NCT03464019

Brief Summary

This was a three-part, multi-center, randomized, double-blind, placebo-controlled study to evaluate the efficacy and safety of etripamil nasal spray (NS) self-administered by participants who experienced an episode of paroxysmal supraventricular tachycardia (PSVT) in an at-home setting. NODE-301 Part 1 included participants that received the randomized study drug to treat an episode of PSVT until the 150th positively adjudicated PSVT episode. Part 2 (also referred as the RAPID study) included participants that did not receive the randomized study drug in Part 1 and newly enrolled participants until the 180th positively adjudicated PSVT episode in Part 2. The study continued for approximately 6 months after the 180th positively adjudicated PSVT episode in Part 2 and this extension is referred to as Part 3 (also referred to as RAPID Extension).

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,097

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jun 2018

Longer than P75 for phase_3

Geographic Reach
9 countries

161 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 7, 2018

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 13, 2018

Completed
3 months until next milestone

Study Start

First participant enrolled

June 18, 2018

Completed
4.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 20, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 20, 2023

Completed
1.5 years until next milestone

Results Posted

Study results publicly available

July 12, 2024

Completed
Last Updated

July 12, 2024

Status Verified

May 1, 2024

Enrollment Period

4.6 years

First QC Date

March 7, 2018

Results QC Date

February 16, 2024

Last Update Submit

June 18, 2024

Conditions

Keywords

Paroxysmal supraventricular tachycardiacardiac monitoringatrioventricular nodal reentrant tachycardiaatrioventricular reciprocating tachycardiacalcium channel blocker administered at homeconversion rate

Outcome Measures

Primary Outcomes (1)

  • The Time to Conversion of an Episode of PSVT to Sinus Rhythm (SR) After Study Drug Administration.

    The primary efficacy endpoint is defined as an adjudicated termination of a positively adjudicated episode of PSVT (AV nodal reentrant tachycardia or AV reentrant tachycardia determination if possible) and conversion to sinus rhythm (SR) for at least 30 seconds within 5 hours (NODE-301 Part 1), or 30 minutes (NODE-301 Parts 2 and 3) of start of study drug dosing.

    NODE-301 Part 1: Within 5 hours of start of study drug dosing. NODE-301 Parts 2 and 3: Within 30 minutes of start of study drug dosing.

Study Arms (6)

Part 1: Etripamil 70 mg Single Dose

EXPERIMENTAL

Self-administration of a single dose etripamil 70 mg for a perceived episode of PSVT.

Drug: Etripamil

Part 1: Placebo Single Dose

PLACEBO COMPARATOR

Self-administration of a single dose of placebo for a perceived episode of PSVT.

Drug: Placebo

Part 1: Test dose only (etripamil 70 mg)

OTHER

Single test dose of etripamil 70 mg in sinus rhythm

Drug: Etripamil Test Dose

Part 2 & Part 3: Etripamil 70 mg with Optional Second Dose

EXPERIMENTAL

Self-administration of 70 mg etripamil for a perceived episode of PSVT followed 10 minutes later by an optional second dose of 70 mg etripamil, if symptoms persisted. Participants could be enrolled in the open-label period to treat an additional PSVT episode with etripamil.

Drug: Etripamil

Part 2 & Part 3: Placebo with Optional Second Dose

PLACEBO COMPARATOR

Self-administration of placebo for a perceived episode of PSVT followed 10 minutes later by an optional second dose of placebo, if symptoms persisted. Participants could be enrolled in the open-label period to treat an additional PSVT episode with etripamil.

Drug: Placebo

Part 2 & Part 3: Test dose only (etripamil 70 mg + 70 mg)

OTHER

Repeat Test Dose of etripamil 70 mg (2X 70mg) 10 minutes apart in sinus rhythm

Drug: Etripamil Test Dose

Interventions

Etripamil administered via the Aptar Pharma Nasal Spray Bidose System, supplied as prefilled devices packaged into child-resistant boxes with instructions for use provided in the study drug box.

Also known as: MSP-2017
Part 1: Etripamil 70 mg Single DosePart 2 & Part 3: Etripamil 70 mg with Optional Second Dose

Placebo administered via the Aptar Pharma Nasal Spray Bidose System, supplied as prefilled devices packaged into child-resistant boxes with instructions for use provided in the study drug box.

Part 1: Placebo Single DosePart 2 & Part 3: Placebo with Optional Second Dose

During the Test Dose, etripamil administered via the Aptar Pharma Nasal Spray Bidose System, supplied as prefilled devices packaged into child-resistant boxes with instructions for use provided in the study drug box.

Also known as: MSP-2017 Test Dose
Part 1: Test dose only (etripamil 70 mg)Part 2 & Part 3: Test dose only (etripamil 70 mg + 70 mg)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants who met all of the following criteria were eligible to participate in the study:
  • Male or female participants at least 18 years of age;
  • Electrographically documented history of PSVT (e.g., electrocardiogram \[ECG\] obtained during an episode of PSVT, Holter monitoring, loop recorder, etc). If participant had a prior ablation for PSVT, participant had to have documented ECG evidence of PSVT post-ablation;
  • History of sustained episodes of PSVT (i.e., typically lasting approximately 20 minutes or longer);
  • Females of childbearing potential who were sexually active with a male partner who were not surgically sterile (i.e., vasectomy) had to agree to use a highly effective form of contraception from the time of signed informed consent until 30 days after the last administration of study drug. Females of childbearing potential had to have a negative serum pregnancy test result at the Screening Visit and at the Final Study Visit, a negative urine pregnancy test at the Test Dose Randomization Visit and had to use a highly effective form of contraception between the visits.
  • The following categories defined females who were NOT considered to be of childbearing potential:
  • Premenopausal females with 1 of the following:
  • Documented hysterectomy,
  • Documented bilateral salpingectomy or tubal ligation; or
  • Documented bilateral oophorectomy, or
  • Postmenopausal females, defined as having amenorrhea for at least 12 months without an alternative medical cause;
  • Male participants, except those who were surgically sterile, had to use an approved highly effective form of contraception during the 3 days after any study drug administration; and
  • Signed written informed consent.

You may not qualify if:

  • Participants who met any of the following criteria were excluded from participation in the study:
  • Systolic blood pressure \<90 mmHg after a 5-minute rest in sitting position at the Screening Visit or before the Test Dose. In participants treated with a chronic prophylactic drug for PSVT (e.g., beta-blockers, verapamil, and diltiazem), the drug could be stopped for at least the equivalent of 5 half-lives, participants could be rescreened once, and chronic use of the drug could not be restarted after randomization;
  • History of severe symptoms of hypotension, especially syncope, during episodes of PSVT;
  • History of atrial arrhythmia that did not involve the AV node as part of the tachycardia circuit (e.g., atrial fibrillation, atrial flutter, intra-atrial tachycardia);
  • History of allergic reaction to verapamil;
  • Current therapy with digoxin or any Class I or III antiarrhythmic drug, except if these drugs were stopped at least the equivalent of 5 half-lives before the Test Dose Randomization Visit;
  • Current chronic therapy with oral amiodarone, or had taken oral amiodarone within 30 days prior to the Test Dose Randomization Visit;
  • Evidence of ventricular pre-excitation (e.g., delta waves, short PR interval \<100 msec, Wolff-Parkinson-White syndrome) on the ECG performed at the Screening Visit or before the Test Dose administration;
  • Evidence of a second- or third-degree AV block on the ECG performed at the Screening Visit or before the Test Dose administration;
  • History or evidence of severe ventricular arrhythmia (e.g., torsades de pointes, ventricular fibrillation, or ventricular tachycardia);
  • Current congestive heart failure defined by the New York Heart Association Class II to IV;
  • History of Acute Coronary Syndrome or stroke within 6 months of screening;
  • Evidence of hepatic dysfunction defined as alanine aminotransferase or aspartate aminotransferase \>3 × the upper limit of normal (ULN) or total bilirubin \>2 × ULN at the Screening Visit, unless due to Gilbert syndrome;
  • Evidence of End-Stage Renal Disease as determined by an estimated glomerular filtration rate assessed at the Screening Visit of \<15 mL/min/1.73m2, or requiring hemodialysis;
  • Females who were pregnant or lactating;
  • +18 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (161)

Arizona Arrhythmia Research Center

Phoenix, Arizona, 85016, United States

Location

Arkansas Cardiology

Little Rock, Arkansas, 72205, United States

Location

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

Medvin Clinical Research

Cerritos, California, 91722, United States

Location

North Coast Cardiolog

Encinitas, California, 92024, United States

Location

Titan Medical Research - Oceanside

Encinitas, California, 92024, United States

Location

Los Alamitos Cardiovascular

Los Alamitos, California, 90720, United States

Location

Amicis Research Center - Northridge

Northridge, California, 91324, United States

Location

RESPIRE Research

Palm Springs, California, 92262, United States

Location

South Denver Cardiology Associates, P.C

Littleton, Colorado, 80120, United States

Location

Cardiology Associates of Fairfield County

Norwalk, Connecticut, 06905, United States

Location

FWD Clinical Research

Boca Raton, Florida, 33486, United States

Location

Baptist Health Ambulatory Services d/b/a

Jacksonville, Florida, 32207, United States

Location

United Health Research, LLC

Miami, Florida, 33144, United States

Location

IACT Health

Columbus, Georgia, 31904, United States

Location

Piedmont Heart Institute- Fayetteville

Fayetteville, Georgia, 30214, United States

Location

Piedmont Heart Institute-Fayetteville

Fayetteville, Georgia, 30309, United States

Location

Georgia Arrythmia Consultants&Research Institute

Macon, Georgia, 31201, United States

Location

St. Luke's Idaho Cardiology Associates

Boise, Idaho, 83702, United States

Location

Idaho Catalyst Clinical Research

Idaho Falls, Idaho, 83404, United States

Location

AMITA Health Medical Group Heart & Vascular Elk Grpve Village

Elk Grove Village, Illinois, 60007, United States

Location

Parkview Physicians Group - Cardiology

Fort Wayne, Indiana, 46845, United States

Location

Mercy One Iowa Heart Center

West Des Moines, Iowa, 50266, United States

Location

Clinical Trials of America, LLC - Monroe, LA

West Monroe, Louisiana, 71291, United States

Location

MedStar Health Research Institute - Chesapeake Cardiovascular Associates

Baltimore, Maryland, 21237, United States

Location

Sparrow Clinical Research Institute

Lansing, Michigan, 48912, United States

Location

Revival Research Institute, LLC - Southgate, MI

Southgate, Michigan, 48195, United States

Location

Mercy Research

St Louis, Missouri, 65804, United States

Location

Cardiovascular Associates of the Delaware Valley - Elmer

Elmer, New Jersey, 08318, United States

Location

Cardiovascular Associates of the Delaware Valley

Haddon Heights, New Jersey, 08035, United States

Location

Atlantic Health System - Morristown Medical Center

Morristown, New Jersey, 07962, United States

Location

Columbia University

New York, New York, 10032, United States

Location

New York Presbyterian Hospital/Weill Cornell Medical Center

New York, New York, 10065, United States

Location

Montefiore Medical Center

The Bronx, New York, 10467, United States

Location

Cary Research Group, LLC

Cary, North Carolina, 27518, United States

Location

Sanger Heart and Vascular Institute

Charlotte, North Carolina, 28204, United States

Location

The Presbyterian Hospital DBA Novant Health Heart and Vascular Institute

Charlotte, North Carolina, 28204, United States

Location

Hatton Institute for Research & Education, Trihealth, Inc. - Cardiology

Cincinnati, Ohio, 45242, United States

Location

The Ohio State University (OSU) Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

Rama Research LLC

Marion, Ohio, 43302, United States

Location

Heart House Research Foundation, LLC

Springfield, Ohio, 45505, United States

Location

ProMedica Toledo Hospital

Toledo, Ohio, 43615, United States

Location

Medical University of South Carolina (MUSC)

Charleston, South Carolina, 29425, United States

Location

Prisma Health Midlands

Columbia, South Carolina, 29203, United States

Location

Monument Health Clinical Research, a department of Monument Health Rapid City Hospital, Inc

Rapid City, South Dakota, 57701, United States

Location

North Texas Research Associates

Allen, Texas, 75013, United States

Location

Cardiovascular Clinic of North Texas

Denton, Texas, 76201, United States

Location

Revival Research Institute, LLC

Denton, Texas, 76201, United States

Location

Apex Trials Group

Fort Worth, Texas, 76104, United States

Location

Angiocardiac Care of Texas

Houston, Texas, 77025, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Scott & White Memorial Hospital: Baylor Scott & White Research Institute

Temple, Texas, 76508, United States

Location

Bay Area Heart

Webster, Texas, 77598, United States

Location

Intermountain Medical Center

Murray, Utah, 84157-7000, United States

Location

Clinique Du Sud- Luxembourg

Arlon, 6700, Belgium

Location

Imelda Hospital

Bonheiden, 2820, Belgium

Location

UVC Brugmann University Hospital - Centre Hospitalier Universitaire (CHU)

Brussels, 1020, Belgium

Location

Universite Libre de Bruxelles (ULB) - Hopital Erasme

Brussels, 1070, Belgium

Location

Antwerp University Hospital (UZA)

Edegem, 2650, Belgium

Location

Grand Hopital de Charleroi (GHdC) - Site Saint-Joseph

Gilly, 6060, Belgium

Location

Pharmacy Campus Virga Jesse (losplaats 7)

Hasselt, 3500, Belgium

Location

University Hospital (UZ) Leuven

Leuven, 3000, Belgium

Location

Regional Hospital Centre Citadelle

Liège, 3000, Belgium

Location

CHU Ambroise Pare

Mons, 7000, Belgium

Location

CHU UCL Namur - Site Godinne

Yvoir, 5530, Belgium

Location

Libin Cardiovascular Institute of Alberta - University of Calgary

Calgary, Alberta, T2N 4Z6, Canada

Location

Royal Alexandra Hospital

Edmonton, Alberta, T5H 3V9, Canada

Location

Medical Arts Health Research Group - North Vancouver

North Vancouver, British Columbia, V5Z 0A9, Canada

Location

Vancouver Coastal Health Research

Vancouver, British Columbia, V5Z 1M9, Canada

Location

Victoria Cardiac Arrhythmia Trials, Inc.

Victoria, British Columbia, V8T 1Z4, Canada

Location

University of Manitoba, St Boniface General Hospital

Winnipeg, Manitoba, R2H 2A6, Canada

Location

Dalhousie University - QEII Health Sciences Centre

Halifax, Nova Scotia, B3H 3A7, Canada

Location

Cambridge Cardiac Care Centre

Cambridge, Ontario, N1R 6V6, Canada

Location

Dawson Road Medical Centre

Guelph, Ontario, N1H 1B1, Canada

Location

Hamilton Health Sciences

Hamilton, Ontario, L8L 0A6, Canada

Location

London Health Sciences Centre

London, Ontario, N6A 5A5, Canada

Location

Partners in Advanced Cardiac Evaluation (PACE) Cardiology Clinic

Newmarket, Ontario, L3Y 2P6, Canada

Location

St. Michael's Hospital

Toronto, Ontario, M5B 1W8, Canada

Location

The Montreal Heart Institute

Montreal, Quebec, H1T 1C8, Canada

Location

CHUM Recherche Cardiologie

Montreal, Quebec, H2X 0A9, Canada

Location

McGill University Health Center - Research Institute

Montreal, Quebec, H3G 1A4, Canada

Location

Institut Universitaire de Cardiologie et de Pneumologie De Quebec

Québec, Quebec, G1V 4G5, Canada

Location

CardioVasc HR

Saint-Jean-sur-Richelieu, Quebec, J3A 1J2, Canada

Location

CIUSSS de l'Estrie - CHUS

Sherbrooke, Quebec, J1H 5N4, Canada

Location

CSSS du Sud de Lanaudiere - Hopital Pierre Le Gardeur

Terrebonne, Quebec, J6V 2H2, Canada

Location

CHRU Besancon - Hopital Jean Minjoz

Besançon, Besancon, 25030, France

Location

CHU Grenoble-Alpes - Hopital Michallon

La Tronche, Grenoble, 38043, France

Location

CHRU de Brest - Hopital de la Cavale Blanche

Brest, 29609, France

Location

HCL Hopital Louis Pradel

Bron, 69677, France

Location

Hopital Saint-Louis de La Rochelle

La Rochelle, 17000, France

Location

CHU de Lille - Institut Cœur Poumon

Lille, 59037, France

Location

Centre Hospitalier de Pau

Pau, 64000, France

Location

Maerkische Gesundheitsholding GmbH - Klinikum Luedenscheid

Lüdenscheid, Ludenscheid, 58515, Germany

Location

Peter Osypka Herzzentrum Munchen

München, Munchen, 81379, Germany

Location

Vivantes Klinikum Neukoelln

Berlin, 12351, Germany

Location

FAZ Dresden-Neustadt GbR

Dresden, 01099, Germany

Location

Kardiologische Praxis

Dresden, 04779, Germany

Location

Kardiologische Gemeinschaftspraxis Papenburg

Papenburg, 26871, Germany

Location

Zentrum fuer Praevention und Rehabilitation

Siegen, 57072, Germany

Location

Dr Lakatos Ferenc Belgyogyaszati-Kardiologiai Maganrendelo

Békéscsaba, Bekescaba, 5600, Hungary

Location

Nehezlegzes Ambulancia

Debrecen, Debrecon, 4026, Hungary

Location

Del-pesti Centrumkorhaz

Budapest, 1097, Hungary

Location

Magyar Honvedseg Egeszsegugyi Kozpont

Budapest, 1134, Hungary

Location

Debreceni Egyetem Klinikai

Debrecen, 4032, Hungary

Location

CRU Hungary Kft.

Encs, H-3860, Hungary

Location

Belvarosi Egeszseghaz

Zalaegerszeg, 8900, Hungary

Location

Meander Medisch Centrum - Locatie Amersfoort

Amersfoort, 3813 TZ, Netherlands

Location

Ziekenhuis Rijnstate - Locatie Arnhem

Arnhem, 6815 AD, Netherlands

Location

Rode Kruis Ziekenhuis

Beverwijk, 1942 LE, Netherlands

Location

Tergooiziekenhuizen Blaricum

Blaricum, 1261 AN, Netherlands

Location

Amphia Ziekenhuis - Locatie Breda Molengracht

Breda, 4818 CK, Netherlands

Location

IJsselland ziekenhuis

Capelle aan den IJssel, 2906 ZC, Netherlands

Location

Reinier de Graaf Gasthuis

Delft, 2625 AD, Netherlands

Location

Deventer Ziekenhuis

Deventer, 7416 SE, Netherlands

Location

Slingeland Ziekenhuis

Doetinchem, 7009 BL, Netherlands

Location

Ziekenhuis Gelderse Vallei

Ede, 6716 RP, Netherlands

Location

Ropcke-Zweers Ziekenhuis

Hardenberg, 7772 SE, Netherlands

Location

Treant Zorggroep

Hoogeveen, 7909, Netherlands

Location

Alrijne Ziekenhuis

Leiderdorp, 2353 GA, Netherlands

Location

Maastricht University Medical Center

Maastricht, 6229 HX, Netherlands

Location

Franciscus Gasthuis & Vlietland - Locatie Vlietland

Schiedam, 3118 JH, Netherlands

Location

Diakonessenhuis - Locatie Utrecht

Utrecht, 3582 KE, Netherlands

Location

Jeroen Bosch Ziekenhuis

Utrecht, 3584 CX, Netherlands

Location

American Heart of Poland S.A., IV Oddzial Kardiologii Inwazyjnej, Elektrostymulacji i Angiologii

Kędzierzyn-Koźle, Kedzierzyn Kozle, 43-450, Poland

Location

Gabinety Daszmed

Krakow, Krakov, 31-534, Poland

Location

Kliniczny Szpital Wojewódzki nr 2, Rzeszów

Rzeszów, Rzeszow, 35-301, Poland

Location

MICS Centrum Medyczne Torun

Bydgoszcz, 85-065, Poland

Location

Centrum Medyczne Kermed

Bydgoszcz, 85-231, Poland

Location

Specjalistyczna Praktyka Lekarska

Katowice, 40-530, Poland

Location

Prywatny Specjalistyczny Gabinet Internistyczny

Libiąż, 32-590, Poland

Location

MEDICOME Sp. z o.o.

Oświęcim, 32-600, Poland

Location

SP ZOZ Szpital Specjalistyczny w Pulawach

Puławy, 24-100, Poland

Location

NZOZ Pro Cordis Sopockie Centrum Badan Kardiologicznych

Sopot, 81-717, Poland

Location

Osrodek Badan Klinicznych CLINSANTE S.C.

Torun, 87-100, Poland

Location

X Oddzial Kardiologii Inwazyjnej, Elektrofizjologii i Elektrostymulacji

Tychy, 43-100, Poland

Location

Kardiosystem

Warsaw, 04-628, Poland

Location

Samodzielny Publiczny Zaklad Opieki Zdrowotnej Centralny Szpital Kliniczny, Uniwersytetu Medycznego w Lodzi

Lodz, Łódź Voivodeship, 92-213, Poland

Location

Instytut Centrum Zdrowia Matki Polki

Lodz, Łódź Voivodeship, 93-338, Poland

Location

Martínez Hervás Cardiólogos

Granada, Andalusia, 18002, Spain

Location

Hospital Germans Trias i Pujol

Badalona, Barcelona, 08916, Spain

Location

Hospital Universitario Reina Sofia

Córdoba, Cordoba, 14004, Spain

Location

Hospital Universitario Virgen de la Victoria

Málaga, Malaga, 29010, Spain

Location

Hospital Clinico Universitario Virgen de la Arrixaca

El Palmar, Murcia, 30120, Spain

Location

Hospital Alvaro Cunqueiro

Vigo, Pontevedra, 36213, Spain

Location

Hospital General Universitario de Valencia (HGUV)

Valencia, Valencia, 46014, Spain

Location

Hospital General Universitario de Alicante

Alicante, 03010, Spain

Location

Hospital Universitario Vall d'Hebron

Barcelona, 08035, Spain

Location

Hospital Universitari de Bellvitge

Barcelona, 08907, Spain

Location

Hospital de la Santa Creu i Sant Pau

Barcelona, 8025, Spain

Location

Complejo Hospitalario Universitario de Granada - Hospital Universitario Virgen de las Nieves

Granada, 18014, Spain

Location

Hospital General Universitario Gregorio Maranon

Madrid, 28007, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Hospital Universitario Puerta de Hierro

Majadahonda, 28222, Spain

Location

Hospital Universitario Central de Asturias

Oviedo, 33011, Spain

Location

Complejo Hospitalario de Navarra

Pamplona, 31008, Spain

Location

Hospital Universitari Sant Joan de Reus

Reus, 43204, Spain

Location

Hospital Universitario la Paz Rua Choupana

Santiago de Compostela, 15706, Spain

Location

Hospital Universitario Virgen Macarena

Seville, 41009, Spain

Location

Hospital Universitario Virgen del Rocio

Seville, 41013, Spain

Location

Hospital Clinico Universitario de Valencia

Valencia, 46010, Spain

Location

Hospital Universitario Clínico Lozano Blesa

Zaragoza, 50009, Spain

Location

Related Publications (3)

  • Stambler BS, Camm AJ, Alings M, Dorian P, Heidbuchel H, Houtgraaf J, Kowey PR, Merino JL, Mondesert B, Piccini JP, Pokorney SD, Sager PT, Verma A, Wharton JM, Bharucha DB, Plat F, Shardonofsky S, Chen M, Ip JE; RAPID Investigators. Self-administered intranasal etripamil using a symptom-prompted, repeat-dose regimen for atrioventricular-nodal-dependent supraventricular tachycardia (RAPID): a multicentre, randomised trial. Lancet. 2023 Jul 8;402(10396):118-128. doi: 10.1016/S0140-6736(23)00776-6. Epub 2023 Jun 15.

  • Stambler BS, Plat F, Sager PT, Shardonofsky S, Wight D, Potvin D, Pandey AS, Ip JE, Coutu B, Mondesert B, Sterns LD, Bennett M, Anderson JL, Damle R, Haberman R, Camm AJ. First Randomized, Multicenter, Placebo-Controlled Study of Self-Administered Intranasal Etripamil for Acute Conversion of Spontaneous Paroxysmal Supraventricular Tachycardia (NODE-301). Circ Arrhythm Electrophysiol. 2022 Dec;15(12):e010915. doi: 10.1161/CIRCEP.122.010915. Epub 2022 Nov 28.

  • Stambler BS, Plat F, Sager PT, Lubkov V, Shardonofsky S, Wight D, Chen M, Camm AJ. Rationale for and design of a multicenter, placebo-controlled, phase 3 study to assess efficacy and safety of intranasal etripamil for the conversion of paroxysmal supraventricular tachycardia. Am Heart J. 2022 Nov;253:20-29. doi: 10.1016/j.ahj.2022.06.005. Epub 2022 Jun 18.

MeSH Terms

Conditions

Tachycardia, VentricularTachycardia, Atrioventricular Nodal Reentry

Interventions

etripamil

Condition Hierarchy (Ancestors)

TachycardiaArrhythmias, CardiacHeart DiseasesCardiovascular DiseasesCardiac Conduction System DiseasePathologic ProcessesPathological Conditions, Signs and SymptomsTachycardia, Reciprocating

Results Point of Contact

Title
Cameron Szakacs_PhD_VP Drug Development
Organization
Milestone Pharmaceuticals Inc.

Study Officials

  • David Bharucha, MD

    Milestone Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Masking Details
Participants, care providers, investigators, and outcomes assessor were blinded to the treatment.
Purpose
TREATMENT
Intervention Model
PARALLEL
Model Details: NODE-301 study comprised 6 arms: * 2 arms consisting of participants enrolled in Part 1 that treated a perceived episode of PSVT with randomized study drug (etripamil NS 70 mg or placebo) in a 2:1 ratio. * 1 arm consisting of participants that only received the Test Dose in Part 1. * 2 arms consisting of participants enrolled in Parts 2 and 3 that treated a perceived episode of PSVT with randomized study drug (etripamil NS 70 mg with optional second dose of 70 mg etripamil or placebo) in a 1:1 ratio and could be enrolled in the open-label period to treat an additional PSVT episode with etripamil * 1 arm consisting of participants that only received the Test Dose in Parts 2 and 3.
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 7, 2018

First Posted

March 13, 2018

Study Start

June 18, 2018

Primary Completion

January 20, 2023

Study Completion

January 20, 2023

Last Updated

July 12, 2024

Results First Posted

July 12, 2024

Record last verified: 2024-05

Data Sharing

IPD Sharing
Will not share

Locations