NCT04180215

Brief Summary

This is a First in Human (FIH) Phase I/II, multinational, multicenter, open-label study of HB-201 single vector therapy and HB-201 \& HB-202 two-vector therapy in patients with HPV 16+ confirmed cancers comprising two parts: Phase I Dose Escalation and Phase II Dose Expansion.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
198

participants targeted

Target at P75+ for phase_1

Timeline
Completed

Started Dec 2019

Longer than P75 for phase_1

Geographic Reach
3 countries

34 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 20, 2019

Completed
2 months until next milestone

First Posted

Study publicly available on registry

November 27, 2019

Completed
14 days until next milestone

Study Start

First participant enrolled

December 11, 2019

Completed
5.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 9, 2025

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 9, 2025

Completed
Last Updated

September 15, 2025

Status Verified

September 1, 2025

Enrollment Period

5.1 years

First QC Date

September 20, 2019

Last Update Submit

September 8, 2025

Conditions

Keywords

VaccineGene TherapyTheraT®E7E6HPV 16 E7E6HNSCCHPV 16+ head and neck squamous cell cancerOropharyngeal cancerHPV16HPV 16Head and neck cancerCarcinomaCarcinoma, squamous cellSquamous cell carcinoma of head and neckNeoplasms, squamous cellHead and neck neoplasmsPembrolizumab

Outcome Measures

Primary Outcomes (2)

  • Phase I Dose Escalation: Determine Phase II dose based on incidence of dose-limiting toxicities.

    Determine the recommended Phase II dose in terms of safety and tolerability for intravenously administered HB-201, and intravenously administered HB-202 by assessing drug limiting toxicities.

    From dosing until 21-28 days after first dose

  • Phase II Dose Expansion: Number of participants with preliminary antitumor activity based on objective response rate.

    Assess the preliminary antitumor activity of dosage regimens of HB-201 and HB-202 using Response Evaluation Criteria in Solid Tumors (RECIST) to determine objective response rate (ORR).

    Until progression, (estimated up to 30-months)

Secondary Outcomes (4)

  • Phase I Dose Escalation: Number of participants with adverse events (type, frequency, severity).

    From informed consent through 30 days after last dose.

  • Phase I Dose Escalation: Number of participants with preliminary antitumor activity based on objective response rate and disease control rate.

    Until progression, (estimated up to 30-months)

  • Phase II Dose Expansion: Number of participants with confirmed duration of preliminary antitumor activity.

    Up to 30-months (until progression)

  • Phase II Dose Expansion: Number of participants with adverse events (type, frequency, severity).

    From informed consent through 30 days after last dose

Study Arms (6)

Ph I, Group 1 and Group 2

EXPERIMENTAL

Patients with HPV 16+ HNSCC or Non-HNSCC who had tumor progression or recurrence on standard of care therapy.

Drug: HB-201 intravenous administration.

Ph I, Group 3 and Group 4

EXPERIMENTAL

Patients with HPV 16+ HNSCC or Non-HNSCC who had tumor progression or recurrence on standard of care therapy.

Drug: HB-202 intravenous administration alternating with HB-201 intravenous administration.

Ph II, Group B

EXPERIMENTAL

Patients with HPV 16+ HNSCC who are eligible to receive immune checkpoint inhibitor as part of standard of care.

Drug: HB-201 intravenous administration + standard of care regimen including pembrolizumab.

Ph II, Group E

EXPERIMENTAL

Patients with HPV 16+ HNSCC who are eligible to receive pembrolizumab as part of 1L standard of care.

Drug: HB-202 / HB-201 alternating intravenous administration + standard of care regimen including pembrolizumab.

Ph II, Group F

EXPERIMENTAL

Patients with HPV 16+ cancers who had tumor progression or recurrence on standard of care therapy and who are eligible to receive pembrolizumab as part of 2L+ standard of care..

Drug: HB-202 / HB-201 alternating intravenous administration + pembrolizumab.

Ph I, sub-study

EXPERIMENTAL

Patients with HPV 16+ HNSCC who had tumor progression or recurrence on standard of care therapy

Drug: HB-201 or HB-201/HB-202 alternating treatment using CD8 PET Tracer (Zr-Df-IAB22M2C)

Interventions

Dose / Schedule determined by 3+3 dose escalation (3 to 6 patients per cohort).

Ph I, Group 1 and Group 2

Dose / Schedule determined by 3+3 dose escalation (3 to 6 patients per cohort).

Ph I, Group 3 and Group 4

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • All Patients:
  • Documentation of confirmed HPV 16+ cancer via genotype testing.
  • ≥ 1 measurable lesion by imaging for tumor response following RECIST
  • ECOG performance status of 0 to 1.
  • Prior curative radiation therapy and prior focal palliative completed per protocol-specified wash-out windows.
  • Screening laboratory values must meet protocol-specified criteria.
  • Able to provide tumor tissue following last treatment, unless otherwise agreed.
  • Treatment Group E or Group F:
  • Documentation of confirmed head and neck squamous cell carcinoma.
  • Eligible to receive pembrolizumab, per standard of care and product label.
  • Group E: this group includes first line / 1L patients who have not yet received treatment in the metastatic/recurrent setting.
  • Group F: Tumor progression or recurrence on standard of care therapy, including ≥1 systemic therapy.
  • Imaging Sub-Study (for specific participants at Memorial Sloan Kettering Cancer Center only):
  • At least 1 non-irradiated measurable lesion documented through imaging.

You may not qualify if:

  • All patients:
  • Metastatic central nervous system disease, and/or carcinomatous meningitis.
  • Any serious or uncontrolled medical disorder that, in the opinion of the Investigator, may increase the risk associated with study participation / treatment administration.
  • Concurrent malignancy that is clinically significant or requires active intervention, unless protocol-defined criteria are met.
  • Active, known or suspected, autoimmune or inflammatory disorders requiring immunosuppressive therapy.
  • Has a life expectancy of less than 3 months.
  • Any toxicities attributed to systemic prior anticancer therapy o that have not resolved to Grade 1 or baseline prior to the first administration of study drug, unless protocol-defined criteria is met.
  • Not meeting the protocol-specified washout periods for prohibited medications.
  • Prior anaphylactic reaction to or known allergy or hypersensitivity to investigational product(s) or any of the excipients of the investigational product(s).
  • Positive hepatitis B surface antigen (HBsAg) or hepatitis C virus (HCV) antibody, indicating acute or chronic infection.
  • Known history of acquired immunodeficiency syndrome.
  • For patients in Groups E or F and certain backfill cohorts:
  • History of severe hypersensitivity reaction to or other contraindication to receiving pembrolizumab.
  • History of/Presently having non-infectious pneumonitis requiring treatment.
  • Was discontinued due to a Grade 3 or higher immune-related AE (irAE) after receiving prior therapy with check point inhibitors.
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (34)

O'Neal Comprehensive Cancer Center at UAB

Birmingham, Alabama, 35294, United States

Location

Banner MD Anderson Cancer Center

Gilbert, Arizona, 85234, United States

Location

University of Arkansas for Medical Sciences, Cancer Institute, Clinical Trials Office

Fayetteville, Arkansas, 72205, United States

Location

USC/Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

UCLA (University of California, Los Angeles)

Los Angeles, California, 90095, United States

Location

Sylvester Comprehensive Cancer Center

Miami, Florida, 33136, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

Loyola University Medical School

Maywood, Illinois, 60153, United States

Location

University of Iowa Hospitals & Clinics

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center

Fairway, Kansas, 66205, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

Nebraska Methodist Hospital

Omaha, Nebraska, 68114, United States

Location

Rutgers Cancer Institute of New Jersey

New Brunswick, New Jersey, 08903, United States

Location

Grossman School of Medicine

New York, New York, 10016, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10021, United States

Location

Icahn School of Medicine at Mount Sinai

New York, New York, 10029, United States

Location

Perlmutter Cancer Center at NYU Langone Hospital-Long Island

New York, New York, 11501, United States

Location

Montefiore-Einstein Center for Cancer Care

The Bronx, New York, 10461, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

University of Oklahoma Health Sciences Center

Oklahoma City, Oklahoma, 73104, United States

Location

Providence Portland Medical Center

Portland, Oregon, 97213, United States

Location

Greenville Hospital System University Medical Center (ITOR)

Greenville, South Carolina, 29605, United States

Location

The University of Texas MD Anderson Cancer Center

Houston, Texas, 77030, United States

Location

University of Virgina Health System

Charlottesville, Virginia, 22908, United States

Location

Froedtert Hospital and Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Amsterdam UMC, Locatie VUMC

Amsterdam, 1081, Netherlands

Location

Hospital Universitari Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Clinic de Barcelona

Barcelona, 08036, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, 8041, Spain

Location

Hospital Universitario Fundacion Jimenez Diaz

Madrid, 28040, Spain

Location

Centro Integral Oncologico Clara Campal

Madrid, 28050, Spain

Location

Hospital Universitario Virgen Macarena

Seville, 410009, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

MeSH Terms

Conditions

Squamous Cell Carcinoma of Head and NeckOropharyngeal NeoplasmsHead and Neck NeoplasmsCarcinomaCarcinoma, Squamous CellNeoplasms, Squamous Cell

Interventions

pembrolizumab

Condition Hierarchy (Ancestors)

Neoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsNeoplasms by SitePharyngeal NeoplasmsOtorhinolaryngologic NeoplasmsPharyngeal DiseasesStomatognathic DiseasesOtorhinolaryngologic Diseases

Study Officials

  • Head of Clinical Development

    Hookipa Biotech GmbH

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 20, 2019

First Posted

November 27, 2019

Study Start

December 11, 2019

Primary Completion

January 9, 2025

Study Completion

January 9, 2025

Last Updated

September 15, 2025

Record last verified: 2025-09

Data Sharing

IPD Sharing
Will not share

Locations