NCT04225312

Brief Summary

Rationale: Natalizumab is an effective drug in the treatment for relapsing remitting multiple sclerosis (RRMS) and is approved by de FDA/EMA in a treatment regimen of 4-weekly 300mg natalizumab infusions. Natalizumab trough concentrations after a 4-weekly interval are high in the large majority of patients which implies a relative overdose in most patients. A recent randomized controlled trial (RCT) suggests natalizumab maintains a high level of effi-cacy in stable patients with RRMS switching to a 6 week interval. Our study group demon-strated that efficacy of natalizumab is maintained when the infusion interval is extended based on natalizumab trough concentrations (personalized extended interval dosing). This leads to fewer hospital visits, a decrease of healthcare costs and decrease of risk of compli-cations of natalizumab treatment. Objective: Our objective is to test feasibility and validate safety of personalized extended interval dosing of natalizumab starting from 6 weeks in a large real-life cohort across the Netherlands. Study design: Prospective national phase IV natalizumab cohort study. Study population: All patients, aged 18 years or older, who are currently treated with natalizumab in the Netherlands for RRMS, with a minimum of 6 consecutive infusions. Intervention: All patients currently included in the NEXT-MS trial will receive an adjusted personalized extended interval dosing treatment regimen of natalizumab based on natalizumab concentrations starting from an infusion interval of 6 weeks. Main study parameters/endpoints: Our main study endpoint is the safety (defined by radiological disease activity) of personalized natalizumab dosing in a large real-life cohort across the Netherlands. Data will be collected regarding disease activity and disability progression. A cost analysis will be performed to show the extent of cost reduction. Patients will be annually followed to assess the influence of personalized dosing on JC virus conversion, JC virus index, incidence of progressive multifocal leukoencephalopathy, treatment satisfaction and quality of life. The influence of personalized dosing on pharmacokinetics will be monitored.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
300

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started Feb 2020

Longer than P75 for phase_4

Geographic Reach
1 country

24 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 3, 2020

Completed
10 days until next milestone

First Posted

Study publicly available on registry

January 13, 2020

Completed
21 days until next milestone

Study Start

First participant enrolled

February 3, 2020

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2025

Completed
Last Updated

April 27, 2023

Status Verified

April 1, 2023

Enrollment Period

5.1 years

First QC Date

January 3, 2020

Last Update Submit

April 25, 2023

Conditions

Keywords

NatalizumabExtended interval dosing

Outcome Measures

Primary Outcomes (1)

  • Change of T2 lesions on brain MRI

    Assessing new/enlarging T2 lesions on brain MRI

    Baseline, year 1, year 2

Secondary Outcomes (13)

  • Annualized relapse rate

    Baseline, year 1, year 2

  • Disability progression during follow-up

    Baseline, year 1, year 2

  • Cost analysis

    Baseline, year 1, year 2

  • JC virus conversion

    6 monthly JCV measurement for two years

  • Course JC virus index

    6 monthly JCV measurement for two years

  • +8 more secondary outcomes

Study Arms (3)

Personalized extended interval dosing

EXPERIMENTAL

Patients will be receiving a personalized dosing schedule from 6 weeks, which will be further extended if the trough level exceeds 10 ug/ml.

Drug: Personalized extended interval dosing of natalizumab

Standard interval dosing

OTHER

Patients who prefer to stay on standard interval dosing.

Drug: Standard interval dosing

Historic cohort

OTHER

Historic cohort of natalizumab treated patients on standard interval dosing.

Drug: Standard interval dosing

Interventions

Personalized extended interval dosing of natalizumab with a schedule from every 6 weeks, which will be further extended if the trough level exceeds 10 ug/ml.

Also known as: EID
Personalized extended interval dosing

Standard interval dosing in control group and historic group

Also known as: SID
Historic cohortStandard interval dosing

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of relapsing remitting multiple sclerosis according to the 2017 criteria
  • or more consecutive natalizumab infusions
  • years or older
  • Agreed to participate (written informed consent)

You may not qualify if:

  • High titer natalizumab (\>100 arbitrary units (AU)/ml) antibodies
  • Contraindication for frequent magnetic resonance imaging (MRI) (ie, pacemaker or other contraindicated implanted metal devices, or have claustrophobia that cannot be medically managed)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

Jeroen Bosch Hospital

's-Hertogenbosch, Netherlands

Location

Ziekenhuisgroep Twente hospital

Almelo, Netherlands

Location

Flevoziekenhuis

Almere Stad, Netherlands

Location

Amsterdam UMC, location VUmc

Amsterdam, Netherlands

Location

OLVG

Amsterdam, Netherlands

Location

Rijnstate Hospital

Arnhem, Netherlands

Location

Wilhelmina hospital Assen

Assen, Netherlands

Location

Amphia Hospital

Breda, Netherlands

Location

Reinier de Graaf hospital

Delft, Netherlands

Location

Slingeland Hospital

Doetinchem, Netherlands

Location

Ommelander Hospital Groningen

Groningen, Netherlands

Location

University Medical Center Groningen

Groningen, Netherlands

Location

Spaarne gasthuis hospital

Haarlem, Netherlands

Location

Sint-Jansdal Hospital

Harderwijk, Netherlands

Location

Medisch Centrum Leeuwarden

Leeuwarden, Netherlands

Location

Alrijne Hospital

Leiden, Netherlands

Location

Maasstad hospital

Maastricht, Netherlands

Location

Canisius Wilhelmina Hospital

Nijmegen, Netherlands

Location

Erasmus Medical Center

Rotterdam, Netherlands

Location

Haaglanden Medical Center

The Hague, Netherlands

Location

Elizabeth tweesteden Hospital

Tilburg, Netherlands

Location

Diakonessenhuis

Utrecht, Netherlands

Location

St. Antonius Hospital

Utrecht, Netherlands

Location

Isala

Zwolle, Netherlands

Location

Related Publications (2)

  • Foley JF, Defer G, Ryerson LZ, Cohen JA, Arnold DL, Butzkueven H, Cutter G, Giovannoni G, Killestein J, Wiendl H, Smirnakis K, Xiao S, Kong G, Kuhelj R, Campbell N; NOVA study investigators. Comparison of switching to 6-week dosing of natalizumab versus continuing with 4-week dosing in patients with relapsing-remitting multiple sclerosis (NOVA): a randomised, controlled, open-label, phase 3b trial. Lancet Neurol. 2022 Jul;21(7):608-619. doi: 10.1016/S1474-4422(22)00143-0. Epub 2022 Apr 25.

    PMID: 35483387BACKGROUND
  • Toorop AA, van Lierop ZY, Gelissen LM, Hoitsma E, Zeinstra EM, van Rooij LC, van Munster CE, Vennegoor A, Mostert JP, Wokke BH, Kalkers NF, Hoogervorst EL, van Eijk JJ, Roosendaal CM, Kragt JJ, Eurelings M, van Genugten J, Nielsen J, Sinnige L, Kloosterziel ME, Arnoldus EP, van Dijk GW, Bouvy WH, Wessels MH, Boonkamp L, Strijbis EM, van Oosten BW, De Jong BA, Lissenberg-Witte BI, Barkhof F, Moraal B, Teunissen CE, Rispens T, Uitdehaag BM, Killestein J, van Kempen ZL. Prospective trial of natalizumab personalised extended interval dosing by therapeutic drug monitoring in relapsing-remitting multiple sclerosis (NEXT-MS). J Neurol Neurosurg Psychiatry. 2024 Apr 12;95(5):392-400. doi: 10.1136/jnnp-2023-332119.

MeSH Terms

Conditions

Multiple Sclerosis, Relapsing-Remitting

Condition Hierarchy (Ancestors)

Multiple SclerosisDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: Prospective national phase IV natalizumab cohort study
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal investigator

Study Record Dates

First Submitted

January 3, 2020

First Posted

January 13, 2020

Study Start

February 3, 2020

Primary Completion

March 1, 2025

Study Completion

March 1, 2025

Last Updated

April 27, 2023

Record last verified: 2023-04

Locations