NCT03569826

Brief Summary

CaNAL is a longitudinal observational cohort study of patients diagnosed with Primary Biliary Cholangitis (PBC), Autoimmune Hepatitis (AIH), or overlap syndrome. This study creates a nationwide registry and network focusing on high quality long-term follow-up of individual patient data from major Canadian centers. Primary Biliary Cholangitis (PBC) and Autoimmune Hepatitis (AIH) are rare and slowly progressive liver diseases associated with development of cirrhosis, liver cancer (HCC) and liver failure requiring liver transplantation or leading to premature death. The rarity and slowly progressive nature of these autoimmune liver diseases make them difficult to study and only a large scale approach combining patient data from multiple centers across Canada will allow new insights. The primary aim of the Canadian Network for Autoimmune Liver Disease is to build a Canadian registry of patients with PBC, AIH, and overlap syndrome. We capture patient characteristics, laboratory assessments and natural history, patient-reported outcomes including quality of life measures and environmental exposures, response to treatment, and pre- and post-transplant outcomes. We will then identify risk factors associated with critical outcomes for the patient, including response to treatment, progression to transplant, risk of liver cancer, and recurrent disease after transplant. We can identify biomarkers (biochemical indicators of progression of disease) to help diagnose autoimmune liver disease at its earliest stages, ensuring timely treatment and preventing disease progression. CaNAL will provide a better understanding of autoimmune liver diseases, biomarkers predictive of disease progression or non-response to therapy as well as better knowledge of the etiology and pathogenesis. CaNAL will also help to serve as a platform for conducting clinical trials or targeted lab-studies to answer important questions that are unlikely to be evaluated by the pharmaceutical industry.

Trial Health

77
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
2,500

participants targeted

Target at P75+ for all trials

Timeline
32mo left

Started Feb 2018

Longer than P75 for all trials

Geographic Reach
1 country

15 active sites

Status
recruiting

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Progress76%
Feb 2018Dec 2028

Study Start

First participant enrolled

February 7, 2018

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

May 25, 2018

Completed
1 month until next milestone

First Posted

Study publicly available on registry

June 26, 2018

Completed
10.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2028

Expected
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2028

Last Updated

June 7, 2021

Status Verified

June 1, 2021

Enrollment Period

10.8 years

First QC Date

May 25, 2018

Last Update Submit

June 4, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Liver transplant-free survival over time

    Time-to-event

    Up to 6 years or time of death/liver transplant

Secondary Outcomes (6)

  • Biochemical values over time (e.g. aspartate aminotransferase, alkaline phosphatase, alanine aminotransferase, Bilirubin)

    Through study completion, an average of 6 months

  • Short Form 36 (SF-36)

    Through study completion, an average of 6 months

  • PBC-40

    Through study completion, an average of 6 months

  • 5D Pruritus Scale

    Through study completion, an average of 6 months

  • Itch Visual Analog Scale

    Through study completion, an average of 6 months

  • +1 more secondary outcomes

Study Arms (1)

Observational

There is no intervention being administered. This registry only observes patients through their regular standard of care visits.

Other: Observational; no intervention

Interventions

Observational; no intervention

Observational

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients with a diagnosis of Primary Biliary Cholangitis and/or Autoimmune Hepatitis across Canada.

You may qualify if:

  • Diagnosis of Primary Biliary Cholangitis and/or Autoimmune Hepatitis

You may not qualify if:

  • Less than 18 years of age

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Foothills Medical Centre

Calgary, Alberta, T2N 2T9, Canada

NOT YET RECRUITING

University of Alberta Hospital

Edmonton, Alberta, T6G 2B7, Canada

RECRUITING

Vancouver General Hospital

Vancouver, British Columbia, V5Z 1M9, Canada

NOT YET RECRUITING

St. Paul's Hospital

Vancouver, British Columbia, V6Z 1Y6, Canada

NOT YET RECRUITING

Health Sciences Centre

Winnipeg, Manitoba, R3A 1R9, Canada

NOT YET RECRUITING

Queen Elizabeth II Health Sciences Centre

Halifax, Nova Scotia, B3H 2Y9, Canada

ACTIVE NOT RECRUITING

McMaster University Medical Centre

Hamilton, Ontario, L8S 4K1, Canada

NOT YET RECRUITING

Kingston Health Sciences Centre (HDH Site)

Kingston, Ontario, K7L 5G2, Canada

ACTIVE NOT RECRUITING

London Health Sciences Centre - University Hospital

London, Ontario, N6A 5A5, Canada

RECRUITING

The Ottawa Hospital

Ottawa, Ontario, K1H 8L6, Canada

RECRUITING

Toronto General Hospital

Toronto, Ontario, M5G 2C4, Canada

RECRUITING

Centre hospitalier de l'Université de Montréal

Montreal, Quebec, H2X 0A9, Canada

RECRUITING

McMaster University Medical Centre

Montreal, Quebec, H4A 3J1, Canada

NOT YET RECRUITING

Université de Sherbrooke

Sherbrooke, Quebec, J1G2E8, Canada

RECRUITING

Royal University Hospital

Saskatoon, Saskatchewan, S7N 0W8, Canada

RECRUITING

MeSH Terms

Conditions

Hepatitis, Autoimmune

Condition Hierarchy (Ancestors)

Hepatitis, ChronicHepatitisLiver DiseasesDigestive System DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Bettina Hansen, PhD

    University Health Network, Toronto General Hospital

    PRINCIPAL INVESTIGATOR
  • Andrew Mason, MD

    University of Alberta

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Surain Roberts, AB

CONTACT

Kattleya Tirona, BA, CCRP

CONTACT

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Target Duration
6 Years
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 25, 2018

First Posted

June 26, 2018

Study Start

February 7, 2018

Primary Completion (Estimated)

December 1, 2028

Study Completion (Estimated)

December 1, 2028

Last Updated

June 7, 2021

Record last verified: 2021-06

Data Sharing

IPD Sharing
Will not share

Patient data will be anonymized. A standardized electronic case record (e-CRF) form will be used to capture the data. The e-CRF form has been designed in REDCap, a secure web based application supporting data capture for research studies. REDCap is designed to comply with HIPAA security regulations. The CaNAL REDCap database (REDCap project CaNAL) has been established at the University of Alberta under the jurisdiction of the Women and Children's Health Research Institute (WCHRI). Individual centres will have access only to their own data and patient identifiers will only be visible to the individual centres. The steering committee will have access to all anonymized data within the REDCap database, that is without any patient identifiers. Main centres in Toronto and Edmonton will have access to de-identified data. Results will be disseminated via publication in international literature and presentation at international liver conferences. Patient data will be anonymous.

Locations