NCT03347526

Brief Summary

This study proposes to assess the efficacy of Cosyntropin Injectable Suspension, 1 mg/mL compared to vigabatrin. Additionally, this study proposes to determine efficacy of combination therapy of Cosyntropin Injectable Suspension, 1 mg/mL and vigabatrin to monotherapy Cosyntropin Injectable Suspension, 1mg/mL in children with new onset infantile spasms (IS).

Trial Health

33
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Trial recruitment is currently suspended
Enrollment
394

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Apr 2018

Typical duration for phase_3

Geographic Reach
1 country

14 active sites

Status
suspended

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 15, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

November 20, 2017

Completed
5 months until next milestone

Study Start

First participant enrolled

April 19, 2018

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2021

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2021

Completed
Last Updated

May 27, 2021

Status Verified

May 1, 2021

Enrollment Period

3.1 years

First QC Date

November 15, 2017

Last Update Submit

May 26, 2021

Conditions

Keywords

VigabatrinCosyntropin

Outcome Measures

Primary Outcomes (1)

  • A comparison of Cosyntropin Injectable Suspension and Vigabatrin on the proportion of subjects who become spasm-free as defined by a) and b).

    a) Resolution of hypsarrhythmia via video electroencephalogram (EEG), and b) Resolution of clinical spasms via video EEG.

    2 weeks

Secondary Outcomes (4)

  • A comparison of combination therapy and Cosyntropin Injectable Suspension alone (monotherapy) on the proportion of subjects who become spasm-free as defined by a) and b)

    Day 14-42

  • A comparison between combination therapy and Cosyntropin Injectable Suspension alone (monotherapy) on the proportion of subjects who become seizure free at 6 months.

    6 months

  • Comparison between combination therapy and Cosyntropin Injectable Suspension alone (monotherapy).

    18 months chronological age

  • Comparison between combination therapy and Cosyntropin Injectable Suspension alone (monotherapy).

    18 months chronological age

Study Arms (3)

Cosyntropin Injectable Suspension, 1mg/mL + vigabatrin

EXPERIMENTAL
Drug: Cosyntropin Injectable Suspension 1 MG/ML + vigabatrin

Cosyntropin Injectable Suspension, 1 mg/mL

EXPERIMENTAL
Drug: Cosyntropin Injectable Suspension, 1 mg/mL

Vigabatrin

ACTIVE COMPARATOR
Drug: Vigabatrin

Interventions

Injectable

Cosyntropin Injectable Suspension, 1 mg/mL

Injectable + oral solution

Cosyntropin Injectable Suspension, 1mg/mL + vigabatrin

oral

Vigabatrin

Eligibility Criteria

Age2 Months - 2 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • New onset infantile spasms
  • Age \> 2 months
  • Age\< 2 years
  • Hypsarrhythmia on video-EEG
  • Normal renal function

You may not qualify if:

  • Prior treatment given for infantile spasms
  • Diagnosis of Ohtahara syndrome or Early Myoclonic Epilepsy
  • Absence of hypsarrhythmia
  • Inability for the parent or caregiver to provide consent
  • Inability for the parent or caregiver to complete seizure diary
  • Diagnosis of:
  • scleroderma,
  • osteoporosis,
  • recent systemic fungal infections,
  • ocular herpes simplex,
  • recent surgery,
  • history of or the presence of a peptic ulcer,
  • congestive heart failure,
  • uncontrolled hypertension

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (14)

Children's Hospital Los Angeles

Los Angeles, California, 90027, United States

Location

UCSF Medical Center

San Francisco, California, 94158, United States

Location

University of Colorado Anschutz Medical Campus

Aurora, Colorado, 80045, United States

Location

Children's National Medical Center

Washington D.C., District of Columbia, 20010, United States

Location

Children's Healthcare of Atlanta at Scottish Rite

Atlanta, Georgia, 30342, United States

Location

Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, 60611, United States

Location

Boston Children's Hospital

Boston, Massachusetts, 02115, United States

Location

C.S. Mott Children's Hospital

Ann Arbor, Michigan, 48109, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

Montefiore Medical Center

The Bronx, New York, 10461, United States

Location

Atrium Health

Charlotte, North Carolina, 28204, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Cook Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

MeSH Terms

Conditions

Spasms, Infantile

Interventions

Vigabatrin

Condition Hierarchy (Ancestors)

Epilepsy, GeneralizedEpilepsyBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesEpileptic Syndromes

Intervention Hierarchy (Ancestors)

gamma-Aminobutyric AcidAminobutyratesButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsAmino AcidsAmino Acids, Peptides, and Proteins

Study Officials

  • Kelly G. Knupp, MD

    University of Colorado, Denver

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Masking Details
Blinded outcome measure
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 15, 2017

First Posted

November 20, 2017

Study Start

April 19, 2018

Primary Completion

June 1, 2021

Study Completion

August 1, 2021

Last Updated

May 27, 2021

Record last verified: 2021-05

Locations