NCT03931785

Brief Summary

To evaluate the safety and tolerability, treatment effect on abdominal pain, and dose response of MD-7246 administered orally to patients with diarrhea-predominant irritable bowel syndrome (IBS-D).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
515

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2019

Shorter than P25 for phase_2

Geographic Reach
1 country

80 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 22, 2019

Completed
8 days until next milestone

First Posted

Study publicly available on registry

April 30, 2019

Completed
1 day until next milestone

Study Start

First participant enrolled

May 1, 2019

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 26, 2020

Completed
14 days until next milestone

Study Completion

Last participant's last visit for all outcomes

March 11, 2020

Completed
1 year until next milestone

Results Posted

Study results publicly available

March 12, 2021

Completed
Last Updated

March 12, 2021

Status Verified

February 1, 2021

Enrollment Period

10 months

First QC Date

April 22, 2019

Results QC Date

February 19, 2021

Last Update Submit

February 19, 2021

Conditions

Keywords

Abdominal painDiarrheaIrritable Bowel Syndrome

Outcome Measures

Primary Outcomes (2)

  • Change From Baseline in Abdominal Pain at Its Worst on a NRS Through the Treatment Period

    Abdominal pain is measured daily in an eDiary, using an 11-point NRS, where 0 is anchored with "no abdominal pain" and 10 is anchored with "worst possible abdominal pain." The postbaseline weekly abdominal pain score is the average of the non-missing daily abdominal pain at its worst scores during a week (Weeks 1-12) if there are at least 4 daily scores entered into the eDiary during the week. Weekly change from baseline was calculated for each week as the weekly score minus the baseline score. Mixed model repeated measures (MMRM) results are based on a repeated measures analysis with treatment, analysis week, and treatment-by-week interaction as fixed effects and baseline as covariate. An unstructured covariance structure was used to model intra-subject correlation with subjects as a random effect. Baseline is derived from the eDiary data collected daily in the Pretreatment Period, specifically the period of time from 14 days before randomization up to the time of randomization.

    Baseline, up to Week 12 (end of the Treatment Period)

  • Percentage of Participants Who Were 6/12 Week Abdominal Pain 30% Change Responders

    A 6/12 Week Abdominal Pain 30% Responder was a participant who had a decrease from baseline of ≥30% in the weekly abdominal pain score for that week for at least 6 out of the 12 weeks of the Treatment Period; for any week, a participant with \< 4 daily abdominal pain scores available was considered a non-responder for that week. Abdominal pain is measured daily in an eDiary, using an 11-point NRS, where 0 is anchored with "no abdominal pain" and 10 is anchored with "worst possible abdominal pain." The postbaseline weekly abdominal pain score is the average of the non-missing daily abdominal pain at its worst scores during a week (Weeks 1-12) if there are at least 4 daily scores entered into the eDiary during the week.

    Baseline through Week 12

Study Arms (4)

MD-7246 300 μg

EXPERIMENTAL

1 MD-7246 300-μg oral tablet and 3 matching placebo oral tablets

Drug: MD-7246Drug: Placebo

MD-7246 600 μg

EXPERIMENTAL

2 MD-7246 300-μg oral tablets and 2 matching placebo oral tablets

Drug: MD-7246Drug: Placebo

MD-7246 1200 μg

EXPERIMENTAL

4 MD-7246 300-μg oral tablets

Drug: MD-7246

Placebo

PLACEBO COMPARATOR

4 matching placebo oral tablets

Drug: Placebo

Interventions

Oral tablet

MD-7246 1200 μgMD-7246 300 μgMD-7246 600 μg

Matching oral tablet

MD-7246 300 μgMD-7246 600 μgPlacebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient meets the Rome IV criteria for diagnosis of IBS-D
  • Patient maintains a minimum level of compliance with daily diary
  • Female patients of childbearing potential must agree to use one of the following methods of birth control:
  • Hormonal contraception
  • Double-barrier method
  • Maintenance of a monogamous relationship with a male partner who has been surgically sterilized by vasectomy

You may not qualify if:

  • Patient has clinically significant findings on a physical examination and/or clinical laboratory tests
  • Patient has symptoms of or been diagnosed with a medical condition that may contribute to abdominal pain
  • Patient has a structural abnormality of the gastrointestinal (GI) tract or a disease or condition that can affect GI motility
  • Patient has any protocol-excluded or clinically significant medical or surgical history that could confound the study assessments

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (80)

Clinical Research Associates

Huntsville, Alabama, 35801, United States

Location

Elite Clinical Studies

Phoenix, Arizona, 85018, United States

Location

Arkansas Gastroenterology

North Little Rock, Arkansas, 72117, United States

Location

GW Research, Inc.

Chula Vista, California, 91910, United States

Location

Kindred Medical Institute for Clinical Trials, LLC

Corona, California, 92879, United States

Location

Diagnamics Inc.

Encinitas, California, 92024, United States

Location

St. Joseph Heritage Healthcare

Fullerton, California, 92835, United States

Location

Paragon Rx Clinical

Garden Grove, California, 92840, United States

Location

Grossmont Center For Clinical Research

La Mesa, California, 91942, United States

Location

Facey Medical Foundation

Mission Hills, California, 91345, United States

Location

Providence Clinical Research

North Hollywood, California, 91606, United States

Location

Precision Research Institute

San Diego, California, 92114, United States

Location

Paragon Rx Clinical, Inc. - Santa Ana

Santa Ana, California, 92703, United States

Location

UNISON Clinical Trials

Sherman Oaks, California, 91403, United States

Location

Millennium Clinical Trials

Thousand Oaks, California, 91360, United States

Location

Advanced Rx Clinical Research

Westminster, California, 92683, United States

Location

Peak Gastroenterology Associates

Colorado Springs, Colorado, 80907, United States

Location

Connecticut Clinical Research Institute

Bristol, Connecticut, 06010, United States

Location

Chase Medical Research of Greater New Haven LLC

Hamden, Connecticut, 06517, United States

Location

The Chappel Group Research, LLC

Kissimmee, Florida, 34744, United States

Location

Well Pharma Medical Research Corporation

Miami, Florida, 33143, United States

Location

New Horizon Research Center

Miami, Florida, 33175, United States

Location

San Marcus Research Clinic Inc

Miami Lakes, Florida, 33014, United States

Location

Ormond Medical Arts Pharmaceutical Research Center

Ormond Beach, Florida, 32174, United States

Location

Meridien Research

St. Petersburg, Florida, 33709, United States

Location

Palm Beach Research Center

West Palm Beach, Florida, 33409, United States

Location

Research Institute of Central Florida, LLC

Winter Park, Florida, 32792, United States

Location

Mount Vernon Clinical Research, LLC

Sandy Springs, Georgia, 30328, United States

Location

Rockford Gastroenterology Associates LTD

Rockford, Illinois, 61107, United States

Location

Clinical Trials Management LLC

Metairie, Louisiana, 70006, United States

Location

Clinical Trials of America -- LA LLC

West Monroe, Louisiana, 71291, United States

Location

Meritus Center For Clinical Research

Hagerstown, Maryland, 21742, United States

Location

Meridian Clinical Research

Rockville, Maryland, 20854, United States

Location

Boston Clinical Trials Inc

Boston, Massachusetts, 02131, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

New England Center For Clinical Research Inc PrimaCare Research, LLC

Fall River, Massachusetts, 02721, United States

Location

MedVadis Research Corporation

Watertown, Massachusetts, 02472, United States

Location

Galen Research

Chesterfield, Missouri, 63005, United States

Location

Bozeman Health Deaconess Hospital

Bozeman, Montana, 59718, United States

Location

Barrett Clinic, P.C. - BTC - PPDS

La Vista, Nebraska, 68128, United States

Location

Meridian Clinical Research

Omaha, Nebraska, 68134, United States

Location

Clinical Research of South Nevada

Las Vegas, Nevada, 89121, United States

Location

Advanced Biomedical Research of America

Las Vegas, Nevada, 89123, United States

Location

Healthwise Medical Associates

Brooklyn, New York, 11206, United States

Location

Long Island Gastrointestinal Research Group LLP

Great Neck, New York, 11023, United States

Location

Rochester Clinical Research, Inc

Rochester, New York, 14609, United States

Location

Carolina Digestive Health Associates

Charlotte, North Carolina, 28210, United States

Location

Carolina Digestive Health Associates

Concord, North Carolina, 28025, United States

Location

Peters Medical Research, LLC

High Point, North Carolina, 27262, United States

Location

Clinical Trials of America-NC, LLC

Mount Airy, North Carolina, 27030, United States

Location

M3 Wake Research, Inc

Raleigh, North Carolina, 43212, United States

Location

PMG Research of Wilmington

Wilmington, North Carolina, 28401, United States

Location

Lyndhurst Clinical Research

Winston-Salem, North Carolina, 27103, United States

Location

PMG Research of Winston-Salem

Winston-Salem, North Carolina, 27103, United States

Location

Progressive Medicine of the Triad, LLC

Winston-Salem, North Carolina, 27103, United States

Location

Lillestol Research

Fargo, North Dakota, 58104, United States

Location

Hometown Urgent Care and Research

Cincinnati, Ohio, 45215, United States

Location

Hightop Medical Research Center

Cincinnati, Ohio, 45224, United States

Location

New Horizons Clinical Research

Cincinnati, Ohio, 45242, United States

Location

Hometown Urgent Care and Research

Columbus, Ohio, 42314, United States

Location

Remington Davis Inc

Columbus, Ohio, 43215, United States

Location

Hometown Urgent Care and Research

Dayton, Ohio, 45424, United States

Location

Central Sooner Research

Norman, Oklahoma, 73071, United States

Location

IPS Research Company

Oklahoma City, Oklahoma, 73106, United States

Location

Digestive Disease Specialists, Inc.

Oklahoma City, Oklahoma, 73112, United States

Location

Oregon Center For Clinical Investigations Inc

Salem, Oregon, 97301, United States

Location

Partners In Clinical Research

Cumberland, Rhode Island, 02864, United States

Location

Ocean State Clinical Research Partners

Lincoln, Rhode Island, 02865, United States

Location

Mountain View Clinical Research Inc

Greer, South Carolina, 29651, United States

Location

WR-ClinSearch, LLC

Chattanooga, Tennessee, 37421, United States

Location

New Phase Research & Development

Knoxville, Tennessee, 37909, United States

Location

MW Clinical Research Center

Beaumont, Texas, 77701, United States

Location

Texas Tech University Health Sciences Center

El Paso, Texas, 79905-2709, United States

Location

Southwest Clinical Trials

Houston, Texas, 77074, United States

Location

Southwest Clinical Trials

Houston, Texas, 77081, United States

Location

Quality Research Inc

San Antonio, Texas, 78209, United States

Location

Diagnostics Research Group

San Antonio, Texas, 78229, United States

Location

DCT - Stone Oak, LLC dba Discovery Clinical Trials

San Antonio, Texas, 78258, United States

Location

Advanced Research Institute

Ogden, Utah, 84405, United States

Location

New River Valley Research Institute

Christiansburg, Virginia, 24073, United States

Location

MeSH Terms

Conditions

Abdominal PainDiarrheaIrritable Bowel Syndrome

Condition Hierarchy (Ancestors)

PainNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsSigns and Symptoms, DigestiveColonic Diseases, FunctionalColonic DiseasesIntestinal DiseasesGastrointestinal DiseasesDigestive System Diseases

Results Point of Contact

Title
Wilmin Bartolini, Ph.D.
Organization
Ironwood Pharmaceuticals, Inc.

Study Officials

  • Wilmin Bartolini, PhD

    Ironwood Pharmaceuticals, Inc.

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 22, 2019

First Posted

April 30, 2019

Study Start

May 1, 2019

Primary Completion

February 26, 2020

Study Completion

March 11, 2020

Last Updated

March 12, 2021

Results First Posted

March 12, 2021

Record last verified: 2021-02

Locations