor), antiphospholipid antibodies, lupus anticoagulant, complete blood count, viral serological assays or microRNA microarray. Patients will undergo dynamic susceptibility contrast-enhanced MRI using a 3.0-T scanner to evaluate CBF, CBV, MTT, lesion number and volume.

Trial Health

47
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
80

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Sep 2017

Typical duration for all trials

Geographic Reach
2 countries

3 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 7, 2017

Completed
2.6 years until next milestone

First Submitted

Initial submission to the registry

April 30, 2020

Completed
8 days until next milestone

First Posted

Study publicly available on registry

May 8, 2020

Completed
4 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 31, 2020

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2020

Completed
Last Updated

May 21, 2020

Status Verified

May 1, 2020

Enrollment Period

3 years

First QC Date

April 30, 2020

Last Update Submit

May 19, 2020

Conditions

Keywords

multiple sclerosisrelapsecoagulationcomplementcerebral blood flow

Outcome Measures

Primary Outcomes (7)

  • plasma concentration of coagulation factor

    Factor VIII (%)

    through study completion, an average of 1 year

  • plasma concentration of coagulation factor

    Factor X (%)

    through study completion, an average of 1 year

  • plasma concentration of coagulation factor

    D-dimer (ng/ml)

    through study completion, an average of 1 year

  • plasma concentration of coagulation factor

    Protein C (%)

    through study completion, an average of 1 year

  • plasma concentration of coagulation factor

    Protein S (%)

    through study completion, an average of 1 year

  • plasma concentration of coagulation factor

    Fibrinogen (mg/dl)

    through study completion, an average of 1 year

  • plasma concentration of coagulation factor

    complement (mg/dl)

    through study completion, an average of 1 year

Secondary Outcomes (3)

  • Brain MRI hemodynamic changes at DSC 3.0-T MRI

    through study completion, an average of 1 year

  • Brain MRI hemodynamic changes at DSC 3.0-T MRI

    through study completion, an average of 1 year

  • Brain MRI hemodynamic changes at DSC 3.0-T MRI

    through study completion, an average of 1 year

Study Arms (3)

Relapsing MS patients

Patients diagnosed with relapsing-remitting multiple sclerosis and in relapse, untreated or treated with only immunomodulatory therapy.

Diagnostic Test: Blood samples and processing

Remitting MS patients

Patients diagnosed with relapsing-remitting multiple sclerosis and in remission, untreated or treated with only immunomodulatory therapy.

Diagnostic Test: Blood samples and processing

Healthy controls

Age- and sex-matched healthy control subjects.

Diagnostic Test: Blood samples and processing

Interventions

DSC perfusion technique at 3.0-T MRI only in MS patients

Also known as: complement C3, C4, C4a, C9, fibrinogen, factor VIII and X, D-dimer, protein C, protein S, antithrombin, aPTT, factor II, v-Willebrand factor, thrombomodulin, Endothelial Protein C Receptor
Healthy controlsRelapsing MS patientsRemitting MS patients

Eligibility Criteria

Age18 Years - 60 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64)
Sampling MethodNon-Probability Sample
Study Population

Relapsing-remitting multiple sclerosis patients and healthy subjects

You may qualify if:

  • patients diagnosed with relapsing-remitting multiple sclerosis, untreated or treated with only immunomodulatory therapy, in relapse o in remission

You may not qualify if:

  • pregnant, with any neoplastic, hematologic, thyroid, metabolic, thrombotic or autoimmune disease, drug or alcohol addicted, treated with immunosuppressive drugs, steroids o any medication interfering with coagulation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

IRCCS Regina Elena National Cancer Institute

Rome, 00144, Italy

Location

University of Rome Sapienza

Rome, 00189, Italy

Location

Related Publications (2)

  • Koudriavtseva T, Lorenzano S, Cellerino M, Truglio M, Fiorelli M, Lapucci C, D'Agosto G, Conti L, Stefanile A, Zannino S, Filippi MM, Cortese A, Piantadosi C, Maschio M, Maialetti A, Galie E, Salvetti M, Inglese M. Tissue factor as a potential coagulative/vascular marker in relapsing-remitting multiple sclerosis. Front Immunol. 2023 Jul 31;14:1226616. doi: 10.3389/fimmu.2023.1226616. eCollection 2023.

  • Koudriavtseva T, Stefanile A, Fiorelli M, Lapucci C, Lorenzano S, Zannino S, Conti L, D'Agosto G, Pimpinelli F, Di Domenico EG, Mandoj C, Giannarelli D, Donzelli S, Blandino G, Salvetti M, Inglese M. Coagulation/Complement Activation and Cerebral Hypoperfusion in Relapsing-Remitting Multiple Sclerosis. Front Immunol. 2020 Oct 27;11:548604. doi: 10.3389/fimmu.2020.548604. eCollection 2020.

Biospecimen

Retention: SAMPLES WITHOUT DNA

Serum/plasma samples

MeSH Terms

Conditions

Multiple SclerosisRecurrenceThrombosis

Interventions

Blood Specimen CollectionPartial Thromboplastin Time

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System DiseasesDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsEmbolism and ThrombosisVascular DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

Specimen HandlingClinical Laboratory TechniquesDiagnostic Techniques and ProceduresDiagnosisPuncturesSurgical Procedures, OperativeInvestigative TechniquesBlood Coagulation TestsHematologic TestsBlood Physiological PhenomenaCirculatory and Respiratory Physiological Phenomena

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
PROSPECTIVE
Target Duration
1 Month
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

April 30, 2020

First Posted

May 8, 2020

Study Start

September 7, 2017

Primary Completion

August 31, 2020

Study Completion

December 31, 2020

Last Updated

May 21, 2020

Record last verified: 2020-05

Locations