NCT03271489

Brief Summary

This randomized multicenter phase 3b study seeks to evaluate the safety of elagolix in combination with estradiol/norethindrone acetate for the management of heavy menstrual bleeding associated with uterine fibroids in premenopausal women. This study was double-blind (DB) during the first 12 months and open-label (OL) for the next 36 months.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
478

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Sep 2017

Longer than P75 for phase_3

Geographic Reach
2 countries

157 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 31, 2017

Completed
5 days until next milestone

First Posted

Study publicly available on registry

September 5, 2017

Completed
8 days until next milestone

Study Start

First participant enrolled

September 13, 2017

Completed
6.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 28, 2024

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 28, 2024

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

July 22, 2025

Completed
Last Updated

July 22, 2025

Status Verified

July 1, 2025

Enrollment Period

6.8 years

First QC Date

August 31, 2017

Results QC Date

June 13, 2025

Last Update Submit

July 21, 2025

Conditions

Keywords

Elagolix SodiumHeavy Menstrual Bleeding (HMB)Heavy Uterine BleedingLeiomyomataMenorrhagiaElagolix + Norethindrone AcetateElagolix + E2/NETAElagolixSafetyEfficacy

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Adverse Events (AEs)

    An AE is defined as any untoward medical occurrence in a patient or clinical investigation in which a participant is administered a pharmaceutical product which does not necessarily have a causal relationship with this treatment. AEs during the 12-month DB period were defined as any AEs with onset on/after first dose of study drug during the DB period and no more than 30 days after the last dose of study drug for participants who discontinued early during the DB period, or until the first dose of study drug in the OL period for participants who entered the OL Treatment Period. AEs during the OL period were defined as AEs with onset on/after first dose of study drug during the OL period and no more than 30 days after the last dose of study drug. During the post-treatment follow-up (PTFU) period, adverse events were collected from 30 days post-last dose until end of study. Safety reporting during the PTFU period included AESIs. Other AEs may have also been reported.

    Baseline to 60 months

Secondary Outcomes (1)

  • Bone Mineral Density (BMD) Recovery After up to 48 Months of Treatment

    Baseline through Month 60

Study Arms (2)

Elagolix plus estradiol (E2)/norethindrone acetate (NETA)

EXPERIMENTAL
Drug: ElagolixDrug: Estradiol /norethindrone acetate (E2/NETA)

Placebo

PLACEBO COMPARATOR
Other: E2/NETA PlaceboOther: Elagolix Placebo

Interventions

Film-coated 300 mg tablets

Elagolix plus estradiol (E2)/norethindrone acetate (NETA)

Estradiol 1 mg/norethindrone acetate 0.5 mg capsules

Elagolix plus estradiol (E2)/norethindrone acetate (NETA)

Placebo capsules

Placebo

Film-coated placebo tablets

Placebo

Eligibility Criteria

Age18 Years - 50 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Participant is a premenopausal female at the time of Screening.
  • Participant has a diagnosis of uterine fibroids documented by a Pelvic Ultrasound \[Transabdominal ultrasound (TAU) or transvaginal ultrasound (TVU)\].
  • Participant has Heavy Menstrual Bleeding (HMB) associated with uterine fibroids as evidenced by Menstrual Blood Loss (MBL) \> 80 mL during each of two screening menses as measured by the alkaline hematin method.
  • Participant has negative urine and/or serum pregnancy test during Washout (if applicable) and/or Screening and just prior to first dose.
  • Participant has an adequate endometrial biopsy performed during Screening, the results of which show no clinical significant endometrial pathology.

You may not qualify if:

  • Participant has screening pelvic ultrasound or Saline Infusion Sonohysterography (SIS) results that show a clinically significant gynecological disorder.
  • Participant has history of osteoporosis or other metabolic bone disease.
  • Participant has clinically significant abnormalities in clinical chemistry, hematology, or urinalysis.
  • Participant has a history of major depression or post-traumatic stress disorder (PTSD) episode within 2 years of screening, OR a history of other major psychiatric disorder at any time (e.g., schizophrenia, bipolar disorder).
  • Participant is using any systemic corticosteroids for over 14 days within 3 months prior to Screening or is likely to require treatment with systemic corticosteroids during the course of the study. Over the counter and prescription topical, inhaled, intranasal or intra-articular injectable (for occasional use) corticosteroids are allowed.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (157)

Alabama Clinical Therapeutics /ID# 160835

Birmingham, Alabama, 35235-3430, United States

Location

Alabama Clinical Therapeutics /ID# 160927

Birmingham, Alabama, 35235-3430, United States

Location

Choice Research, LLC /ID# 161498

Dothan, Alabama, 36303, United States

Location

Southern Women's Specialists PC /ID# 161531

Fairhope, Alabama, 36532-3029, United States

Location

E Squared Research /ID# 163645

Huntsville, Alabama, 35801, United States

Location

Women's Health Alliance of Mobile /ID# 161443

Mobile, Alabama, 36604-1410, United States

Location

Mobile, OBGYN P.C. /ID# 161530

Mobile, Alabama, 36608, United States

Location

Mesa Obstetricians and Gynecologists /ID# 160955

Mesa, Arizona, 85209, United States

Location

Noble Clinical Research /ID# 166949

Tucson, Arizona, 85704, United States

Location

Vision's Clinical Research-Tucson /ID# 161508

Tucson, Arizona, 85712, United States

Location

Eclipse Clinical Research /ID# 161516

Tucson, Arizona, 85745, United States

Location

Duplicate_Core Healthcare Group /ID# 160858

Cerritos, California, 90703, United States

Location

Diagnamics Inc. /ID# 160950

Encinitas, California, 92024, United States

Location

HRC Fertility /ID# 161493

Encino, California, 91436, United States

Location

SC Clinical Research /ID# 164395

Garden Grove, California, 92844, United States

Location

Duplicate_Duplicate_Marvel Clinical Research /ID# 167297

Huntington Beach, California, 92647, United States

Location

Grossmont Ctr Clin Research /ID# 165120

La Mesa, California, 91942, United States

Location

Olympia Clinical Trials /ID# 201562

Los Angeles, California, 90036-4667, United States

Location

National Research Institute /ID# 160952

Los Angeles, California, 90057, United States

Location

Futura Research, Org /ID# 160924

Montebello, California, 90640, United States

Location

California Medical Research Associates /ID# 161481

Northridge, California, 91324, United States

Location

Northern California Research /ID# 161561

Sacramento, California, 95821-2640, United States

Location

Precision Research Institute - San Diego /ID# 163069

San Diego, California, 92114-3643, United States

Location

MD Strategies Research Centers /ID# 161544

San Diego, California, 92119, United States

Location

Health care Affiliates Medical Group /ID# 163324

Santa Ana, California, 92704, United States

Location

Alta California Medical Group /ID# 163564

Simi Valley, California, 93065, United States

Location

Upland Clinical Research /ID# 164528

Upland, California, 91786-4027, United States

Location

Bayview Research Group LLC /ID# 161484

Valley Village, California, 91607, United States

Location

Advanced RX Clinical Research /ID# 161599

Westminster, California, 92683-4567, United States

Location

Emerson Clinical Research Inst /ID# 162181

Washington D.C., District of Columbia, 20011, United States

Location

James A. Simon, MD, PC /ID# 160931

Washington D.C., District of Columbia, 20036, United States

Location

Women's Health Partners /ID# 203577

Boca Raton, Florida, 33433-7041, United States

Location

David Lubetkin MD LLC /ID# 203578

Boca Raton, Florida, 33486-2269, United States

Location

Brandon Premier Health Care, PA/Gulf Coast Research Group, LLC /ID# 160910

Brandon, Florida, 33510-3107, United States

Location

Omega Research Maitland, LLC /ID# 160857

DeBary, Florida, 32713-2260, United States

Location

Midland Florida Clinical Research Center /ID# 161487

DeLand, Florida, 32720-0920, United States

Location

KO Clinical Research, LLC /ID# 160928

Fort Lauderdale, Florida, 33316, United States

Location

Sweet Hope Research Specialty Inc /ID# 163522

Hialeah, Florida, 33016-1897, United States

Location

Solutions Through Adv Rch /ID# 160935

Jacksonville, Florida, 32256, United States

Location

Altus Research, Inc /ID# 160912

Lake Worth, Florida, 33461, United States

Location

Wellington Anti-Aging Centre /ID# 203540

Loxahatchee Groves, Florida, 33470-4937, United States

Location

South Florida Wellness & Clinic /ID# 161535

Margate, Florida, 33063, United States

Location

Invictus Clinical Research Group,LLC /ID# 160925

Miami, Florida, 33144, United States

Location

Healthcare Clinical Data, Inc /ID# 160888

Miami, Florida, 33161, United States

Location

Palmetto Professional Research /ID# 161442

Miami, Florida, 33172, United States

Location

Vista Health Research, LLC /ID# 163044

Miami, Florida, 33176-1032, United States

Location

Duplicate_Precision Research Organization /ID# 161522

Miami Lakes, Florida, 33016-1501, United States

Location

Ocean Blue Medical Research Center, Inc /ID# 161549

Miami Springs, Florida, 33166, United States

Location

Salom Tangir, LLC /ID# 162542

Miramar, Florida, 33027, United States

Location

Advanced Research Institute, Inc /ID# 163748

New Port Richey, Florida, 34653, United States

Location

A Premier Medical Research of FL /ID# 201882

Orange City, Florida, 32763-2833, United States

Location

Clinical Associates of Orlando /ID# 160889

Orlando, Florida, 32819-8900, United States

Location

Oncova Clinical Research, Inc. /ID# 160937

Saint Cloud, Florida, 34769, United States

Location

Physician Care Clin. Res., LLC /ID# 161547

Sarasota, Florida, 34239, United States

Location

Accel Research Sites - St Petersburg Clinical Research Unit /ID# 160913

St. Petersburg, Florida, 33709-3113, United States

Location

Treasure Coast Research /ID# 161824

Stuart, Florida, 34996, United States

Location

Discovery Clinical Research /ID# 160891

Sunrise, Florida, 33324, United States

Location

Precision Clinical Research /ID# 165377

Sunrise, Florida, 33351-7311, United States

Location

GCP Clinical Research, LLC /ID# 164593

Tampa, Florida, 33609-4044, United States

Location

University of South Florida- Neuroscience Institute /ID# 160960

Tampa, Florida, 33613, United States

Location

Jedidiah Clinical Research /ID# 167114

Tampa, Florida, 33617, United States

Location

Virtus Research Consultants, LLC /ID# 160855

Wellington, Florida, 33414, United States

Location

Comprehensive Clinical Trials LLC /ID# 161479

West Palm Beach, Florida, 33409, United States

Location

Journey Medical Research Insti /ID# 160958

Alpharetta, Georgia, 30005, United States

Location

Paramount Research Solutions /ID# 161557

Alpharetta, Georgia, 30005, United States

Location

AGILE Clinical Research Trials /ID# 160941

Atlanta, Georgia, 30328-5532, United States

Location

Mount Vernon Clinical Res, LLC /ID# 161491

Atlanta, Georgia, 30328, United States

Location

Atlanta Women's Research Institute /ID# 160844

Atlanta, Georgia, 30342, United States

Location

Medisense Inc /ID# 161494

Atlanta, Georgia, 30363, United States

Location

Duplicate_Atlanta Gynecology Research Institute /ID# 160851

Suwanee, Georgia, 30024-7159, United States

Location

Bingham Memorial Hospital /ID# 201130

Blackfoot, Idaho, 83221, United States

Location

Leavitt Womens Healthcare /ID# 163419

Idaho Falls, Idaho, 83404, United States

Location

Womens Healthcare Assoc, DBA /ID# 160933

Idaho Falls, Idaho, 83404, United States

Location

Sonora Clinical Research /ID# 167610

Meridian, Idaho, 83646-1144, United States

Location

Asr, Llc /Id# 162179

Nampa, Idaho, 83687, United States

Location

Women's Health Practice, LLC /ID# 161553

Champaign, Illinois, 61820, United States

Location

Moore for Women Healthcare and Wellness Institute, LLC /ID# 167118

Chicago, Illinois, 60605-2168, United States

Location

Duplicate_University of Chicago /ID# 162667

Chicago, Illinois, 60637, United States

Location

Alliance for Multispecialty Research, LLC /ID# 160932

Oak Brook, Illinois, 60523, United States

Location

Women's Health Advantage /ID# 161537

Fort Wayne, Indiana, 46825, United States

Location

Womens & Family Care, LLC dba /ID# 160890

Shawnee Mission, Kansas, 66218, United States

Location

Bluegrass Clinical Research /ID# 163485

Louisville, Kentucky, 40291-1988, United States

Location

Clinical Trials Management, LLC - Covington /ID# 160838

Covington, Louisiana, 70433, United States

Location

Clinical Trials Management, LLC - Covington /ID# 160893

Covington, Louisiana, 70433, United States

Location

Praetorian Pharmaceutical Research /ID# 161532

Marrero, Louisiana, 70072, United States

Location

Ochsner Baptist Medical Centre /ID# 161507

New Orleans, Louisiana, 70115, United States

Location

Women Under Study, LLC /ID# 163990

New Orleans, Louisiana, 70125-1923, United States

Location

Willis-Knighton Pediatric GI S /ID# 161534

Shreveport, Louisiana, 71118, United States

Location

Exordia Medical Research, Inc /ID# 160853

Fall River, Massachusetts, 02723, United States

Location

Duplicate_Great Lakes Research Group, Inc. /ID# 161511

Bay City, Michigan, 48602, United States

Location

Wayne State University /ID# 160944

Detroit, Michigan, 48201-2013, United States

Location

Valley OB-Gyn Clinic - Saginaw /ID# 203579

Saginaw, Michigan, 48602-4323, United States

Location

Saginaw Valley Med Res Group /ID# 160840

Saginaw, Michigan, 48604, United States

Location

Quad Clinical Research, LLC /ID# 200943

St Louis, Missouri, 63109, United States

Location

Excel Clinical Research /ID# 165588

Las Vegas, Nevada, 89109, United States

Location

Office of Edmond E. Pack, MD /ID# 162604

Las Vegas, Nevada, 89113, United States

Location

Private practice: Dr. Rex G. Mabey JR /ID# 160915

Las Vegas, Nevada, 89128, United States

Location

Jersey Shore University Medical Center /ID# 160916

Neptune City, New Jersey, 07753-4859, United States

Location

Lovelace Scientific Resources /ID# 163644

Albuquerque, New Mexico, 87108, United States

Location

Bosque Women's Care /ID# 162606

Albuquerque, New Mexico, 87109, United States

Location

SUNY Downstate Medical Center /ID# 160922

Brooklyn, New York, 11203, United States

Location

Duplicate_Northwell Health System - Manhasset /ID# 201058

Manhasset, New York, 11030-3816, United States

Location

Columbia Univ Medical Center /ID# 161519

New York, New York, 10032-3725, United States

Location

Hamburg Regional Gynecology Gr /ID# 161427

Orchard Park, New York, 14127, United States

Location

DJL Clinical Research, PLLC /ID# 161548

Charlotte, North Carolina, 28211, United States

Location

Carolina Women's Research and Wellness Center /ID# 160914

Durham, North Carolina, 27713-7512, United States

Location

Unified Women's Clinical Resea /ID# 163014

Raleigh, North Carolina, 27607, United States

Location

Wake Radiology UNC REX Healthcare - Raleigh Office /ID# 161490

Raleigh, North Carolina, 27612, United States

Location

Unified Women's Clinical Resea /ID# 160957

Winston-Salem, North Carolina, 27103, United States

Location

Clinical Inquest Center Ltd /ID# 160892

Beavercreek, Ohio, 45431-2573, United States

Location

Duplicate_CTI Clinical Research Center /ID# 160942

Cincinnati, Ohio, 45212, United States

Location

Univ Hosp Cleveland /ID# 160953

Cleveland, Ohio, 44106, United States

Location

Central Ohio Clinical Research /ID# 201162

Columbus, Ohio, 43213-3399, United States

Location

Duplicate_Optimed Research /ID# 165600

Columbus, Ohio, 43235, United States

Location

Hilltop Obstetrics & Gynecology /ID# 203576

Middletown, Ohio, 45005-5200, United States

Location

University of Toledo /ID# 160923

Toledo, Ohio, 43614, United States

Location

Oregon Medical Research Center /ID# 161514

Portland, Oregon, 97239, United States

Location

OB/GYN Associates of Erie /ID# 161541

Erie, Pennsylvania, 16507-1423, United States

Location

Penn State University and Milton S. Hershey Medical Center /ID# 160896

Hershey, Pennsylvania, 17033, United States

Location

University of Pennsylvania /ID# 160936

Philadelphia, Pennsylvania, 19104-5502, United States

Location

DUP_Thomas Jefferson University /ID# 200304

Philadelphia, Pennsylvania, 19107, United States

Location

Vista Clinical Research /ID# 160946

Columbia, South Carolina, 29201, United States

Location

VitaLink Research-Spartanburg /ID# 164592

Spartanburg, South Carolina, 29303, United States

Location

Duplicate_Chattanooga Medical Research /ID# 160885

Chattanooga, Tennessee, 37404, United States

Location

WR-ClinSearch /ID# 160887

Chattanooga, Tennessee, 37421-1605, United States

Location

The Jackson Clinic, PA /ID# 162496

Jackson, Tennessee, 38305, United States

Location

Research Memphis Associates, LLC /ID# 160939

Memphis, Tennessee, 38119-3895, United States

Location

OBGYN North /ID# 203580

Austin, Texas, 78758-5444, United States

Location

Austin Area Obstetrics, Gynecology, and Fertility /Id# 203542

Austin, Texas, 78758-5653, United States

Location

Discovery Clinical Trials -HCWC /ID# 161543

Dallas, Texas, 75230-2571, United States

Location

Duplicate_The University of Texas Southwestern Medical Center /ID# 161496

Dallas, Texas, 75390-8575, United States

Location

Baylor Scott & White /ID# 161515

Fort Worth, Texas, 76104-4110, United States

Location

Willowbend Health and Wellness - Frisco /ID# 160954

Frisco, Texas, 75035, United States

Location

The Ob/Gyn Center /ID# 165928

Houston, Texas, 77030, United States

Location

Precision Research Institute, LLC /ID# 161554

Houston, Texas, 77036, United States

Location

The Woman's Hospital of Texas /ID# 160959

Houston, Texas, 77054, United States

Location

Centex Studies, Inc /ID# 163858

Houston, Texas, 77058-2705, United States

Location

Centex Studies, Inc. - Houston /ID# 160917

Houston, Texas, 77058, United States

Location

UAG Innovation Women Research, /ID# 167415

Houston, Texas, 77074, United States

Location

America's Adv. Wellness Center /ID# 167548

Houston, Texas, 77080, United States

Location

FMC Science /ID# 160886

Lampasas, Texas, 76550, United States

Location

Advances in Health, Inc. /ID# 160930

Pearland, Texas, 77854, United States

Location

ClinRx Research, LLC /ID# 201170

Plano, Texas, 75024-5280, United States

Location

Clinical Trials of Texas, Inc /ID# 161510

San Antonio, Texas, 78229, United States

Location

VIP Trials /ID# 161546

San Antonio, Texas, 78230, United States

Location

Houston Ctr for Clin Research /ID# 160837

Sugar Land, Texas, 77479, United States

Location

The Univ Texas HSC at Tyler /ID# 161533

Tyler, Texas, 75708, United States

Location

Center of Reproductive Medicine /ID# 162498

Webster, Texas, 77598, United States

Location

Univ of Virgnia Medical center /ID# 166283

Charlottesville, Virginia, 22908-0816, United States

Location

Eastern Virginia Med School /ID# 160856

Norfolk, Virginia, 23507-1627, United States

Location

Clinical Research Partners /ID# 160929

North Chesterfield, Virginia, 23235, United States

Location

Clinical Research Partners /ID# 160948

North Chesterfield, Virginia, 23235, United States

Location

Clinical Trials Virginia, Inc. /ID# 160943

Richmond, Virginia, 23225, United States

Location

Specialists for Women /ID# 201129

Suffolk, Virginia, 23434-8151, United States

Location

Tidewater Clinical Research /ID# 160949

Virginia Beach, Virginia, 23456, United States

Location

Henry A. Rodriguez Ginorio, MD /ID# 160861

San Juan, 00917-5022, Puerto Rico

Location

School of Medicine University of Puerto Rico-Medical Science Campus /ID# 160862

San Juan, 00935, Puerto Rico

Location

MeSH Terms

Conditions

MenorrhagiaLeiomyoma

Interventions

elagolixEstradiolNorethindrone Acetate

Condition Hierarchy (Ancestors)

Uterine HemorrhageUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesHemorrhagePathologic ProcessesPathological Conditions, Signs and SymptomsMenstruation DisturbancesNeoplasms, Muscle TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasms

Intervention Hierarchy (Ancestors)

EstrenesEstranesSteroidsFused-Ring CompoundsPolycyclic CompoundsEstradiol CongenersGonadal Steroid HormonesGonadal HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNorethindroneNorpregnenesNorpregnanesNorsteroids

Results Point of Contact

Title
Global Medical Services
Organization
AbbVie

Study Officials

  • ABBVIE INC.

    AbbVie

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 31, 2017

First Posted

September 5, 2017

Study Start

September 13, 2017

Primary Completion

June 28, 2024

Study Completion

June 28, 2024

Last Updated

July 22, 2025

Results First Posted

July 22, 2025

Record last verified: 2025-07

Data Sharing

IPD Sharing
Will share

AbbVie is committed to responsible clinical trial data sharing. This includes access to anonymized, individual and trial-level data (analysis data sets), as well as other information.

Shared Documents
STUDY PROTOCOL, SAP, CSR, ANALYTIC CODE
Time Frame
For details on when studies are available for sharing visit https://vivli.org/ourmember/abbvie/
Access Criteria
To learn more about the process, or to submit a request, visit the following link https://www.abbvieclinicaltrials.com/hcp/data-sharing/
More information

Locations