NCT03471078

Brief Summary

Phase 3 randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of avatrombopag in subjects with chemotherapy-induced thrombocytopenia receiving chemotherapy for the treatment of ovarian, lung (small cell and non-small cell) and bladder cancer.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
122

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Oct 2018

Typical duration for phase_3

Geographic Reach
7 countries

55 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 7, 2018

Completed
13 days until next milestone

First Posted

Study publicly available on registry

March 20, 2018

Completed
7 months until next milestone

Study Start

First participant enrolled

October 12, 2018

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 28, 2020

Completed
1.2 years until next milestone

Results Posted

Study results publicly available

November 24, 2021

Completed
1.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

January 31, 2023

Completed
Last Updated

September 28, 2023

Status Verified

September 1, 2023

Enrollment Period

1.9 years

First QC Date

March 7, 2018

Results QC Date

September 10, 2021

Last Update Submit

September 19, 2023

Conditions

Keywords

CITThrombocytopenia

Outcome Measures

Primary Outcomes (1)

  • Percentage of Subjects Who do Not Require Platelet Transfusion, Dose Reduction in Chemotherapy by 15%, or Chemotherapy Delay by >=4 Days

    Randomization up to 33 days

Secondary Outcomes (3)

  • Duration of Severe Thrombocytopenia Defined as a Platelet Count <50 x 10^9/L

    Randomization up to 33 days

  • Change in Platelet Count From Baseline (Nadir)

    Randomization up to 33 days

  • Percentage of Subjects Who Did Not Have Major or Non-major Clinically Relevant Bleeding During the Period After Post-chemotherapy Study Drug Treatment in Cycle X+1 Through Chemotherapy Day of Cycle X+2.

    Randomization up to 33 days

Study Arms (2)

Avatrombopag

EXPERIMENTAL

Study is 2:1 randomization ratio (avatrombopag to placebo). Investigational product administered orally once daily for 5 days prior to chemotherapy and 5 days following chemotherapy treatment.

Drug: Avatrombopag

Placebo

PLACEBO COMPARATOR

Study is 2:1 randomization ratio (avatrombopag to placebo). Investigational product administered orally once daily for 5 days prior to chemotherapy and 5 days following chemotherapy treatment.

Drug: Placebo Oral Tablet

Interventions

Oral avatrombopag tablet

Avatrombopag

Placebo comparator tablet

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Men and women greater than or equal to 18 years of age;
  • A diagnosis of ovarian, lung (small cell or non-small cell) or bladder cancer requiring systemic chemotherapy
  • Participant receiving a chemotherapy regimen given in a 21 or 28-day cycle, including 1 or more of the following agents or class of agents:
  • Nucleoside analog, including gemcitabine and fluorouracil;
  • Carboplatin or cisplatin;
  • Anthracycline; or
  • Alkylating agent;
  • Participant experienced severe thrombocytopenia, defined as 2 platelet counts \<50 x 109/L measured at least 24 hours apart, during the qualifying chemotherapy cycle, of their current chemotherapy regimen
  • ECOG performance status \<=2

You may not qualify if:

  • Participant has experienced \>=Grade 2 CIT other than during the current chemotherapy treatment regimen within 6 months of Screening;
  • Participant has any history of hematologic malignancies, including leukemia, myeloma, myeloproliferative disease, lymphoma, or myelodysplastic diseases;
  • Participant has received \>2 previous lines of chemotherapy or is receiving whole brain radiation during the study treatment period;
  • Participant has a known medical history of genetic prothrombotic syndromes
  • Participant has a history of arterial or venous thrombosis within 3 months of screening;
  • Use of vitamin K antagonists;
  • Participant has previously received a thrombopoietin receptor agonist or recombinant human thrombopoietin for the treatment of CIT within 3 months of screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (55)

Dova Site

Anaheim, California, 92801, United States

Location

Dova Site

Bakersfield, California, 93309, United States

Location

Dova Site

Riverside, California, 92501, United States

Location

Dova Site

Santa Monica, California, 90403, United States

Location

Dova Site

Augusta, Georgia, 30912, United States

Location

Dova Site

Harvey, Illinois, 60426, United States

Location

Dova Site

Skokie, Illinois, 60076, United States

Location

Dova Site

Bloomington, Indiana, 47403, United States

Location

Dova Site

Wichita, Kansas, 67214, United States

Location

Dova Site

Ashland, Kentucky, 41101, United States

Location

Dova Site

Boston, Massachusetts, 02114, United States

Location

Dova Site

Minneapolis, Minnesota, 55417, United States

Location

Dova Site

Canton, Ohio, 44718, United States

Location

Dova Site

Gettysburg, Pennsylvania, 17325, United States

Location

Dova Site

Harbin, China

Location

Dova Site

Linyi, China

Location

Dova Site

Neijiang, China

Location

Dova Site

Shanghai, China

Location

Dova Site

Tianjin, China

Location

Dova Site

Budapest, Hungary

Location

Dova Site

Debrecen, Hungary

Location

Dova Site

Nyíregyháza, Hungary

Location

Dova Site

Törökbálint, Hungary

Location

Dova Site

Lublin, Poland

Location

Dova Site

Olsztyn, Poland

Location

Dova Site

Prabuty, Poland

Location

Dova Site

Tomaszów Mazowiecki, Poland

Location

Dova Site

Warsaw, Poland

Location

Dova Site

Arkhangelsk, Russia

Location

Dova Site

Kazan', Russia

Location

Dova Site

Kursk, Russia

Location

Dova Site

Moscow, Russia

Location

Dova Site

Novosibirsk, Russia

Location

Dova Site

Omsk, Russia

Location

Dova Site

Pyatigorsk, 357502, Russia

Location

Dova Site

Saint Petersburg, 188663, Russia

Location

Dova Site

Saint Petersburg, Russia

Location

Dova Site

Saransk, Russia

Location

Dova Site

Sochi, Russia

Location

Dova Site

Belgrade, Serbia

Location

Dova Site

Kamenitz, Serbia

Location

Dova Site

Kragujevac, Serbia

Location

Dova Site

Cherkasy, Ukraine

Location

Dova Site

Chernihiv, Ukraine

Location

Dova Site

Chernivtsi, Ukraine

Location

Dova Site

Ivano-Frankivsk, Ukraine

Location

Dova Site

Kharkiv, Ukraine

Location

Dova Site

Kherson, Ukraine

Location

Dova Site

Kropyvnytskyi, Ukraine

Location

Dova Site

Kyiv, Ukraine

Location

Dova Site

Odesa, Ukraine

Location

Dova Site

Sumy, Ukraine

Location

Dova Site

Ternopil, Ukraine

Location

Dova Site

Uzhhorod, Ukraine

Location

Dova Site

Vinnytsia, Ukraine

Location

Related Publications (1)

  • Al-Samkari H, Kolb-Sielecki J, Safina SZ, Xue X, Jamieson BD. Avatrombopag for chemotherapy-induced thrombocytopenia in patients with non-haematological malignancies: an international, randomised, double-blind, placebo-controlled, phase 3 trial. Lancet Haematol. 2022 Mar;9(3):e179-e189. doi: 10.1016/S2352-3026(22)00001-1.

    PMID: 35240074BACKGROUND

MeSH Terms

Conditions

Thrombocytopenia

Interventions

avatrombopag

Condition Hierarchy (Ancestors)

Blood Platelet DisordersHematologic DiseasesHemic and Lymphatic DiseasesCytopenia

Results Point of Contact

Title
VP of Global Drug Development
Organization
Dova

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
SUPPORTIVE CARE
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 7, 2018

First Posted

March 20, 2018

Study Start

October 12, 2018

Primary Completion

August 28, 2020

Study Completion

January 31, 2023

Last Updated

September 28, 2023

Results First Posted

November 24, 2021

Record last verified: 2023-09

Locations