NCT03327727

Brief Summary

The purpose of the trial is to evaluate the safety and efficacy of a new antifungal with a novel mechanism of action in immunocompromised adults with invasive aspergillosis.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
4

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Feb 2018

Shorter than P25 for phase_2

Geographic Reach
6 countries

28 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 27, 2017

Completed
4 days until next milestone

First Posted

Study publicly available on registry

October 31, 2017

Completed
4 months until next milestone

Study Start

First participant enrolled

February 20, 2018

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 14, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 14, 2019

Completed
Last Updated

February 27, 2019

Status Verified

February 1, 2019

Enrollment Period

11 months

First QC Date

October 27, 2017

Last Update Submit

February 25, 2019

Conditions

Keywords

IA

Outcome Measures

Primary Outcomes (1)

  • All-cause mortality (ACM)

    4 weeks

Secondary Outcomes (2)

  • ACM

    6 weeks

  • Number of participants with adverse events

    6 weeks

Study Arms (2)

VL-2397

EXPERIMENTAL

Investigational agent VL-2397 600 mg IV infusion administered every day for 28 days (4 weeks) followed by 2 weeks of standard treatment

Drug: Investigational Agent: VL-2397Drug: Standard treatment: Voriconazole, Isavuconazole, or Liposomal amphotericin B

Standard (First-Line) Treatment

ACTIVE COMPARATOR

Investigator selected standard treatments of voriconazole, isavuconazole, or liposomal amphotericin B administered every day for 42 days (6 weeks) per product package insert

Drug: Standard treatment: Voriconazole, Isavuconazole, or Liposomal amphotericin B

Interventions

Voriconazole, Isavuconazole, or Liposomal amphotericin B

Standard (First-Line) TreatmentVL-2397

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Acute Leukemia (AML or ALL) patient or allo-HCT recipient with a diagnosis of IA

You may not qualify if:

  • Pregnant or breastfeeding
  • IA involving sites other than lungs and sinuses
  • Graft failure, acute or extensive chronic GvHD
  • Uncontrolled diabetes

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

University of Alabama at Birmingham Hospital, Division of Infectious Diseases

Birmingham, Alabama, 35233, United States

Location

UC San Diego Moores Cancer Center

La Jolla, California, 92093, United States

Location

UC Davis Health, Dept. of Internal Medicine, Div. of Infectious Diseases

Sacramento, California, 95817, United States

Location

Christiana Care Health Services, Department of Medicine

Newark, Delaware, 19718, United States

Location

Medical College of Georgia at Augusta University

Augusta, Georgia, 30912, United States

Location

DMC Harper University Hospital

Detroit, Michigan, 48201, United States

Location

University of Minnesota, Department of Medicine

Minneapolis, Minnesota, 55455, United States

Location

Washington University School of Medicine, Division of Infectious Disease

St Louis, Missouri, 63110, United States

Location

The University of Texas Health Science Center, Department of Internal Medicine

Houston, Texas, 77030, United States

Location

Fred Hutchinson Cancer Research Center (FHCRC)

Seattle, Washington, 98109, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

University Hospital Antwerp (UZA), Department of Hematology

Edegem, Antwerp, B-2650, Belgium

Location

General Hospital Saint-Jan, Department of Hematology

Bruges, 8000, Belgium

Location

Jules Bordet Institute, Department of Infectious Disease

Brussels, 1000, Belgium

Location

University Hospitals Leuven, Campus Gasthuisberg, Department of Hematology

Leuven, 3000, Belgium

Location

UCL Mont-Godinne University Hospitals, Department of Hematology

Yvoir, B-5530, Belgium

Location

Hamilton Health Sciences, Infectious Disease Research

Hamilton, Ontario, L8V 1C3, Canada

Location

Toronto General Hospital

Toronto, Ontario, M5G 2N2, Canada

Location

McGill University Health Centre (MUHC), Division of Infectios Diseases

Montreal, Quebec, H4A 3J1, Canada

Location

Grenoble University Hospital Center, Department of Hematology

Grenoble, 38700, France

Location

South Lyon Hospital Center

Pierre-Bénite, 69310, France

Location

Hautepierre Hospital

Strasbourg, 67200, France

Location

University Hospital Jena

Jena, 07740, Germany

Location

Hospital Neuperlach - Municipal Hospital Munich GmbH, Clinic of Hematology and Oncology

Munich, 81737, Germany

Location

Chonnam National University

Hwasun, 519-809, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Seoul National University Hospital

Seoul, 11 0-744, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

MeSH Terms

Conditions

Invasive Pulmonary Aspergillosis

Interventions

isavuconazoleliposomal amphotericin B

Condition Hierarchy (Ancestors)

Pulmonary AspergillosisAspergillosisMycosesBacterial Infections and MycosesInfectionsInvasive Fungal InfectionsLung Diseases, FungalLung DiseasesRespiratory Tract Diseases

Study Officials

  • Mammen P Mammen, MD, FIDSA

    Vical

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Masking Details
The Sponsor, safety monitoring board, and data review committee are masked.
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 27, 2017

First Posted

October 31, 2017

Study Start

February 20, 2018

Primary Completion

January 14, 2019

Study Completion

January 14, 2019

Last Updated

February 27, 2019

Record last verified: 2019-02

Data Sharing

IPD Sharing
Will not share

Locations