NCT04006223

Brief Summary

Systemic amyloidosis is a multi-system disease caused by extracellular deposition of insoluble amyloid fibrils in various tissues and organs, leading to progressive organ dysfunction. The clinical manifestations of different types of amyloidosis are complex and diverse, and the prognosis is very poor. Early detection and classification of amyloid deposition is becoming increasingly important. However, conventional imaging techniques including ultrasound and magnetic resonance are not sensitive or specific. Endocardial biopsy is the gold standard for the diagnosis of cardiac amyloidosis, but it is an invasive procedure with a clinical complication rate of 6%. Positron emission tomography (PET) provides a valuable tool for diagnosing systemic amyloidosis. Recently, amyloid PET imaging agents (11C-PIB or 18F-florbetapir) have been shown to be effective as novel positron tracers to detect potential amyloid deposition in some small sample studies. The investigators will use the most advanced imaging equipment, integrated PET/MR with amyloid PET imaging agents(11C-PIB or 18F-florbetapir) to image patients suspected or confirmed systemic amyloidosis, the aim is to explore the value of hybrid PET/MR for systemic amyloidosis.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
30

participants targeted

Target at below P25 for all trials

Timeline
Completed

Started Mar 2019

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 11, 2019

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

June 30, 2019

Completed
5 days until next milestone

First Posted

Study publicly available on registry

July 5, 2019

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2023

Completed
Last Updated

February 14, 2023

Status Verified

February 1, 2023

Enrollment Period

4.8 years

First QC Date

June 30, 2019

Last Update Submit

February 13, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Sensitivity and specificity per patient analysis

    For patient without any treatment, detection and initial diagnosis, results of 11C-PiB or 18F-florbetapir PET/MR will be compared to histopathological, clinical, laboratory, radiological evidence and follow-up result.

    up to 2 years

Secondary Outcomes (3)

  • Sensitivity and specificity per organ analysis

    up to 2 years

  • Change after treatment

    up to 2 years

  • Correlation with severity

    up to 2 years

Study Arms (1)

11C-PIB or 18F-florbetapir PET/MR

Patients suspected of or diagnosed with systemic amyloidosis will be scanned by 11C-PIB or 18F-florbetapir PET/MR twice. One is before biopsy and treatment, and the other is after at least half a year of treatment.

Diagnostic Test: 11C-PIB or 18F-florbetapir PET/MR before biopsy and treatmentDiagnostic Test: 11C-PIB or 18F-florbetapir PET/MR after treatment

Interventions

10-20 mCi 11C-PIB or 5-10 mCi 18F-florbetapir will be injected intravenously prior to imaging.

11C-PIB or 18F-florbetapir PET/MR

10-20 mCi 11C-PIB or 5-10 mCi 18F-florbetapir will be injected intravenously prior to imaging.

11C-PIB or 18F-florbetapir PET/MR

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Central China

You may qualify if:

  • Patient with Monoclonal Ganunopathy, adds one of the following criteria:
  • Histologically confirmed Amyloidosis of any organ.
  • Average left ventricular thickness of the echocardiogram is more than 11 mm without uncontrolled high blood pressure.
  • lead ECG shows unexplained low voltage \<0.5 mV.

You may not qualify if:

  • Patient can not lie flat
  • NYHA Level 4 Heart Failure
  • Patient is pregnant or nursing
  • Patient is allergic to amyloid PET imaging agents
  • Patient with acute systemic diseases and electrolyte disorders
  • Patient with severe claustrophobia or unstable vital sigh
  • Other serious comorbidities evaluated by primary investigator

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

China, Hubei Province

Wuhan, Hubei, 430022, China

RECRUITING

MeSH Terms

Conditions

Immunoglobulin Light-chain Amyloidosis

Condition Hierarchy (Ancestors)

Neoplasms, Plasma CellNeoplasms by Histologic TypeNeoplasmsAmyloidosisProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic DiseasesLymphoproliferative DisordersImmunoproliferative DisordersImmune System DiseasesParaproteinemias

Study Officials

  • Xiaoli Lan, MD, PhD

    Union Hospital, Tongji Medical College, Huazhong University of Science and Technology

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Xiaoli Lan, MD, PhD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Director of the Department of nuclear medicine

Study Record Dates

First Submitted

June 30, 2019

First Posted

July 5, 2019

Study Start

March 11, 2019

Primary Completion

December 31, 2023

Study Completion

December 31, 2023

Last Updated

February 14, 2023

Record last verified: 2023-02

Locations