NCT04378855

Brief Summary

This study will ultimately aim at developing a GIMEMA platform for collecting HRQoL and symptom burden information on Italian patients with Philadelphia chromosome negative MPN. The main objective of the protocol is to improve our understanding of the impact of the disease and various treatments on patients-wellbeing, symptom burden and daily functioning.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
572

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started May 2020

Longer than P75 for all trials

Geographic Reach
1 country

25 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 28, 2020

Completed
9 days until next milestone

First Posted

Study publicly available on registry

May 7, 2020

Completed
22 days until next milestone

Study Start

First participant enrolled

May 29, 2020

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 15, 2023

Completed
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

November 15, 2025

Completed
Last Updated

September 23, 2025

Status Verified

September 1, 2025

Enrollment Period

3.5 years

First QC Date

April 28, 2020

Last Update Submit

September 17, 2025

Conditions

Outcome Measures

Primary Outcomes (1)

  • Compare HRQoL profiles of Philadelphia chromosome negative MPN patients with those of their peers in the general population

    To detect a baseline difference of at least 4 points between MPN patients and their peers in the general population in any of the following primary scales of the EORTC QLQ-C30 questionnaire: fatigue, global QoL/health status, physical, emotional and role functioning (all ranging from 0 to 100 points).

    After 5 years from study entry

Secondary Outcomes (10)

  • Compare HRQoL profiles of Philadelphia chromosome negative MPN patients with those of their peers in the general population

    After 5 years from study entry

  • Compare HRQoL profiles of Philadelphia chromosome negative MPN patients with those of their peers in the general population

    After 5 years from study entry

  • MPN patients' baseline profiles of self-reported HRQoL

    After 5 years from study entry

  • Prognostic value of baseline patients' self-reported fatigue

    After 5 years from study entry

  • Prognostic value of baseline patients' self-reported HRQoL

    After 5 years from study entry

  • +5 more secondary outcomes

Interventions

Quality of life assessment

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Adult patients with myeloproliferative neoplasms (MPN)

You may qualify if:

  • Patients diagnosed with Polycythemia Vera (PV), Essential Thrombocythemia (ET) and Primary Myelofibrosis (pre-PMF, overt-PMF) and post-ET/post-PV Myelofibrosis (MF), (i.e. Philadelphia chromosome negative myeloproliferative neoplasm (MPN)) according to 2016 WHO classification.
  • Known IPSS/IPSET/DIPSS risk score category at time of initial diagnosis of PV, ET and PMF, respectively.
  • Initial diagnosis of MPN within one year before date of registration.
  • Having a full baseline PRO Evaluation completed.
  • Adult patients (≥ 18 years old).
  • Written informed consent provided.

You may not qualify if:

  • Having any kind of psychiatric disorder or major cognitive dysfunction problems hampering a self-reported evaluation.
  • Not able to read and understand local language (i.e. Italian).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

Aon Ss. Antonio E Biagio E C. Arrigo - Alessandria - Soc Ematologia

Alessandria, Italy

Location

Asl Di Asti, Ospedali Riuniti - Presidio Ospedaliero Cardinal G. Massaia - Sc Oncologia

Asti, Italy

Location

Aou Consorziale Policlinico - Bari - Uo Ematologia Con Trapianto

Bari, Italy

Location

Irccs Oncologico Istituto Tumori Giovanni Paolo Ii - Bari - Uo Ematologia

Bari, Italy

Location

Istituto di Ematologia "Lorenzo e A. Seragnoli"

Bologna, Italy

Location

Ao Brotzu, Presidio Ospedaliero A. Businco - Cagliari - Sc Ematologia E Ctmo

Cagliari, Italy

Location

Aou Careggi - Firenze - Sod Ematologia

Florence, Italy

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico UOC Oncoematologia- Padiglione Marcora 2° piano

Milan, Italy

Location

Aou Di Modena - Sc Ematologia

Modena, Italy

Location

Azienda Ospedaliera "S.Gerardo"

Monza, Italy

Location

Aou Federico Ii - Napoli - Uoc Ematologia

Napoli, Italy

Location

.C.D.U. Ematologia - Università del Piemonte Orientale Amedeo Avogadro

Novara, Italy

Location

Aou Policlinico P. Giaccone - Palermo - Uo Ematologia

Palermo, Italy

Location

Fondazione Ircss Policlinico San Matteo - Pavia - Uo Ematologia

Pavia, Italy

Location

Aou Pisana - Uo Ematologia Universitaria

Pisa, Italy

Location

Ausl Di Reggio Emilia - Arcispedale Santa Maria Nuova, Irccs - Sc Ematologia

Reggio Emilia, Italy

Location

Ausl Della Romagna, Ospedale "Infermi" - Rimini - Uo Ematologia

Rimini, Italy

Location

C.R.O.B. - I.R.C.C.S. - Rionero in Volture - Uoc Ematologia

Rionero in Vulture, Italy

Location

Asl Roma 2, Ospedale S. Eugenio- Ospedale S.Eugenio - Uoc Ematologia

Roma, Italy

Location

Fondazione Policlinico Universitario Agostino Gemelli Irccs - Roma - Area Ematologica

Roma, Italy

Location

Università Degli Studi Di Roma "Sapienza" - Dipartimento Di Medicina Traslazionale E Di Precisione - U.O.C. Ematologia

Roma, Italy

Location

Aou Di Sassari - Cliniche Universitarie - Stabilimento Cliniche Di San Pietro - Uoc Ematologia

Sassari, Italy

Location

Aou Città Della Salute E Della Scienza, Ospedale S. Giovanni Battista Molinette - Torino - Sc Ematologia - Università Degli Studi Di Torino

Torino, Italy

Location

Asl to 2, Torino Nord Emergenza San Giovanni Bosco - Ssd Ematologia

Torino, Italy

Location

Ospedale Mauriziano Umberto I - Torino - Scdu Ematologia

Torino, Italy

Location

MeSH Terms

Conditions

Myeloproliferative Disorders

Interventions

Surveys and Questionnaires

Condition Hierarchy (Ancestors)

Bone Marrow DiseasesHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Data CollectionEpidemiologic MethodsInvestigative TechniquesHealth Care Evaluation MechanismsQuality of Health CareHealth Care Quality, Access, and EvaluationPublic HealthEnvironment and Public Health

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 28, 2020

First Posted

May 7, 2020

Study Start

May 29, 2020

Primary Completion

November 15, 2023

Study Completion

November 15, 2025

Last Updated

September 23, 2025

Record last verified: 2025-09

Data Sharing

IPD Sharing
Will not share

Locations