NCT04036292

Brief Summary

The objective of this study is to evaluate the safety and effectiveness of OC-01 Nasal Spray as compared to placebo on signs and symptoms of dry eye disease.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
758

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jul 2019

Geographic Reach
1 country

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 23, 2019

Completed
2 days until next milestone

First Submitted

Initial submission to the registry

July 25, 2019

Completed
4 days until next milestone

First Posted

Study publicly available on registry

July 29, 2019

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 10, 2020

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

February 5, 2021

Completed
10 months until next milestone

Results Posted

Study results publicly available

November 22, 2021

Completed
Last Updated

November 22, 2021

Status Verified

August 1, 2021

Enrollment Period

9 months

First QC Date

July 25, 2019

Results QC Date

August 23, 2021

Last Update Submit

October 22, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percent of Subjects Who Achieve ≥10 mm Improvement in Schirmer's Test Score From Baseline at Visit 4 (Day 28)

    The primary endpoint was the percentage of subjects who achieve ≥10 mm improvement in Schirmer's Test Score from baseline to 28 days in the study eye following treatment with OC-01. Schirmer's test scores from 0-35 mm where a higher score is indicative of a better outcome.

    28 Days [Visit 1 (baseline) and Visit 4b (28 days)]

Secondary Outcomes (5)

  • Mean Change From Baseline in Eye Dryness Score in CAE at Week 4 at 5 Minutes

    28 Days [Visit 1 (baseline) and Visit 4a (28 days)]

  • Mean Change From Baseline in Eye Dryness Score From Baseline to Day 28

    28 Days [Visit 1 (baseline) and Visit 4b (28 days)]

  • Mean Change Form Baseline in Schirmer's Test Score From Baseline to Day 28

    28 Days [Visit 1 (baseline) and Visit 4b (28 days)]

  • Mean Change From Baseline in Eye Dryness Score in the Study Eye at Week 2

    14 Days [Visit 1 (baseline) and Visit 3 (14 days)]

  • Mean Change From Baseline in Eye Dryness Score in the Study Eye at Week 1

    7 Days [Visit 1 (baseline) and Visit 2 (7 days)]

Study Arms (3)

OC-01 Low Dose, 0.6 mg/mL

ACTIVE COMPARATOR

OC-01 (varenicline) nasal spray, 0.6 mg/ML

Drug: OC-01 (varenicline) nasal spray

OC-01 High Dose, 1.2 mg/mL

ACTIVE COMPARATOR

OC-01 (varenicline) nasal spray, 1.2 mg/ML

Drug: OC-01 (varenicline) nasal spray

Placebo (vehicle) nasal spray

PLACEBO COMPARATOR

Placebo (vehicle) nasal spray

Drug: Placebo (vehicle) nasal spray

Interventions

OC-01 (varenicline) nasal spray

OC-01 High Dose, 1.2 mg/mLOC-01 Low Dose, 0.6 mg/mL

Placebo (vehicle) nasal spray

Placebo (vehicle) nasal spray

Eligibility Criteria

Age22 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • \- Have used and/or desired to use an artificial tear substitute for dry eye symptoms within 6 months prior to Visit 1

You may not qualify if:

  • Have had any intraocular surgery (such as cataract surgery) or extraocular surgery in either eye within three months or refractive surgery (e.g. laser-assisted in-situ keratomileusis, laser epithelial keratomileusis, photorefractive keratectomy or corneal implant) within twelve months of Visit 1.
  • Have a history or presence of any ocular disorder or condition in either eye that would, in the opinion of the Investigator, likely interfere with the interpretation of the study results or participant safety such as significant corneal or conjunctival scarring; pterygium or nodular pinguecula; current ocular infection, conjunctivitis, or inflammation not associated with dry eye; anterior (epithelial) basement membrane corneal dystrophy or other clinically significant corneal dystrophy or degeneration; ocular herpetic infection; evidence of keratoconus; etc. Blepharitis not requiring treatment and mild meibomian gland disease that are typically associated with dry eye disease are allowed.
  • Have a systemic condition or disease not stabilized or judged by the Investigator to be incompatible with participation in the study or with the lengthier assessments required by the study (e.g., current systemic infection, uncontrolled autoimmune disease, uncontrolled immunodeficiency disease, history of myocardial infarction or heart disease, etc.)
  • Have a known hypersensitivity to any of the procedural agents or study drug components
  • Have any condition or history that, in the opinion of the investigator, may interfere with study compliance, outcome measures, safety parameters, and/or the general medical condition of the subject.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Phoenix

Phoenix, Arizona, 85032, United States

Location

New Port Beach

Newport Beach, California, 92663, United States

Location

Fort Collins

Fort Collins, Colorado, 80528, United States

Location

Waterbury

Waterbury, Connecticut, 06708, United States

Location

Delray Beach

Delray Beach, Florida, 33484, United States

Location

Indianapolis

Indianapolis, Indiana, 46290, United States

Location

Louisville

Louisville, Kentucky, 40206, United States

Location

Raynham

Raynham, Massachusetts, 02767, United States

Location

Las Vegas

Las Vegas, Nevada, 89052, United States

Location

Raleigh

Raleigh, North Carolina, 27603, United States

Location

Shelby

Shelby, North Carolina, 28150, United States

Location

Fargo

Fargo, North Dakota, 58103, United States

Location

Cranberry Township

Cranberry Township, Pennsylvania, 16066, United States

Location

Warwick

Warwick, Rhode Island, 02842, United States

Location

Sioux Falls

Sioux Falls, South Dakota, 57108, United States

Location

Nashville

Nashville, Tennessee, 37210, United States

Location

Austin

Austin, Texas, 78731, United States

Location

Houston

Houston, Texas, 77025, United States

Location

San Antonio

San Antonio, Texas, 78209, United States

Location

San Antonio

San Antonio, Texas, 78229, United States

Location

Layton

Layton, Utah, 84041, United States

Location

Lynchburg

Lynchburg, Virginia, 24502, United States

Location

Related Publications (3)

  • Hauswirth SG, Kabat AG, Hemphill M, Somaiya K, Hendrix LH, Gibson AA. Safety, adherence and discontinuation in varenicline solution nasal spray clinical trials for dry eye disease. J Comp Eff Res. 2023 Jun;12(6):e220215. doi: 10.57264/cer-2022-0215. Epub 2023 Apr 25.

  • Nijm LM, Zhu D, Hemphill M, Blemker GL, Hendrix LH, Kabat AG, Gibson AA. Does Menopausal Status Affect Dry Eye Disease Treatment Outcomes with OC-01 (Varenicline Solution) Nasal Spray? A Post Hoc Analysis of ONSET-1 and ONSET-2 Clinical Trials. Ophthalmol Ther. 2023 Feb;12(1):355-364. doi: 10.1007/s40123-022-00607-7. Epub 2022 Nov 18.

  • Wirta D, Vollmer P, Paauw J, Chiu KH, Henry E, Striffler K, Nau J; ONSET-2 Study Group. Efficacy and Safety of OC-01 (Varenicline Solution) Nasal Spray on Signs and Symptoms of Dry Eye Disease: The ONSET-2 Phase 3 Randomized Trial. Ophthalmology. 2022 Apr;129(4):379-387. doi: 10.1016/j.ophtha.2021.11.004. Epub 2021 Nov 10.

MeSH Terms

Conditions

Dry Eye Syndromes

Interventions

VareniclineNasal Sprays

Condition Hierarchy (Ancestors)

Lacrimal Apparatus DiseasesEye Diseases

Intervention Hierarchy (Ancestors)

BenzazepinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsQuinoxalinesAerosolsColloidsComplex MixturesDosage FormsPharmaceutical Preparations

Results Point of Contact

Title
Jeffrey Nau
Organization
Oyster Point Pharma, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 25, 2019

First Posted

July 29, 2019

Study Start

July 23, 2019

Primary Completion

April 10, 2020

Study Completion

February 5, 2021

Last Updated

November 22, 2021

Results First Posted

November 22, 2021

Record last verified: 2021-08

Data Sharing

IPD Sharing
Will not share

Locations