NCT03996486

Brief Summary

The purpose of this study is to investigate the safety of a test drug to treat hemophilia in adult men.

Trial Health

15
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Oct 2019

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 21, 2019

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 24, 2019

Completed
4 months until next milestone

Study Start

First participant enrolled

October 28, 2019

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 29, 2020

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 31, 2020

Completed
Last Updated

October 22, 2019

Status Verified

October 1, 2019

Enrollment Period

7 months

First QC Date

June 21, 2019

Last Update Submit

October 21, 2019

Conditions

Keywords

Coagulation Factor VIII (FVIII)Coagulation Factor IX (FIX)Anti-tissue factor pathway inhibitor (aTFPI)Human monoclonal immunoglobulin G2 antibody

Outcome Measures

Primary Outcomes (3)

  • Frequency of drug-related adverse events

    Up to 3 months

  • Frequency of drug-related serious adverse events

    Up to 3 months

  • Frequency of adverse events of special interest

    Adverse events of special interest comprise thromboembolic and thrombotic microangiopathy events, and hypersensitivity reactions.

    Up to 3 months

Study Arms (1)

Hemophilia

EXPERIMENTAL

Dose escalation starting with 200 mg of BAY1093884

Drug: BAY1093884

Interventions

Drug administered via subcutaneous injections once weekly for 6 weeks (= 6 doses)

Also known as: Human monoclonal immunoglobulin G2 antibody blocking the endogenous tissue factor pathway inhibitor (TFPI)
Hemophilia

Eligibility Criteria

Age18 Years - 65 Years
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants with hemophilia A and FVIII activity \<1% or hemophilia B with FIX activity \<2%
  • Participants must be currently without inhibitors or with low titer inhibitors (inhibitor titer \< 5 Bethesda units) who are receiving current on demand treatment with any FVIII or FIX (recombinant or plasma-derived; modified or unmodified)

You may not qualify if:

  • History or at risk of developing diseases related to venous thromboembolic events (e.g., pulmonary embolism, deep vein thrombosis or thrombophlebitis)
  • History of any other clinically relevant coagulation disorder (particularly disseminated intravascular coagulopathy or combined FVIII/Factor V deficiency) or platelet disorder
  • History or at risk of developing cardiac, coronary and/or arterial peripheral atherosclerotic disease and/or arterial thromboembolic events, particularly myocardial infarction, cerebrovascular accident, stroke, transient ischemic attack, congestive heart failure, angina pectoris, treatment for angina pectoris or uncontrolled hypertension
  • History or at risk for thrombotic microangiopathy

Contact the study team to confirm eligibility.

Sponsors & Collaborators

MeSH Terms

Conditions

Hemophilia AHemophilia B

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesGenetic Diseases, X-Linked
0

Study Design

Study Type
interventional
Phase
phase 1
Masking
NONE
Purpose
OTHER
Intervention Model
SEQUENTIAL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 21, 2019

First Posted

June 24, 2019

Study Start

October 28, 2019

Primary Completion

May 29, 2020

Study Completion

July 31, 2020

Last Updated

October 22, 2019

Record last verified: 2019-10