NCT04145219

Brief Summary

A research study of how house dust mite tablets work compared to placebo in children aged between 5 and 11 years and who have allergy to house dust mites (MATIC)

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,460

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2019

Typical duration for phase_3

Geographic Reach
11 countries

113 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 11, 2019

Completed
1 day until next milestone

Study Start

First participant enrolled

October 12, 2019

Completed
18 days until next milestone

First Posted

Study publicly available on registry

October 30, 2019

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2023

Completed
20 days until next milestone

Study Completion

Last participant's last visit for all outcomes

April 21, 2023

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

June 12, 2024

Completed
Last Updated

June 12, 2024

Status Verified

June 1, 2024

Enrollment Period

3.5 years

First QC Date

October 11, 2019

Results QC Date

March 22, 2024

Last Update Submit

June 11, 2024

Conditions

Keywords

Allergic rhinitisHDMpediatric

Outcome Measures

Primary Outcomes (1)

  • Average Daily Total Combined Rhinitis Symptom and Medication Score (TCRS) During the Primary Efficacy Assessment Period

    The primary endpoint in the trial was the average daily total combined rhinitis symptoms and medication score (TCRS) during the primary efficacy assessment period. The average daily TCRS evaluates the treatment effect based on the reduction in daily rhinitis symptoms and medication score (on a scale of 0-24). Higher scores indicate more severe symptoms and/or more use of rhinitis medication. The endpoint is calculated as the average score of all reported daily values during the 8-week primary efficacy assessment period. For example, if a subject reported 56 daily TCRS values, the primary endpoint is calculated as the average of those values.

    8 weeks (primary efficacy assessment period), which started 44-49 weeks after initiation of IMP

Secondary Outcomes (17)

  • The Average Rhinitis Daily Symptom Score (DSS) During the Primary Efficacy Assessment Period

    8 weeks (primary efficacy assessment period), which started 44-49 weeks after initiation of IMP

  • The Average Rhinitis Daily Medication Score (DMS) During the Primary Efficacy Assessment Period

    8 weeks (primary efficacy assessment period), which started 44-49 weeks after initiation of IMP

  • The Average Daily Total Combined Rhinoconjunctivitis Symptom and Medication Score (TCS) During the Primary Efficacy Assessment Period

    8 weeks (primary efficacy assessment period), which started 44-49 weeks after initiation of IMP

  • The Average Rhinoconjunctivitis Daily Symptom Score (DSS) During the Primary Efficacy Assessment Period

    8 weeks (primary efficacy assessment period), which started 44-49 weeks after initiation of IMP

  • The Average Rhinoconjunctivitis Daily Medication Score (DMS) During the Primary Efficacy Assessment Period

    8 weeks (primary efficacy assessment period), which started 44-49 weeks after initiation of IMP

  • +12 more secondary outcomes

Study Arms (2)

Active treatment

EXPERIMENTAL

HDM SLIT-tablet plus allergy and asthma rescue medication

Biological: Sublingual allergy immunotherapy tablet

Placebo

PLACEBO COMPARATOR

Placebo oral tablet plus allergy and asthma rescue medication

Other: Placebo

Interventions

For daily administration (1 tablet per day)

Also known as: Acarizax, Odactra
Active treatment
PlaceboOTHER

For daily administration (1 tablet per day)

Also known as: Placebo sublingual tablet
Placebo

Eligibility Criteria

Age5 Years - 11 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Male or female subjects aged 5-11 years
  • A clinical history of HDM AR/C (Allergic rhinitis/rhinoconjunctivitis) (with or without asthma) and with allergic rhinitis symptoms despite having received allergy pharmacotherapy during the previous year prior to screening
  • Have a certain level of AR (Allergic rhinitis) symptoms on at least 8 of the last 14 days of the baseline period
  • Use symptomatic medication for treatment of HDM allergic rhinitis during at least 8 of the last 14 days of the baseline period
  • Positive skin prick test (SPT) and IgE (Immunoglobulin E) to D. pteronyssinus or D. farinae at screening
  • Lung function ≥ 70% of predicted value

You may not qualify if:

  • Sensitised and regularly exposed to perennial allergens
  • Any nasal or pharyngeal condition that could interfere with the safety or efficacy evaluation
  • Asthma requiring treatment with high dose of inhaled corticosteroid
  • A relevant history of systemic allergic reaction

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (113)

Allergy & Asthma Specialists Medical Group and Research Center

Huntington Beach, California, 92647, United States

Location

California Allergy and Asthma Medical Group

Los Angeles, California, 90025, United States

Location

Allergy & Asthma Medical Group and Research Center, A P.C.

San Diego, California, 92123, United States

Location

Miami Clinical Research

Miami, Florida, 33155, United States

Location

Pensacola Research Consultants, Inc. d.b.a. Avanza Medical Research Center

Pensacola, Florida, 32503, United States

Location

Sarasota Clinical Research

Sarasota, Florida, 34239, United States

Location

GCP, Global Clinical Professionals

St. Petersburg, Florida, 33705, United States

Location

Aeroallergy Research Labs of Savannah, Inc.

Savannah, Georgia, 31406, United States

Location

Clinical Research Atlanta

Stockbridge, Georgia, 30281, United States

Location

Deaconess Clinic Allergy

Evansville, Indiana, 47715, United States

Location

PMG Research of McFarland Clinic

Ames, Iowa, 50010, United States

Location

Clinical Research Institute

Minneapolis, Minnesota, 55402, United States

Location

University of Missouri

Columbia, Missouri, 65201, United States

Location

Clinical Research of The Ozarks Inc

Warrensburg, Missouri, 64093, United States

Location

Summit Medical Group

Berkeley Heights, New Jersey, 07922, United States

Location

Allergy & Asthma Associates of Monmouth City

Little Silver, New Jersey, 07739, United States

Location

Allergy Partners of Western North Carolina

Asheville, North Carolina, 28801, United States

Location

The Children's Research Institute, Department of Pediatrics, University of North Carolina Children's Hospital

Chapel Hill, North Carolina, 27599, United States

Location

UNC Children's Raleigh

Raleigh, North Carolina, 27607, United States

Location

Bernstein Clinical Research Center

Cincinnati, Ohio, 45231, United States

Location

Allergy, Asthma & Clinical Research Center

Oklahoma City, Oklahoma, 73120, United States

Location

Oklahoma Institute of Allergy & Asthma Clinical Research, LLC

Oklahoma City, Oklahoma, 73131, United States

Location

Vital Prospects Clinical Research Institute, P.C.

Tulsa, Oklahoma, 74136, United States

Location

The Corvallis Clinic

Corvallis, Oregon, 97330, United States

Location

West Ashley office: Charleston Allergy & Asthma

Charleston, South Carolina, 29414, United States

Location

ADAC Research, PA

Greenville, South Carolina, 29607, United States

Location

Charleston Allergy & Asthma

Summerville, South Carolina, 29485, United States

Location

Biogenics Research Institute

San Antonio, Texas, 78229, United States

Location

Allergy, Asthma & Sinus Center, S.C.

Greenfield, Wisconsin, 53228, United States

Location

Multiprofile Hospital for active treatment, Department of Pediatrics

Gabrovo, 5300, Bulgaria

Location

Multiprofile Hospital for Active Treatment, Department of Pediatrics

Kyustendil, 2500, Bulgaria

Location

University Multiprofile Hospital for Active Treatment Sveti Georgi EAD

Plovdiv, 4002, Bulgaria

Location

University Multiprofile Hospital for Active Treatment "Sveti Georgi" EAD

Plovdiv, Bulgaria

Location

Multiprofile Hospital for Active Treatment, Department of pneumology and phthisiatrics

Razgrad, 7200, Bulgaria

Location

Outpatient Clinic for individual practice for specialized outpatient medical care in Allergology

Razgrad, 7200, Bulgaria

Location

Specialized Hospital For Active Treatment of Pneumo - Phtisiatric Diseases Dr Dimitar Gramatikov - Ruse

Rousse, 7002, Bulgaria

Location

Acibadem City Clinic Multiprofile Hospital for Active Treatment Tokuda, EAD, Clinic in Pediatrics

Sofia, 1407, Bulgaria

Location

Sv. Vratch and Sv.Sv. Kuzma i Damian

Sofia, 1408, Bulgaria

Location

Alitea-Med-Medical-Center

Sofia, 1618, Bulgaria

Location

Diagnostic-Consultative center Ritam TR

Stara Zagora, 6000, Bulgaria

Location

Halton Pediatric Allergy

Burlington, L7L 6W6, Canada

Location

Triple A Lab

Hamilton, L8S 1G5, Canada

Location

Kingston General Hospital - Division of Allergy & Immunology

Kingston, K7L 2V7, Canada

Location

CHU Ste-Justine

Montreal, H3T1C5, Canada

Location

The Montreal Children's Hospital

Montreal, H4A 3J1, Canada

Location

Niagara Clinical Research

Niagara Falls, L2G 1J4, Canada

Location

Gordon Sussman Clinical Research, Inc.

North York, Canada

Location

Clinique spécialisée en allergie de la capitale

Québec, G1V 4W2, Canada

Location

Hospital for Sick Children

Toronto, M5G 1X8, Canada

Location

Joel Liem Medicine Professional Corporation

Windsor, N8X 2G1, Canada

Location

Hôpital Morvan - Service de Pédiatrie

Brest, France

Location

CHU de Montpellier - Service Pneumologie et Addictologie

Montpellier, 34090, France

Location

Kinderarztpraxis Bramsche

Bramsche, 49565, Germany

Location

HNO praxis - Dr Yury Yarin

Dresden, 01139, Germany

Location

Klinikum der Johann-Wolfgang-Goethe Universität - Zentrum f. Kinder- u. Jugendmedizin

Frankfurt, Germany

Location

GMAP/HNO am Neckar

Heidelberg, 68120, Germany

Location

CD8 klinika

Kaunas, LT-44191, Lithuania

Location

Siauliai Republican Hospital

Šiauliai, LT-76231, Lithuania

Location

JSC Seimos gydytojas

Vilnius, LT-01118, Lithuania

Location

Center of Allergy Diagnosis and Treatment

Vilnius, LT-08109, Lithuania

Location

Inlita JSC, Santara KTC

Vilnius, Lithuania

Location

Indywidualna Specjalistyczna Praktyka Lekarska Elzbieta Matusz

Gryfice, 72-300, Poland

Location

Specjalistyczna Praktyka Lekarska Dr n. med. Joanna Orlicz-Widawska

Katowice, 40-338, Poland

Location

Centrum Medyczne ALL-MED

Krakow, 30-033, Poland

Location

Centrum Medyczne Plejady

Krakow, 30-363, Poland

Location

Poradnia Alergologiczna

Lodz, 90-141, Poland

Location

Poradnia Alergologiczna

Lodz, 90-329, Poland

Location

Alergotest s.c. Specjalistyczne Centrum Medyczne Andrzej Emeryk

Lublin, 20-050, Poland

Location

Centrum Alergologii Teresa Hofman Sp. z o.o.

Poznan, 60-214, Poland

Location

Podkarpacki Ośrodek Pulmonologii i Alergologii Sp. z o.o.

Rzeszów, 35-612, Poland

Location

Prywatny Gabinet Lekarski Malgorzata Pawlukiewicz

Rzeszów, Poland

Location

IRMED Irena Wojciechowska

Warsaw, 01-157, Poland

Location

All-Med" Specjalistyczna Opieka Medyczna, Medyczny Instytut Badawczy Marek Jutel

Wroclaw, 53-201, Poland

Location

City Children's Hospital

Kolpino, 196657, Russia

Location

Prof. V.F. Voino-Yasenetsky Krasnoyarsk State Medical University

Krasnoyarsk, 660022, Russia

Location

NRC Institute of Immunology

Moscow, 115478, Russia

Location

Moscow City Children's Hospital No 9

Moscow, 123317, Russia

Location

City Сhildren's Сlinical Polyclinic No5

Perm, 614066, Russia

Location

I.P. Pavlov Ryazan State Medical University

Ryazan, 390026, Russia

Location

Medical Technologies" Ltd.

Saint Petersburg, 191025, Russia

Location

City Children's Polyclinic No44

Saint Petersburg, 191144, Russia

Location

ArsVitae Severo-Zapad LLC

Saint Petersburg, 194223, Russia

Location

North-Western State Medical University named after I.I. Mechnikov, Ministry of Public Health of Russian Federation

Saint Petersburg, 194291, Russia

Location

Сurator LLC

Saint Petersburg, 196240, Russia

Location

City Children's Polyclinic No45

Saint Petersburg, Russia

Location

Сity Children's Polyclinic No 35

Saint Petersburg, Russia

Location

Smolensk State Medical University

Smolensk, 214019, Russia

Location

Scientific Medical Center for General Therapy and Pharmacology

Stavropol, 355000, Russia

Location

Regional Children's Hospital

Tomsk, 634009, Russia

Location

Alersa, s.r.o, Ambulancia klinickej alergológie a imunológie

Košice, Slovakia

Location

Ambulancia klinickej imunologie a alergologie

Levice, 93501, Slovakia

Location

ALFA EL, Imunoalergologická ambulancia

Poprad, 05801, Slovakia

Location

Ambulancia klinickej imunologie a alergologie

Šurany, 94201, Slovakia

Location

Hospital Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Sant Joan de Deu

Esplugues de Llobregat, 08950, Spain

Location

Hospital Universitario de Jerez de la Frontera

Jerez de la Frontera, 11407, Spain

Location

Hospital de Sagunto

Sagunto, 46520, Spain

Location

Hospital de Sagunto

Valencia, Spain

Location

Hospital la Plana

Villarreal, 12540, Spain

Location

Chernivtsi Regional Children's Clinical Hospital, Department of Pediatrics and Children's Infectious Diseases

Chernivtsi, 58023, Ukraine

Location

Clinical Emergency Hospital" of Dnipro City Council, Department of Pediatric Allergology at the Allergology Center

Dnipro, 49006, Ukraine

Location

Dnipro City Children's Municipal Clinical Hospital #2

Dnipro, Ukraine

Location

City Children's Clinic № 16" of Kharkiv City Council

Kharkiv, 61000, Ukraine

Location

City Children's Clinical Hospital # 19" of Kharkiv City Council

Kharkiv, 61000, Ukraine

Location

Kryvyi Rih City Clinical Hospital #8'' of Kryvyi Rih City Council, Department of Pediatric Pulmonology; State Institution "Dnipropetrovsk Medical Academy of the Ministry of Health of Ukraine

Kryvyi Rih, 50082, Ukraine

Location

O.S. Kolomiychenko Institute, Center of Allergic Diseases of Upper Respiratory Ways and Ear

Kyiv, 03057, Ukraine

Location

State Institution Phthisiology and Pulmonology Institute named after F.G. Yanovskyy of NAMS of Ukraine

Kyiv, 03680, Ukraine

Location

Institute of Pediatrics, Obstetrics and Gynecology named after Academician O. M. Lukianova of the National Academy of Medical Sciences of Ukraine

Kyiv, 04050, Ukraine

Location

Communal Nonprofit Enterprise "Lviv City Children's Clinical Hospital", Allergology Department, Lviv City Children's Allergology Center

Lviv, 79000, Ukraine

Location

Children's Clinical Hospital of Poltava Regional Council

Poltava, 36011, Ukraine

Location

Regional Children Clinical Hospital, Infectious-Diagnostic Department

Sumy, 40031, Ukraine

Location

Regional Children's Clinical Hospital of Vinnytsia Regional Council

Vinnytsia, 21029, Ukraine

Location

City Children's Hospital #5" of Zaporizhzhya City Council, Allergology Department

Zaporizhzhya, 69076, Ukraine

Location

Related Publications (2)

  • Schuster A, Caimmi D, Nolte H, Novakova S, Mikler J, Foss-Skiftesvik MH, Osterdal AS, Emeryk A, Gagnon R, Pfaar O. Efficacy and safety of SQ house dust mite sublingual immunotherapy-tablet (12 SQ-HDM) in children with allergic rhinitis/rhinoconjunctivitis with or without asthma (MT-12): a randomised, double-blind, placebo-controlled, phase III trial. Lancet Reg Health Eur. 2024 Nov 26;48:101136. doi: 10.1016/j.lanepe.2024.101136. eCollection 2025 Jan.

  • Field K, Blaiss MS. Sublingual Versus Subcutaneous Immunotherapy for Allergic Rhinitis: What Are the Important Therapeutic and Real-World Considerations? Curr Allergy Asthma Rep. 2020 Jun 16;20(9):45. doi: 10.1007/s11882-020-00934-4.

MeSH Terms

Conditions

Rhinitis, Allergic

Condition Hierarchy (Ancestors)

RhinitisNose DiseasesRespiratory Tract DiseasesRespiratory HypersensitivityOtorhinolaryngologic DiseasesHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Results Point of Contact

Title
Vice President, Clinical Operations Strategy
Organization
ALK-Abelló A/S

Study Officials

  • Antje Schuster, MD

    Professor of Pediatrics, Düsseldorf University Hospital

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Masking Details
Double-blind
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 11, 2019

First Posted

October 30, 2019

Study Start

October 12, 2019

Primary Completion

April 1, 2023

Study Completion

April 21, 2023

Last Updated

June 12, 2024

Results First Posted

June 12, 2024

Record last verified: 2024-06

Data Sharing

IPD Sharing
Will not share

Locations