NCT03691168

Brief Summary

Based on a clinical multi-center study of the natural course of inherited retinal dystrophies in Chinese population, screening fundus imaging indicators for patients with Chinese inherited retinal dystrophies, describing the clinical features of Chinese patients with inherited retinal dystrophies, and establishing a diagnosis of hereditary retinal diseases - Follow-up norms; establish a network-based multi-center diagnosis and follow-up platform; obtain a biological sample library of hereditary retinal diseases mainly in China. The research will further improve and enrich the genotype, phenotypic characteristics and natural course of Chinese inherited retinal dystrophies, in order to promote the clinical evaluation of clinical inherited retinal dystrophies and the standardization of genetic diagnosis. It is also the evidence for the best timing for future gene therapy, to obtain the best therapeutic effect, and to provide a theoretical basis for achieving precise treatment.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
500

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jun 2018

Longer than P75 for all trials

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2018

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

September 28, 2018

Completed
3 days until next milestone

First Posted

Study publicly available on registry

October 1, 2018

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 30, 2019

Completed
4 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 30, 2023

Completed
Last Updated

October 1, 2018

Status Verified

September 1, 2018

Enrollment Period

12 months

First QC Date

September 28, 2018

Last Update Submit

September 28, 2018

Conditions

Keywords

Inherited retinal dystrophies, Gene screen

Outcome Measures

Primary Outcomes (1)

  • Visual acuity

    A typical Snellen chart that if frequently used for visual acuity testing

    60 months

Eligibility Criteria

Age4 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients with inherited retinal dystrophies

You may qualify if:

  • Patients with IRDs whose mutations have been identified
  • \~70 years old
  • Complete 4 basic examinations of the eye: Corrective vision; fundus photography; OCT; ERG

You may not qualify if:

  • Has participated in other interventional treatment studies;
  • Patients with severe systemic diseases, mental dysplasia, mental illness;
  • Unable to accept eye examination patients;
  • Traumatic retinopathy, retinal inflammatory disease, paraneoplastic retinopathy, drug toxicity, and rare diseases such as diffuse unilateral subacute optic retinitis
  • At the initial visit, the patient's binocular vision is displayed as no light.
  • Both eyes have a history of internal eye surgery

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Shanghai General Hospital

Shanghai, Shanghai Municipality, 200080, China

RECRUITING

Biospecimen

Retention: SAMPLES WITH DNA

Blood

Study Officials

  • XiaoDong Sun, PHD

    Shanghai General Hospital, Shanghai Jiao Tong University School of Medicine

    PRINCIPAL INVESTIGATOR

Central Study Contacts

huixun Jia, Master

CONTACT

Wenqiu Wang, PHD

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Professor

Study Record Dates

First Submitted

September 28, 2018

First Posted

October 1, 2018

Study Start

June 1, 2018

Primary Completion

May 30, 2019

Study Completion

May 30, 2023

Last Updated

October 1, 2018

Record last verified: 2018-09

Locations