NCT03312361

Brief Summary

To determine if a prolonged high altitude simulation test (HAST) lasting two hours, identifies more patients at risk of respiratory failure than the standard HAST lasting 20 minutes, in patients with neuromuscular disease (NMD) and severe pulmonary restriction. To evaluate the safety of supplemental oxygen administered in those with a positive HAST in the NMD population.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
23

participants targeted

Target at below P25 for not_applicable

Timeline
Completed

Started Apr 2016

Typical duration for not_applicable

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2016

Completed
1.5 years until next milestone

First Submitted

Initial submission to the registry

October 12, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

October 17, 2017

Completed
6 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2018

Completed
Last Updated

August 19, 2021

Status Verified

August 1, 2021

Enrollment Period

2 years

First QC Date

October 12, 2017

Last Update Submit

August 12, 2021

Conditions

Outcome Measures

Primary Outcomes (1)

  • Prolonged high altitude simulation test

    To determine if a prolonged high altitude simulation test (HAST) lasting two hours, identifies more patients at risk of respiratory failure than the standard HAST lasting 20 minutes, in patients with NMD and severe pulmonary restriction

    3 years

Secondary Outcomes (1)

  • Interventional high altitude simulation test

    3 years

Study Arms (1)

15% Oxygen

EXPERIMENTAL

All participants will breath in 15% oxygen for 2 hours

Drug: 15% oxygen

Interventions

Participants will inhale 15% oxygen for 2 hours to see how it affects them.

15% Oxygen

Eligibility Criteria

Age5 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • individuals with a confirmed diagnosis of NMD
  • age ≥ 5 years of age
  • absence of hypoxia at rest, defined as oxygen saturation ≥ 92% for two consecutive minutes while at rest and breathing room air
  • absence of daytime hypercapnea at rest, defined by partial pressure of carbon dioxide (pCO2) less than 45 mmHg on capillary or arterial blood gas at rest
  • patient or authorized substitute decision maker provides consent to study participation.

You may not qualify if:

  • current respiratory tract infection
  • inability to comply with the study procedures
  • severe heart failure as defined by uncontrolled symptoms of heart failure, or left ventricular ejection fraction \< 30%
  • presence of a tracheostomy
  • use of domiciliary bilevel positive airway pressure (BPAP) for more than 12 hours daily
  • recent hospital admission within the past 4 weeks.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

The Hospital for Sick Children

Toronto, Ontario, M5G 1X8, Canada

Location

MeSH Terms

Conditions

Neuromuscular Diseases

Interventions

Oxygen

Condition Hierarchy (Ancestors)

Nervous System Diseases

Intervention Hierarchy (Ancestors)

ChalcogensElementsInorganic ChemicalsGases

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
DIAGNOSTIC
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Respirologist

Study Record Dates

First Submitted

October 12, 2017

First Posted

October 17, 2017

Study Start

April 1, 2016

Primary Completion

April 1, 2018

Study Completion

April 1, 2018

Last Updated

August 19, 2021

Record last verified: 2021-08

Data Sharing

IPD Sharing
Will not share

Locations