NCT04322149

Brief Summary

This is a Phase 2a, multi-center, open label, multiple dose study of AT-1501, a humanized monoclonal antibody antagonist to CD40 ligand (CD40L). Approximately 54 adults with Amyotrophic Lateral Sclerosis (ALS) will be enrolled into the study in the United States and Canada at approximately 13 ALS treatment sites. Participants will be enrolled into one of four ascending doses.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
54

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Oct 2020

Shorter than P25 for phase_2

Geographic Reach
2 countries

13 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 20, 2020

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 26, 2020

Completed
7 months until next milestone

Study Start

First participant enrolled

October 16, 2020

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 24, 2022

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 24, 2022

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

June 28, 2023

Completed
Last Updated

June 28, 2023

Status Verified

June 1, 2023

Enrollment Period

1.4 years

First QC Date

March 20, 2020

Results QC Date

May 10, 2023

Last Update Submit

June 6, 2023

Conditions

Keywords

ALSLou Gehrig's Diseasemotor neuron diseasemotor neuron degenerationAT-1501humanized blocking antibody to CD40LGCD40L inhibitormonoclonal antibody

Outcome Measures

Primary Outcomes (2)

  • Safety and Tolerability

    Incidence of adverse events (AEs) reported as number of participants with at least one TEAE (Treatment Emergent Adverse Event) and at least one SAE (Serious Adverse Event).

    Up to 18 Weeks

  • Safety and Tolerability

    Incidence of adverse events (AEs) reported as number of TEAEs (Treatment Emergent Adverse Events) having occurred.

    Up to 18 Weeks

Study Arms (1)

AT-1501

EXPERIMENTAL

4 sequential dose cohorts

Drug: AT-1501

Interventions

AT-1501 monoclonal antibody targeting CD40L given as an IV infusion

AT-1501

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • ALS diagnosed as possible, laboratory supported probable, probable, or definite as defined by revised El Escorial criteria
  • ALS Functional Rating Scale - Revised (ALSFRS-R) Aggregate score of 37 or greater
  • No more than 24 months from diagnosis

You may not qualify if:

  • Any other central or peripheral nervous system disease that may interfere with the evaluation of ALS or its progression
  • Presence of a tracheostomy, or use of permanent assistive ventilation (ventilatory support for 23 hours per day or more)
  • History of malignancy within the previous 5 years, except for localized non-melanoma skin cancers
  • Abnormal function of the immune system resulting from:
  • Clinical conditions affecting the immune system (e.g. HIV infection, agammaglobulinemia),
  • Systemic administration of corticosteroids (PO/IV/IM) at a dose equivalent to 20 mg/day of prednisone for more than 14 consecutive days within 90 days prior to screening,
  • Administration of anti-neoplastic and/or immunomodulating agents (e.g. Tumor necrosis factor alpha (TNF α) antagonists or anti-B cell antibodies) or radiotherapy within 1 year prior to screening.
  • Recipient of Stem Cell or Gene Therapy
  • Positive test for Hepatitis B surface antigen, Hepatitis C antibody, or HIV.
  • History of deep venous thrombosis or pulmonary embolism
  • History of active substance abuse within the past 2 years
  • History of stroke, poorly controlled or significant cardiovascular disease, diabetes

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Barrows Neurological Institute

Phoenix, Arizona, 85013, United States

Location

University of California Irvine

Orange, California, 92868, United States

Location

California Pacific Medical Center

San Francisco, California, 94109, United States

Location

Augusta University

Augusta, Georgia, 30912, United States

Location

University of Indiana

Indianapolis, Indiana, 46202, United States

Location

The University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Johns Hopkins University Medical Center

Baltimore, Maryland, 21287, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Hospital for Special Surgery (HSS)

New York, New York, 10021, United States

Location

Providence Brain & Spine Institute

Portland, Oregon, 97213, United States

Location

Texas Neurology, P.A.

Dallas, Texas, 75206, United States

Location

Houston Methodist Neurological Institute

Houston, Texas, 77030, United States

Location

Montreal Neurological Institute and Hospital

Montreal, H3A 2B4, Canada

Location

Related Publications (1)

  • Perrin S, Ladha S, Maragakis N, Rivner MH, Katz J, Genge A, Olney N, Lange D, Heitzman D, Bodkin C, Jawdat O, Goyal NA, Bornstein JD, Mak C, Appel SH, Paganoni S. Safety and tolerability of tegoprubart in patients with amyotrophic lateral sclerosis: A Phase 2A clinical trial. PLoS Med. 2024 Oct 31;21(10):e1004469. doi: 10.1371/journal.pmed.1004469. eCollection 2024 Oct.

MeSH Terms

Conditions

Amyotrophic Lateral SclerosisMotor Neuron Disease

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesNervous System DiseasesNeurodegenerative DiseasesTDP-43 ProteinopathiesNeuromuscular DiseasesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic Diseases

Results Point of Contact

Title
Laura Batterman
Organization
Eledon Pharmaceuticals

Study Officials

  • Jeff Bornstein, MD

    Eledon Pharmaceuticals

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 20, 2020

First Posted

March 26, 2020

Study Start

October 16, 2020

Primary Completion

March 24, 2022

Study Completion

March 24, 2022

Last Updated

June 28, 2023

Results First Posted

June 28, 2023

Record last verified: 2023-06

Locations