NCT03657095

Brief Summary

This is a multi-center, open-label study for eligible participants who were actively participating in the BPS-314d-MR-PAH-302 double-blind study (NCT01908699) at the time the study was concluded. This open-label extension (OLE) study will evaluate the safety, tolerability, and efficacy of long-term treatment with esuberaprost sodium tablets (Beraprost Sodium 314d Modified Release tablets).

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
112

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Dec 2018

Shorter than P25 for phase_3

Geographic Reach
2 countries

45 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 18, 2018

Completed
4 months until next milestone

First Posted

Study publicly available on registry

September 4, 2018

Completed
3 months until next milestone

Study Start

First participant enrolled

December 10, 2018

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 20, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 20, 2019

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

September 7, 2020

Completed
Last Updated

September 7, 2020

Status Verified

September 1, 2020

Enrollment Period

7 months

First QC Date

May 18, 2018

Results QC Date

August 4, 2020

Last Update Submit

September 3, 2020

Conditions

Keywords

HypertensionFamilial Primary Pulmonary HypertensionHypertension, PulmonaryLung DiseasesVascular DiseasesCardiovascular DiseasesRespiratory Tract DiseasesProstacyclinBeraprostEpoprostenolPlatelet Aggregation InhibitorsVasodilator AgentsAntihypertensive Agents

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Treatment Emergent Adverse Events (TEAEs)

    A TEAE is any untoward medical occurrence or undesirable event(s) experienced in a participant that begins or worsens following administration of study drug, whether or not considered related to study drug by Investigator. A serious adverse event (SAE) is an adverse event (AE) resulting in any of the following outcomes or deemed significant for any other reason, death, initial or prolonged inpatient hospitalization, life-threatening experience (immediate risk of dying), or persistent or significant disability/incapacity. AEs included both SAEs and non-serious AEs. AEs were coded using Medical Dictionary for Regulatory Activities (MedDRA) Version 20.1. A summary of serious and all other non-serious adverse events, regardless of causality, is located in the Reported Adverse Events module.

    Baseline up to Month 7

Secondary Outcomes (4)

  • Area Walked for the 6 Minute Walk Distance (6MWD) Test

    Week 4 and then every 3 months until study termination (Month 7)

  • Borg Dyspnea Score

    Week 4 and then every 3 months until study termination (Month 7)

  • Number of Participants in Each Category of the World Health Organization (WHO) Functional Class (FC)

    Week 4 and then every 3 months until study termination (Month 7)

  • Number of Participants With a TEAE of N-terminal Pro-brain Natriuretic Peptide (NT-pro-BNP) Increased

    Baseline up to Month 7

Study Arms (2)

Esuberaprost

EXPERIMENTAL

Participants who received esuberaprost during the BPS-314d-MR-PAH-302 double-blind study will receive 2 tablets of 15 μg esuberaprost sodium tablets for oral administration QID for up to 7 months (which will include the 4 weeks of blinded transition).

Drug: Esuberaprost

Placebo/Esuberaprost

PLACEBO COMPARATOR

Participants who received placebo during the BPS-314d-MR-PAH-302 double-blind study will receive 1 esuberaprost tablet and 1 placebo tablet QID during the first 2 weeks of the blinded transition and then receive 2 esuberaprost tablets QID for the rest of the study, for up to 7 months (which will include the other 2 weeks of the total 4-week blinded transition).

Drug: EsuberaprostDrug: Placebo

Interventions

Sodium tablets

Also known as: Beraprost Sodium 314d Modified Release tablets
EsuberaprostPlacebo/Esuberaprost

Placebo tablets, which are identical in size and appearance to those containing Esuberaprost.

Placebo/Esuberaprost

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participant must have been actively participating in the double-blind study, BPS-314d-MR-PAH-302 (NCT01908699), when the Sponsor concluded that study.
  • In the Investigator's opinion, participant must be competent to understand the information given in the Institutional Review Board (IRB) or Independent Ethics Committee (IEC) approved informed consent form (ICF) and must sign the form prior to the initiation of any study procedures.
  • Women of child-bearing potential (defined as less than 1 year post-menopausal and not surgically sterile) must be practicing abstinence or using 2 highly-effective methods of contraception (defined as a method of birth control that results in a low failure rate \[that is, less than 1% per year, such as approved hormonal contraceptives, barrier methods (such as a condom or diaphragm) used with a spermicide or an intrauterine device\]). Participant must have a negative pregnancy test at the BPS-314d-MR-PAH-302 EOS Visit / BPS-314d-MR-PAH-303 Enrollment Visit.
  • Participant must be willing and able to comply with study requirements and restrictions.

You may not qualify if:

  • Participant is pregnant or lactating.
  • Participant is scheduled to receive another investigational drug, device, or therapy during the course of the study.
  • Participant is taking or intends to take any prostacyclin / prostacyclin (IP) analog or IP receptor agonist (except for treprostinil, inhaled \[Tyvaso®\]).
  • Participant has any other clinically significant illness or other reason that, in the opinion of the Investigator, might put the participant at risk of harm during the study or might adversely affect the interpretation of the study data.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (45)

The University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Cedars-Sinai Medical Center

Beverly Hills, California, 90211, United States

Location

University of California San Diego Medical Center

La Jolla, California, 92093, United States

Location

University of California Los Angeles UCLA

Los Angeles, California, 90024, United States

Location

West Los Angeles VA Healthcare Center

Los Angeles, California, 90073, United States

Location

Santa Barbara Pulmonary Associates

Santa Barbara, California, 93102, United States

Location

Stanford Hospital and Clinics

Stanford, California, 94305, United States

Location

Harbor-UCLA Medical Center

Torrance, California, 90502, United States

Location

Allianz Research Institute

Westminster, California, 92683, United States

Location

University of Colorado Health Sciences Center

Aurora, Colorado, 80045, United States

Location

Aurora Denver Cardiology Associates

Denver, Colorado, 80128, United States

Location

South Denver Cardiology Associates

Littleton, Colorado, 80120, United States

Location

Bay Area Cardiology Research

Brandon, Florida, 33511, United States

Location

University of Florida Clinical Research Center

Gainesville, Florida, 32610, United States

Location

Florida Hospital

Orlando, Florida, 32803, United States

Location

South Miami Heart Specialists

South Miami, Florida, 33143, United States

Location

Cleveland Clinic Florida

Weston, Florida, 33331, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Pulmonary & Critical Care of Atlanta

Atlanta, Georgia, 30342, United States

Location

Georgia Clinical Research

Austell, Georgia, 30106, United States

Location

Indiana University Health North Hospital

Indianapolis, Indiana, 46202, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 54224, United States

Location

University of Louisville Research Foundation

Louisville, Kentucky, 40202, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

University of Maryland Medical Center

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21205, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Beaumont Health

Troy, Michigan, 48085, United States

Location

Albany Medical Center

Albany, New York, 12208, United States

Location

The Mount Sinai Hospital

New York, New York, 10029, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

The Ohio State University Wexner Medical Center

Columbus, Ohio, 43221, United States

Location

The University of Toledo

Toledo, Ohio, 43614, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Anderson Pharmaceutical Research, LLC

Anderson, South Carolina, 29621, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Scott & White Memorial Hospital

Temple, Texas, 76508, United States

Location

Sentara Cardiovascular Research Institute

Norfolk, Virginia, 23507, United States

Location

University of Washington Medical Center

Seattle, Washington, 98195, United States

Location

Rabin Medical Center

Petah Tikva, 49100, Israel

Location

The Chaim Sheba Medical Center

Tel Litwinsky, 52621, Israel

Location

MeSH Terms

Conditions

Pulmonary Arterial HypertensionHypertensionFamilial Primary Pulmonary HypertensionHypertension, PulmonaryLung DiseasesVascular DiseasesCardiovascular DiseasesRespiratory Tract Diseases

Interventions

beraprost

Limitations and Caveats

The study was terminated early due to the pivotal study, BPS-314d-MR-PAH-302 (NCT01908699), failed to demonstrate efficacy.

Results Point of Contact

Title
Lung Biotechnology PBC
Organization
Lung Biotechnology PBC Study Director

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NON RANDOMIZED
Masking
NONE
Masking Details
Treatment during the first 4 weeks of this study will be double-blind. The Investigator and study staff, the participants, the monitors, and the Sponsor will remain blinded to the treatment group allocation from BPS-314d-MR-PAH-302 double-blind study (NCT01908699) and to study drug during the first 4 weeks of the OLE study while the participants transition to the OLE treatment. After the 4 weeks, the study will continue as unblinded and open label.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 18, 2018

First Posted

September 4, 2018

Study Start

December 10, 2018

Primary Completion

July 20, 2019

Study Completion

July 20, 2019

Last Updated

September 7, 2020

Results First Posted

September 7, 2020

Record last verified: 2020-09

Locations