NCT03604198

Brief Summary

This is an open-label extension study to evaluate the long-term safety of relacorilant in patients with endogenous Cushing syndrome who successfully completed participation in a Corcept-sponsored study of relacorilant and may benefit from continuing treatment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
125

participants targeted

Target at P75+ for phase_2

Timeline
7mo left

Started May 2018

Longer than P75 for phase_2

Geographic Reach
10 countries

48 active sites

Status
active not recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress93%
May 2018Dec 2026

First Submitted

Initial submission to the registry

May 1, 2018

Completed
6 days until next milestone

Study Start

First participant enrolled

May 7, 2018

Completed
3 months until next milestone

First Posted

Study publicly available on registry

July 27, 2018

Completed
8.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2026

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2026

Last Updated

April 21, 2026

Status Verified

April 1, 2026

Enrollment Period

8.6 years

First QC Date

May 1, 2018

Last Update Submit

April 16, 2026

Conditions

Keywords

Cushing SyndromeCushing DiseaseCushingHypercortisolemiaCushingoidType 2 DiabetesImpaired Glucose IntoleranceHypertensionAdrenal Corticotrophic Hormone (ACTH)Adrenocortical CarcinomaPrimary Pigmented Nodular Adrenal Disease (PPNAD)Moon FaciesDorsocervical Fat PadAdrenal AdenomaAdrenal CarcinomaAdrenal AutonomyCortisol

Outcome Measures

Primary Outcomes (1)

  • Long-term safety of relacorilant

    Number of participants with treatment-emergent adverse events (TEAEs)as assessed by CTCAE v4.0

    36 months

Other Outcomes (6)

  • Long-term benefit of relacorilant

    36 months

  • Long-term benefit of relacorilant

    36 months

  • Long-term benefit of relacorilant

    36 months

  • +3 more other outcomes

Study Arms (1)

relacorilant (CORT125134)

EXPERIMENTAL
Drug: relacorilant

Interventions

CORT125134 is supplied as capsules for oral dosing.

Also known as: CORT125134
relacorilant (CORT125134)

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Have completed a Corcept-sponsored study of relacorilant in endogenous Cushing syndrome with at least 80% compliance with the dosing schedule.
  • According to the Investigator's opinion will benefit from continuing treatment with relacorilant

You may not qualify if:

  • Premature discontinuation from a relacorilant parent study.
  • Has uncontrolled, clinically significant hypothyroidism or hyperthyroidism
  • Has poorly controlled hypertension
  • Has Stage ≥ 4 renal failure

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (48)

Site 49

Phoenix, Arizona, 85013, United States

Location

Site 35

Stanford, California, 94305, United States

Location

Site 39

Torrance, California, 90502, United States

Location

Site 50

Miami, Florida, 33136, United States

Location

Site 10

Atlanta, Georgia, 30318, United States

Location

Site 9

Chicago, Illinois, 60611, United States

Location

Site 1

Indianapolis, Indiana, 46202, United States

Location

Site 5

Metairie, Louisiana, 70006, United States

Location

Site 27

Baltimore, Maryland, 21287, United States

Location

Site 13

Fall River, Massachusetts, 02721, United States

Location

Site 8

Ann Arbor, Michigan, 48109, United States

Location

Site 36

Rochester, Minnesota, 55905, United States

Location

Site 34

Jackson, Mississippi, 39202, United States

Location

Site 3

St Louis, Missouri, 63110, United States

Location

Site 55

Reno, Nevada, 89511, United States

Location

Site 6

Albany, New York, 12206, United States

Location

Site 24

New York, New York, 10021, United States

Location

Site 4

Wilmington, North Carolina, 28401, United States

Location

Site 43

Cleveland, Ohio, 44195, United States

Location

Site 2

Pittsburgh, Pennsylvania, 15212, United States

Location

Site 46

Pittsburgh, Pennsylvania, 15213, United States

Location

Site 11

Dallas, Texas, 75390, United States

Location

Site 7

El Paso, Texas, 79935, United States

Location

Site 32

Fort Worth, Texas, 76132, United States

Location

Site 12

Houston, Texas, 77079, United States

Location

Site 14

Vienna, 1090, Austria

Location

Site 51

Nova Scotia, Canada

Location

Site 16

Munich, Germany

Location

Site 42

Würzburg, 97080, Germany

Location

Site 20

Ramat Gan, 5265601, Israel

Location

Site 29

Tel Aviv, 64239, Israel

Location

Site 40

Ancona, 60126, Italy

Location

Site 44

Messina, 98125, Italy

Location

Site 25

Milan, 20145, Italy

Location

Site 21

Naples, 80131, Italy

Location

Site 48

Padova, 35128, Italy

Location

Site 52

Torino, Italy

Location

Site 33

Rotterdam, 3015 GD, Netherlands

Location

Site 47

Krakow, 30-688, Poland

Location

Site 45

Lublin, 20412, Poland

Location

Site 37

Bucharest, 050474, Romania

Location

Site 31

Bucharest, 10825, Romania

Location

Site 28

Bucharest, 11863, Romania

Location

Site 53

Alicante, Spain

Location

Site 18

Girona, Spain

Location

Site 17

Madrid, 28007, Spain

Location

Site 38

Málaga, 29006, Spain

Location

Site 19

Seville, Spain

Location

MeSH Terms

Conditions

Cushing SyndromePituitary ACTH HypersecretionACTH Syndrome, EctopicDiabetes Mellitus, Type 2HypertensionAdrenocortical CarcinomaAdrenal Cortex Neoplasms

Interventions

relacorilant

Condition Hierarchy (Ancestors)

Adrenocortical HyperfunctionAdrenal Gland DiseasesEndocrine System DiseasesHyperpituitarismPituitary DiseasesHypothalamic DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesParaneoplastic Endocrine SyndromesParaneoplastic SyndromesNeoplasmsDiabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesVascular DiseasesCardiovascular DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeAdrenal Gland NeoplasmsEndocrine Gland NeoplasmsNeoplasms by SiteAdrenal Cortex Diseases

Study Officials

  • Ying Ru, MD, PhD

    Corcept Therapeutics

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 1, 2018

First Posted

July 27, 2018

Study Start

May 7, 2018

Primary Completion (Estimated)

December 1, 2026

Study Completion (Estimated)

December 1, 2026

Last Updated

April 21, 2026

Record last verified: 2026-04

Data Sharing

IPD Sharing
Will not share

Locations