NCT04048564

Brief Summary

This is a multicentre ambispective cohort study involving French patients who have started or are receiving for less than 6 months a treatment with ponatinib. This study aims at better qualifying the ponatinib benefit-risk balance in real life and in relation with CML patients' therapeutic history.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
120

participants targeted

Target at P50-P75 for all trials

Timeline
Completed

Started Feb 2018

Longer than P75 for all trials

Geographic Reach
1 country

40 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 23, 2018

Completed
1.4 years until next milestone

First Submitted

Initial submission to the registry

August 6, 2019

Completed
1 day until next milestone

First Posted

Study publicly available on registry

August 7, 2019

Completed
3.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2022

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 3, 2023

Completed
Last Updated

September 28, 2023

Status Verified

September 1, 2023

Enrollment Period

4.9 years

First QC Date

August 6, 2019

Last Update Submit

September 26, 2023

Conditions

Keywords

Chronic myeloid leukemiaIclusigponatinib

Outcome Measures

Primary Outcomes (2)

  • For participants in chronic myeloid leukemia in chronic (CP-CML) phase: Proportion of participants who achieve a major molecular response after the initiation of study treatment

    Chronic myeloid leukemia (CML) response criteria as defined by the European LeukemiaNet Recommendations for Management of Chronic Myeloid Leukemia (Hochhaus et al Leukemia 2020).

    from 24-60 months

  • For participants in chronic myeloid leukemia in accelerated phase (AP-CML) or chronic myeloid leukemia in blast phase (BP-CML): Proportion of participants who achieve a complete hematologic response

    CML response criteria as defined by the European LeukemiaNet Recommendations for Management of Chronic Myeloid Leukemia.

    from 24-60 months

Secondary Outcomes (14)

  • Proportion of participants in CP-CML phase who achieved complete hematologic response

    from 24-60 months

  • Proportion of participants in AP and BP phases who achieved major (complete + partial) cytogenetic response

    from 24-60 months

  • Proportion of participants who achieved major molecular response and/or depth molecular response: (MR4 or MR4.5 or MR5)

    from 24-60 months

  • Duration of response

    from 24-60 months

  • Time to progression to AP-CML or BP-CML (for those participants not in AP-CML or BP-CML)

    from 24-60 months

  • +9 more secondary outcomes

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

70 public and private French investigative centers of hematology will be recruited.

You may qualify if:

  • Presenting a CML in any phase.
  • Having initiated for less than six months a treatment with ponatinib.
  • The ability to understand the requirements of the study and to comply with the study data collection procedures.

You may not qualify if:

  • Patients previously treated with investigational ponatinib (within a clinical trial).
  • Patients receiving an investigational agent.
  • Patients who are pregnant and/or breastfeeding.
  • Patients with contraindications for Ponatinib according to Summary of Products Characteristics.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (40)

CHU SUD Reunion GHSR

Saint-Pierre, Reunion, 97410, France

Location

CHU Amiens-Picardie- Site SUD

Amiens, 80054, France

Location

CHU D'Angers

Angers, 49100, France

Location

CH Annecy

Annecy, 74370, France

Location

Centre Hospitalier Argenteuil

Argenteuil, 95107, France

Location

Centre Hospitalier D'Avignon

Avignon, 84000, France

Location

CH Beziers

Béziers, 34500, France

Location

Institut Bergonie

Bordeaux, 33076, France

Location

Cabinet D'hematologie De La Clinique Du Parc

Castelnau-le-Lez, 34170, France

Location

CH William Morey

Chalon-sur-Saône, 71321, France

Location

CH Chambery

Chambéry, 73000, France

Location

CHU Estaing Clermont Ferrand

Clermont-Ferrand, 63003, France

Location

CHU Dijon, François Mitterrand

Dijon, 21000, France

Location

Centre Hospitalier De Dunkerque

Dunkirk, 59240, France

Location

Centre Hospitalier Departemental Vendee

La Roche-sur-Yon, 85000, France

Location

CH De Versailles (Andre Mignot)

Le Chesnay, 78157, France

Location

Hopital Bicetre

Le Kremlin-Bicêtre, 94270, France

Location

CH De Libourne

Libourne, 33505, France

Location

CHRU De Lille - Hôpital Huriez

Lille, 59037, France

Location

CH Limoges

Limoges, 87042, France

Location

Leon Berard, Lyon

Lyon, 69373, France

Location

Centre Hospitalier De Meaux

Meaux, 77100, France

Location

Hopitaux Prives Metz Centre De Belle-Isle

Metz, 57000, France

Location

CH De Metz (Hopital De Mercy - CHR Metz Thionville)

Metz, 57530, France

Location

CHU Montpellier

Montpellier, 34090, France

Location

Hopital Salpetriere

Paris, 75013, France

Location

La Pitié Salpêtrière - Paris

Paris, 75013, France

Location

Hopital Necker

Paris, 75015, France

Location

CH St Jean

Perpignan, 66000, France

Location

CHU De Poitiers

Poitiers, 86021, France

Location

Hôpital Rene Dubos

Pontoise, 95300, France

Location

CH De Cornouaille

Quimper, 29107, France

Location

CHU De Rennes

Rennes, 35033, France

Location

Hopital Victor Provo

Roubaix, 59056, France

Location

La Clinique Sainte-Anne

Strasbourg, 67000, France

Location

CHRU Strasbourg

Strasbourg, 67200, France

Location

Institut Universitaire Du Cancer Toulouse - Oncopo

Toulouse, 31059, France

Location

CH Troyes

Troyes, 10000, France

Location

CHRU De Nancy - Hôpitaux De Brabois

Vandœuvre-lès-Nancy, 54511, France

Location

CHU Sud, St Pierre - La Réunion

Vandœuvre-lès-Nancy, 54511, France

Location

Related Publications (1)

  • Huguet F, Guerci-Bresler A, Roth-Guepin G, Cayssials E, Slama B, Santagostino A, Penot A, Quittet P, Cony-Makhoul P, Saad A, Bastie JN, Hacini M, Coiteux V, Uzunov M, Roy L, Le Clech L, Berger M, Agneray AM, Messas E, Etienne G, Turhan A, Nicolini FE, Rousselot P. Clinical outcomes in patients in any phase of CML treated with ponatinib in France-Data from the TOPASE observational study. Br J Haematol. 2024 Dec;205(6):2295-2304. doi: 10.1111/bjh.19819. Epub 2024 Nov 6.

MeSH Terms

Conditions

Leukemia, Myelogenous, Chronic, BCR-ABL Positive

Condition Hierarchy (Ancestors)

Leukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasmsMyeloproliferative DisordersBone Marrow DiseasesHematologic DiseasesHemic and Lymphatic DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Study Officials

  • Ali G. Turnan, MD, PhD

    Paris Sud University Hospitals-Bicetre

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 6, 2019

First Posted

August 7, 2019

Study Start

February 23, 2018

Primary Completion

December 31, 2022

Study Completion

July 3, 2023

Last Updated

September 28, 2023

Record last verified: 2023-09

Data Sharing

IPD Sharing
Will not share

Locations