NCT03662776

Brief Summary

The purpose of this study is to find out about the quality of life and health in patients who had retinoblastoma in one eye (unilateral retinoblastoma), who either received treatment with chemotherapy injected directly into an artery leading to the eye (intra-arterial chemotherapy) or removal of the eye (enucleation). By quality of life, the investigators mean how the participants are feeling about being satisfied with things in their life, including, physical health, emotional health, and their ability to carry out daily activities. The investigators want to see if either treatment option would affect quality of life differently. The investigators hope that this information will help us provide better care to future children with retinoblastoma and better follow-up care for survivors of retinoblastoma.

Trial Health

75
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
120

participants targeted

Target at P50-P75 for all trials

Timeline
2mo left

Started Aug 2018

Longer than P75 for all trials

Geographic Reach
1 country

2 active sites

Status
enrolling by invitation

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress97%
Aug 2018Aug 2026

Study Start

First participant enrolled

August 31, 2018

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

September 4, 2018

Completed
3 days until next milestone

First Posted

Study publicly available on registry

September 7, 2018

Completed
7.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2026

Last Updated

September 3, 2025

Status Verified

September 1, 2025

Enrollment Period

7.9 years

First QC Date

September 4, 2018

Last Update Submit

September 2, 2025

Conditions

Keywords

Quality of Lifephysical healthemotional health18-397

Outcome Measures

Primary Outcomes (3)

  • social-emotional health

    as measured by Behavior Assessment System for Children, 3rd edition, (BASC™-3;as measured by the BASC-3) Surveys have been normed on a representative sample that closely matches United States census population characteristics; T scores and percentiles in relation to general norms are calculated for each scale. The BASC-3 uses a T score metric where 50 is the mean for the population norm and the standard deviation is 10.

    2 years

  • behavioral health

    as measured by Behavior Assessment System for Children, 3rd edition, (BASC™-3; The following four T Scores will be analyzed for these BASC-3 summary scores (1) Externalizing Problems, (2) Internalizing Problems, (3) Behavior Symptoms Index and (4) Adaptive Skills. The "at-risk" category applies to any individual who scores 2 SD above the mean of 50, while "clinically significant" risk refers to those who score 3 SD above the mean. Additional scores are also provided which may be used to identify risk for more specific behavioral or emotional areas of concern.

    2 year

  • compare HRQoL

    as measured by the Patient Reported Outcomes Measurement Information System (PROMIS®) PROMIS measures use a T-score metric where 50 is the mean for the reference population and 10 is the standard deviation of that population. Higher scores correspond to a higher degree of symptom burden (for those items measuring symptoms) or a higher level of functioning (for physical functioning items)

    2 years

Study Arms (2)

retinoblastoma survivors treated with enucleation

MSK will contact all families of 1-year survivors of unilateral retinoblastoma treated with enucleation or intra-arterial chemotherapy at MSK and TCH between 2006 or later for completion of validated questionnaires integrating the BASC-3 and PROMIS surveys. The survey may be administered in-person during clinic or by mail, based upon participant preference.

Behavioral: BASC-3 surveyBehavioral: PROMIS survey

retinoblastoma survivors treated with intra-arteria chemo

MSK will contact all families of 1-year survivors of unilateral retinoblastoma treated with enucleation or intra-arterial chemotherapy at MSK and TCH between 2006 or later for completion of validated questionnaires integrating the BASC-3 and PROMIS surveys. The survey may be administered in-person during clinic or by mail, based upon participant preference.

Behavioral: BASC-3 surveyBehavioral: PROMIS survey

Interventions

BASC-3 surveyBEHAVIORAL

A comprehensive questionnaire, incorporating the BASC-3 and PROMIS measures, will be administered to parents of participants ages 8-17. The BASC-3 and PROMIS scales each have a parent and child version; these scales will be used to measure the secondary objective of parent and patient concordance rates for all participants ages 8 and older.

retinoblastoma survivors treated with enucleationretinoblastoma survivors treated with intra-arteria chemo
PROMIS surveyBEHAVIORAL

A comprehensive questionnaire, incorporating the BASC-3 and PROMIS measures, will be administered to parents of participants ages 8-17. The BASC-3 and PROMIS scales each have a parent and child version; these scales will be used to measure the secondary objective of parent and patient concordance rates for all participants ages 8 and older.

retinoblastoma survivors treated with enucleationretinoblastoma survivors treated with intra-arteria chemo

Eligibility Criteria

Age8 Years - 17 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

Eligible survivors of unilateral retinoblastoma will be identified via the MSK and TCH databases and offered participation in the study.

You may qualify if:

  • Ability to speak and understand English or Spanish
  • Diagnosis of unilateral retinoblastoma at any age, confirmed by the enrolling institution
  • Treatment of retinoblastoma between 2006 or later
  • Patients must between the age of 8-17 years old
  • At least 1 year since completion of all cancer-directed therapy
  • Treatment with enucleation of the affected eye or intra-arterial chemotherapy
  • Parent of patient:
  • Ability to speak and understand English or Spanish
  • Ability to confirm that he or she is the parent of a child treated for unilateral retinoblastoma who meets the eligibility criteria listed above
  • Ability to provide informed consent

You may not qualify if:

  • Patients, or parents of patients, treated with both enucleation and intra-arterial chemotherapy are not eligible

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Texas Children's Hospital (Data Collection)

Houston, Texas, 77030, United States

Location

Related Links

MeSH Terms

Conditions

Psychological Well-Being

Condition Hierarchy (Ancestors)

Personal SatisfactionBehavior

Study Officials

  • Laura Cimini, PhD

    Memorial Sloan Kettering Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
CASE CROSSOVER
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 4, 2018

First Posted

September 7, 2018

Study Start

August 31, 2018

Primary Completion (Estimated)

August 1, 2026

Study Completion (Estimated)

August 1, 2026

Last Updated

September 3, 2025

Record last verified: 2025-09

Locations