NCT03951077

Brief Summary

This study will assess the potential impact of elagolix on disordered pituitary and ovarian hormones in women with polycystic ovary syndrome (PCOS).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
118

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Aug 2019

Shorter than P25 for phase_2

Geographic Reach
2 countries

54 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 6, 2019

Completed
9 days until next milestone

First Posted

Study publicly available on registry

May 15, 2019

Completed
3 months until next milestone

Study Start

First participant enrolled

August 12, 2019

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 10, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 10, 2021

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

June 8, 2022

Completed
Last Updated

June 8, 2022

Status Verified

May 1, 2022

Enrollment Period

1.5 years

First QC Date

May 6, 2019

Results QC Date

May 16, 2022

Last Update Submit

May 16, 2022

Conditions

Keywords

Polycystic Ovary SyndromeHormoneElagolix

Outcome Measures

Primary Outcomes (1)

  • Percentage of Menstrual Cycle Responders

    A participant was considered a menstrual cycle responder if she has at least 2 normal menstrual cycles during the final 4 months of the treatment period. In addition, a participant was considered a complete menstrual cycle responder if she has normal menstrual cycles beginning at or before Month 3 that are maintained through Month 6 during the treatment period.

    Week 0 (Baseline) to Week 24 (Month 6)

Secondary Outcomes (1)

  • Change From Baseline in Area Under the Luteinizing Hormone (LH) Serum Concentration-time Curve (AUC) at Week 1

    Week 0 (Baseline), Week 1: before the morning dose (0 hour) and at 0.5 (± 5 minutes), 1 (± 5 minutes), 1.5 (± 5 minutes), 2 (± 15 minutes), 2.5 (± 15 minutes), 3 (± 15 minutes), 3.5 (± 15 minutes), and 4 (± 15 minutes) hours after dosing.

Study Arms (6)

Placebo

PLACEBO COMPARATOR

Placebo taken orally twice a day (BID)

Drug: Placebo

Elagolix 25 mg BID

EXPERIMENTAL

Elagolix 25 mg taken orally BID plus placebo

Drug: ElagolixDrug: Placebo

Elagolix 50 mg Once Daily (QD)

EXPERIMENTAL

Elagolix 50 mg taken orally QD plus placebo

Drug: ElagolixDrug: Placebo

Elagolix 75 mg BID

EXPERIMENTAL

Elagolix 75 mg taken orally BID plus placebo

Drug: ElagolixDrug: Placebo

Elagolix 150 mg QD

EXPERIMENTAL

Elagolix 150 mg taken orally QD plus placebo

Drug: ElagolixDrug: Placebo

Elagolix 300 mg QD

EXPERIMENTAL

Elagolix 300 mg taken orally QD plus placebo

Drug: ElagolixDrug: Placebo

Interventions

Capsule administered orally

Also known as: Orilissa
Elagolix 150 mg QDElagolix 25 mg BIDElagolix 300 mg QDElagolix 50 mg Once Daily (QD)Elagolix 75 mg BID

Capsule administered orally

Elagolix 150 mg QDElagolix 25 mg BIDElagolix 300 mg QDElagolix 50 mg Once Daily (QD)Elagolix 75 mg BIDPlacebo

Eligibility Criteria

Age18 Years - 35 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Participants with clinical diagnosis of PCOS.
  • Participants with a body mass index (BMI) of 18.5 to 38 kg/m\^2 at time of Screening.

You may not qualify if:

  • Participants with newly diagnosed medical condition requiring intervention that has not been stabilized at least 30 days prior to Baseline.
  • Participants with a significant medical condition that require intervention during the course of study participation (such as anticipated major elective surgery).
  • Participants with an unstable medical condition (including, but not limited to, uncontrolled hypertension, epilepsy requiring anti-epileptic medicine, unstable angina, confirmed inflammatory bowel disease, hyperprolactinemia, clinically significant infection or injury).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (54)

Alabama Clinical Therapeutics /ID# 211498

Birmingham, Alabama, 35235-3430, United States

Location

Mobile, OBGYN P.C. /ID# 205574

Mobile, Alabama, 36608, United States

Location

Medical Ctr for Clin Research /ID# 205694

San Diego, California, 92108, United States

Location

UCSF Center for Reproductive Health /ID# 210836

San Francisco, California, 94158-2518, United States

Location

Avail Clinical Research /ID# 210873

DeLand, Florida, 32720-0834, United States

Location

University of FL Southside Women's Specialists /ID# 210872

Jacksonville, Florida, 32207-4918, United States

Location

Segal Institute for Clinical Research /ID# 205490

North Miami, Florida, 33161-5821, United States

Location

A Premier Medical Research of FL /ID# 215659

Orange City, Florida, 32763-2833, United States

Location

Virtus Research Consultant,LLC /ID# 205475

Wellington, Florida, 33414, United States

Location

Comprehensive Clinical Trials LLC /ID# 205458

West Palm Beach, Florida, 33409, United States

Location

Mount Vernon Clinical Res, LLC /ID# 205695

Atlanta, Georgia, 30328, United States

Location

Bingham Memorial Hospital /ID# 205606

Blackfoot, Idaho, 83221, United States

Location

Leavitt Womens Healthcare /ID# 205571

Idaho Falls, Idaho, 83404-8322, United States

Location

Womens Healthcare Assoc, DBA /ID# 211528

Idaho Falls, Idaho, 83404, United States

Location

Sonora Clinical Research /ID# 205623

Meridian, Idaho, 83646-1144, United States

Location

Asr, Llc /Id# 207037

Nampa, Idaho, 83687, United States

Location

PRN Professional Research Network of Kansas, LLC /ID# 205875

Wichita, Kansas, 67205, United States

Location

Clinical Trials Management, LLC - Covington /ID# 211219

Covington, Louisiana, 70433, United States

Location

Clinical Trials Management, LLC - Metairie /ID# 205494

Metairie, Louisiana, 70006-4165, United States

Location

Baltimore Suburban Health /ID# 205619

Baltimore, Maryland, 21208, United States

Location

Johns Hopkins University /ID# 205617

Baltimore, Maryland, 21287, United States

Location

Capital Women's Care - Frederi /ID# 210276

Frederick, Maryland, 21702, United States

Location

NECCR Fall River LLC /ID# 205567

Fall River, Massachusetts, 02720-2972, United States

Location

Wayne State University Physician Group - Southfield /ID# 210245

Southfield, Michigan, 48034, United States

Location

Private practice: Dr. Rex G. Mabey JR /ID# 211149

Las Vegas, Nevada, 89128, United States

Location

Dr. Nader and Associates M.D. P.C. /ID# 211150

North Las Vegas, Nevada, 89030-7187, United States

Location

Cooper University Hospital/Sheridan Pavilion /ID# 205576

Marlton, New Jersey, 08053-3464, United States

Location

University of New Mexico /ID# 212594

Albuquerque, New Mexico, 87102-4517, United States

Location

SUNY Downstate Medical Center /ID# 211180

Brooklyn, New York, 11203, United States

Location

University of Rochester - Strong Fertility Center - Rochester /ID# 210328

Rochester, New York, 14623-4284, United States

Location

OB.GYN Associates of WNY /ID# 210765

West Seneca, New York, 14224, United States

Location

Upstate Clinical Research Associates /ID# 205717

Williamsville, New York, 14221-6046, United States

Location

Carolina Institute for Clinical Research - Fayetteville /ID# 211319

Fayetteville, North Carolina, 28303, United States

Location

Wake Forest Baptist Medical Center /ID# 211473

Winston-Salem, North Carolina, 27157-0001, United States

Location

Duplicate_Aventiv Research, Inc. /ID# 205460

Columbus, Ohio, 43213, United States

Location

Univ Hosp Landerbrook /ID# 205558

Mayfield Heights, Ohio, 44124, United States

Location

AC Clinical Research /ID# 205492

Tiffin, Ohio, 44883, United States

Location

Penn State University and Milton S. Hershey Medical Center /ID# 205555

Hershey, Pennsylvania, 17033-2360, United States

Location

Thomas Jefferson University /ID# 205614

Philadelphia, Pennsylvania, 19107, United States

Location

Reading Hospital /ID# 211322

Reading, Pennsylvania, 19611, United States

Location

Chattanooga Medical Research /ID# 215190

Chattanooga, Tennessee, 37404, United States

Location

WR-Medical Research Center of Memphis LLC /ID# 205636

Memphis, Tennessee, 38120-8328, United States

Location

The University of Texas Southwestern Medical Center /ID# 210804

Dallas, Texas, 75390-8575, United States

Location

University of Texas (UT) Health Women's Research Center at Memorial City /ID# 216266

Houston, Texas, 77024-2515, United States

Location

Advances in Health, Inc. /ID# 211249

Houston, Texas, 77030, United States

Location

Duplicate_Diagnostic Clinic of Longview /ID# 211019

Longview, Texas, 75605, United States

Location

Center of Reproductive Medicine /ID# 211250

Webster, Texas, 77598, United States

Location

Virginia Mason - Seattle Orthapedics /ID# 205586

Seattle, Washington, 98101, United States

Location

Seattle Women's Health, Research, Gynecology /ID# 205569

Seattle, Washington, 98105, United States

Location

North Spokane Women's Health /ID# 205585

Spokane, Washington, 99207, United States

Location

Puerto Rico Medical Research /ID# 211104

Ponce, 00717, Puerto Rico

Location

University of Puerto Rico, Medical Sciences Campus /ID# 212320

Rio Piedras, 00935, Puerto Rico

Location

Duplicate_Rodriguez-Ginorio, San Juan /ID# 211105

San Juan, 00917, Puerto Rico

Location

Mindful Medical Research /ID# 212323

San Juan, 00918-3756, Puerto Rico

Location

Related Publications (1)

  • Snabes MC, Ng J, Li H, Ali I, Shebley M, Schlaff WD. Phase 2, double-blind, randomized, placebo-controlled study of the safety and efficacy of elagolix in women with polycystic ovary syndrome. F S Rep. 2023 Feb 21;4(2):206-212. doi: 10.1016/j.xfre.2023.02.007. eCollection 2023 Jun.

Related Links

MeSH Terms

Conditions

Polycystic Ovary Syndrome

Interventions

elagolix

Condition Hierarchy (Ancestors)

Ovarian CystsCystsNeoplasmsOvarian DiseasesAdnexal DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesGonadal DisordersEndocrine System Diseases

Results Point of Contact

Title
Global Medical Services
Organization
AbbVie

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 6, 2019

First Posted

May 15, 2019

Study Start

August 12, 2019

Primary Completion

February 10, 2021

Study Completion

February 10, 2021

Last Updated

June 8, 2022

Results First Posted

June 8, 2022

Record last verified: 2022-05

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible data sharing regarding the clinical trials we sponsor. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information (e.g., protocols and clinical study reports), as long as the trials are not part of an ongoing or planned regulatory submission. This includes requests for clinical trial data for unlicensed products and indications.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
For details on when studies are available for sharing, please refer to the link below.
Access Criteria
Access to this clinical trial data can be requested by any qualified researchers who engage in rigorous, independent scientific research, and will be provided following review and approval of a research proposal and Statistical Analysis Plan (SAP) and execution of a Data Use Agreement (DUA). For more information on the process, or to submit a request, visit the following link.
More information

Locations