NCT04351243

Brief Summary

Study KIN-1901-2001 is a multi-center, adaptive, randomized, double-blind, placebo-controlled study to assess the efficacy and safety of gimsilumab in subjects with lung injury or acute respiratory distress syndrome (ARDS) secondary to COVID-19.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
227

participants targeted

Target at P50-P75 for phase_2 covid19

Timeline
Completed

Started Apr 2020

Typical duration for phase_2 covid19

Geographic Reach
1 country

33 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 15, 2020

Completed
Same day until next milestone

Study Start

First participant enrolled

April 15, 2020

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 17, 2020

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2020

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2021

Completed
8 months until next milestone

Results Posted

Study results publicly available

December 10, 2021

Completed
Last Updated

December 14, 2021

Status Verified

December 1, 2021

Enrollment Period

8 months

First QC Date

April 15, 2020

Results QC Date

November 26, 2021

Last Update Submit

December 10, 2021

Conditions

Keywords

Granulocyte macrophage-colony stimulating factor (GM-CSF)ImmunomodulatorCytokine stormCOVID-19CoronavirusSevere Acute Respiratory Syndrome (SARS)Lung InjuryMonoclonal antibody

Outcome Measures

Primary Outcomes (1)

  • Incidence of Mortality

    "Incidence" is defined as the percent of subjects that died by Day 43

    Day 43

Secondary Outcomes (3)

  • Proportion of Subjects Who Are Alive and Not on Mechanical Ventilation

    Day 29

  • Number of Ventilator-free Days

    Baseline to Day 29

  • Time to Hospital Discharge

    Baseline to Day 43

Study Arms (2)

Gimsilumab

EXPERIMENTAL

Gimsilumab 400 mg on Day 1 Gimsilumab 200 mg on Day 8

Drug: Gimsilumab

Placebo

PLACEBO COMPARATOR

Normal saline on Day 1 Normal saline on Day 8

Drug: Placebo

Interventions

Gimsilumab is a fully human monoclonal antibody (mAb).

Also known as: KIN-1901
Gimsilumab

Normal saline

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or non-pregnant female age ≥18 years, inclusive
  • Subject (or legally authorized representative) is able and willing to provide written informed consent, which includes compliance with study requirements and restrictions listed in the consent form
  • Has laboratory-confirmed SARS-CoV-2 infection as determined by PCR or other approved clinical testing prior to randomization
  • Radiographic evidence of bilateral infiltrates
  • Subject requires high-flow oxygen or meets clinical classification for ARDS
  • Elevated serum CRP or ferritin

You may not qualify if:

  • Evidence of life-threatening dysrhythmia or cardiac arrest on presentation
  • Intubated \>72 hours
  • Absolute neutrophil count \< 1,000 per mm3
  • Platelet count \< 50,000 per mm3
  • AST or ALT \> 5X upper limit of normal
  • eGFR \<30 mL/min/1.73m2 or requiring hemofiltration or dialysis
  • History of known anti-GM-CSF autoantibodies or pulmonary alveolar proteinosis
  • Severe chronic respiratory disease (e.g., COPD, PAH, IPF, ILD) requiring supplemental oxygen therapy or mechanical ventilation pre-hospitalization (e.g., prior to COVID-19 diagnosis)
  • Use of any immunomodulatory biologic, cell therapy, or small molecule JAK inhibitor within past 7 days or 5 half lives or planned use of any of these agents unless approved by medical monitor
  • Chronic (\>4 weeks) use of corticosteroids \>10mg/day of prednisone or equivalent
  • Known or suspected active and untreated TB, HIV, hepatitis B or C infection

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

Banner University Medical Center

Phoenix, Arizona, 85006, United States

Location

HonorHealth John C. Lincoln Medical Center

Phoenix, Arizona, 85020, United States

Location

HonorHealth Scottsdale Osborn Medical Center

Scottsdale, Arizona, 85251, United States

Location

HonorHealth

Scottsdale, Arizona, 85258, United States

Location

HonorHealth Scottsdale Shea Medical Center

Scottsdale, Arizona, 85260, United States

Location

Banner University Medical Center

Tucson, Arizona, 85719, United States

Location

UCLA Ronald Reagan Medical Center

Los Angeles, California, 90095, United States

Location

University of Florida

Gainesville, Florida, 32610, United States

Location

Miami Cancer institute

Miami, Florida, 33176, United States

Location

Piedmont Healthcare

Atlanta, Georgia, 30309, United States

Location

Emory University School of Medicine

Atlanta, Georgia, 30322, United States

Location

NorthShore University HealthSystem

Evanston, Illinois, 60201, United States

Location

East Jefferson General Hospital

Metairie, Louisiana, 70006, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Beaumont Hospital - Royal Oak

Royal Oak, Michigan, 48073, United States

Location

Jamaica Hospital Medical Center

Jamaica, New York, 11418, United States

Location

Mount Sinai Beth Israel

New York, New York, 10003, United States

Location

Mount Sinai West

New York, New York, 10019, United States

Location

Mount Sinai Morningside

New York, New York, 10025, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, 19140, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Baylor Jack & Jane Hamilton Heart and Vascular Hospital

Dallas, Texas, 75226, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

Baylor Scott & White All Saints Medical Center

Fort Worth, Texas, 75061, United States

Location

Memorial Hermann Hospital Affiliated with University of Texas Health Science Center at Houston, McGovern Medical School

Houston, Texas, 77030, United States

Location

Baylor Scott & White Medical Center

Irving, Texas, 75061, United States

Location

Baylor Scott & White Heart Hospital

Plano, Texas, 75093, United States

Location

Baylor Scott & White Medical Center

Plano, Texas, 75093, United States

Location

Baylor Scott & White Medical Center

Round Rock, Texas, 78665, United States

Location

Baylor Scott & White Medical Center

Temple, Texas, 76508, United States

Location

Inova Fairfax Medical Campus

Falls Church, Virginia, 22042, United States

Location

Related Publications (1)

  • Criner GJ, Lang FM, Gottlieb RL, Mathews KS, Wang TS, Rice TW, Madduri D, Bellam S, Jeanfreau R, Case AH, Glassberg MK, Lyon GM, Ahmad K, Mendelson R, DiMaio JM, Tran MP, Spak CW, Abbasi JA, Davis SG, Ghamande S, Shen S, Sherman L, Lowry S. Anti-Granulocyte-Macrophage Colony-Stimulating Factor Monoclonal Antibody Gimsilumab for COVID-19 Pneumonia: A Randomized, Double-Blind, Placebo-controlled Trial. Am J Respir Crit Care Med. 2022 Jun 1;205(11):1290-1299. doi: 10.1164/rccm.202108-1859OC.

MeSH Terms

Conditions

COVID-19Cytokine Release SyndromeCoronavirus InfectionsSevere Acute Respiratory SyndromeLung Injury

Interventions

gimsilumab

Condition Hierarchy (Ancestors)

Pneumonia, ViralPneumoniaRespiratory Tract InfectionsInfectionsVirus DiseasesCoronaviridae InfectionsNidovirales InfectionsRNA Virus InfectionsLung DiseasesRespiratory Tract DiseasesSystemic Inflammatory Response SyndromeInflammationPathologic ProcessesPathological Conditions, Signs and SymptomsShockThoracic InjuriesWounds and Injuries

Limitations and Caveats

The Sponsor stopped enrollment of subjects prior to achieving the planned sample size of 270. At the completion of study enrollment, 227 subjects were randomized and 225 received at least one dose of gimsilumab or placebo. All randomized subjects (227 subjects), where possible, completed all study-related activities and had data collected through the planned Day 43 and Day 169 analyses. No safety findings were observed which warranted study termination.

Results Point of Contact

Title
Simon Lowry, MD, Chief Medical Officer
Organization
Kinevant Sciences, Inc. on behalf of Kinevant Sciences GmbH

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 15, 2020

First Posted

April 17, 2020

Study Start

April 15, 2020

Primary Completion

December 1, 2020

Study Completion

April 1, 2021

Last Updated

December 14, 2021

Results First Posted

December 10, 2021

Record last verified: 2021-12

Data Sharing

IPD Sharing
Will not share

Locations